- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: APX001
Total 247 results
-
Aspen NeuroscienceCalifornia Institute for Regenerative Medicine (CIRM)Enrolling by invitation
-
Annexon, Inc.Active, not recruitingGeographic AtrophyUnited States, Australia, New Zealand
-
Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, United Kingdom, Canada, Germany, Italy
-
Amicus TherapeuticsCompletedFabry DiseaseAustralia, Brazil
-
Amicus TherapeuticsCompletedFabry DiseaseUnited States
-
Amicus TherapeuticsTerminatedFabry DiseaseUnited Kingdom, United States, Australia, Brazil, France
-
Amicus TherapeuticsCompletedFabry DiseaseFrance, United Kingdom
-
Asana BioSciencesTerminatedProstate Cancer | Cancer of the Prostate | Neoplasms, Prostate | Prostatic Cancer | Neoplasms, Prostatic | Prostate Neoplasms, Castration-resistantUnited States
-
Vertex Pharmaceuticals IncorporatedNot yet recruiting
-
Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Italy, Germany, Saudi Arabia
-
Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, Germany, Italy, United Kingdom, Canada
-
Spruce BiosciencesRecruitingCongenital Adrenal Hyperplasia | 21-OHDUnited States
-
Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
-
Amicus TherapeuticsTerminatedFabry DiseaseAustralia, United States, Italy, Spain, Belgium, Turkey, Brazil, Argentina, United Kingdom, Denmark, France, Canada, Egypt
-
Schmidhofer, Mark, MDCystic Fibrosis Foundation; Mast Therapeutics, Inc.Active, not recruiting
-
AlphaVax, Inc.Duke UniversityCompletedBreast Cancer | Colorectal Cancer | Pancreatic Cancer | Lung Cancer | Colon CancerUnited States
-
Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Canada, Denmark, Estonia, Germany, Ireland, Italy, Korea, Republic of, Latvia, Lithuania, Netherlands, Poland, Romania, Spain, Sweden, Switzerland, Turkey, United Kingdom
-
Tetra Bio-PharmaCompleted
-
Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Estonia, Germany, Korea, Republic of, Latvia, Lithuania, Poland, Romania, Spain, Sweden, Turkey, Canada, Italy, United Kingdom
-
Amicus TherapeuticsCompletedOpen-Label Extension Study of the Long-Term Effects of Migalastat HCL in Patients With Fabry DiseaseFabry DiseaseUnited States, Austria, United Kingdom, Argentina, Australia, Belgium, Brazil, Canada, Denmark, Egypt, France, Italy, Japan, Spain, Turkey
-
Amicus TherapeuticsCompletedFabry DiseaseUnited States, Italy, Spain, Turkey, Brazil, Canada, United Kingdom, France, Poland, Australia, Egypt, Argentina, Denmark
-
Bio-Path Holdings, Inc.CompletedRecurrent Adult Acute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Ph1 Positive CMLUnited States
-
Alector Inc.CompletedHealthy | Frontotemporal DementiaUnited States, Canada, United Kingdom
-
Origin Inc.CompletedFoot Ulcer, DiabeticUnited States
-
Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingSickle Cell Disease | Hemoglobinopathies | Hematological Diseases | Hydroxyurea Failure | Hydroxyurea IntoleranceUnited States, Italy, United Kingdom, Germany
-
Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Hematological DiseasesUnited States, Belgium, Canada, France, Germany, Italy, United Kingdom
-
Novartis PharmaceuticalsActive, not recruiting
-
Duke UniversityAlphaVax, Inc.CompletedStage III Colon CancerUnited States
-
UNION therapeuticsCompleted
-
Hadassah Medical OrganizationCompletedThrombocytopenia
-
Emergent BioSolutionsCompleted
-
ChimerixCompletedDouble-stranded DNA VirusUnited States
-
ChimerixTerminated
-
ChimerixFood and Drug Administration (FDA)Withdrawn
-
Novartis PharmaceuticalsActive, not recruitingChronic Myelogenous LeukemiaSpain, United Kingdom, Germany, Canada, Austria, France, Korea, Republic of, Greece, Singapore, Italy, Argentina, Poland, Vietnam, Malaysia, Oman, Brazil
-
Bio-Path Holdings, Inc.WithdrawnAcute Myeloid Leukemia | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia, Ph1-PositiveUnited States
-
Apeptico Forschung und Entwicklung GmbHCompleted
-
AmDermaInternational Dermatology Research, Inc.CompletedPlaque PsoriasisDominican Republic
-
Spruce BiosciencesCompletedPolycystic Ovary SyndromeUnited States
-
ChimerixTerminated
-
ChimerixNo longer available
-
Baxalta now part of ShireCompletedHemophilia AUnited States, France, Austria, United Kingdom, Germany, Belgium, Canada, Italy, Sweden
-
Amicus TherapeuticsCompleted
-
Allakos Inc.Completed
-
ChimerixCompletedAdenovirus InfectionUnited States
-
Bio-Path Holdings, Inc.RecruitingFallopian Tube Neoplasms | Carcinoma, Ovarian Epithelial | Solid Tumor | Endometrial Cancer | Peritoneal Cancer | Solid Tumor, AdultUnited States
-
AmDermaCompletedActinic KeratosisUnited States
-
ChimerixCompletedAdenovirus DiseaseUnited States