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Search clinical trials for: Genetic: AAV5-hRKp.RPGR
Total 1586 results
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Saglik Bilimleri Universitesi Gulhane Tip FakultesiCompletedAnxiety | Knowledge, Attitudes, Practice | Decision Making | Chromosome AbnormalityTurkey
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University of PennsylvaniaUnited States Department of DefenseCompleted
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Genomind, LLCWithdrawnMajor Depressive DisorderUnited States
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University of British ColumbiaCompletedSchizophrenia | Schizoaffective Disorder | Bipolar DisorderCanada
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National Institute on Aging (NIA)National Human Genome Research Institute (NHGRI)Completed
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Paul S. BernsteinActive, not recruitingAge-Related Macular Degeneration | Genetic Testing | Nutritional BiomarkersUnited States
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University of Southern CaliforniaNational Cancer Institute (NCI)Recruiting
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MeiraGTx UK II LtdCompletedLeber Congenital AmaurosisUnited Kingdom, United States
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaCompleted
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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UniQure Biopharma B.V.RecruitingHuntington DiseasePoland, United Kingdom, Germany
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MeiraGTx UK II LtdSyne Qua Non LimitedCompletedEye Diseases | Retinal Diseases | Eye Diseases, Hereditary | Leber Congenital Amaurosis (LCA)United States, United Kingdom
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Institut National de la Santé Et de la Recherche...RecruitingInfections | Autoimmune Diseases | Diagnosis | Immune DeficiencyFrance, United States, Australia, Belgium, Japan, Netherlands
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Imperial College LondonRecruiting
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Nantes University HospitalRecruitingCongenital Complete Heart Block | Cardiac Conduction Defect ProgressiveFrance
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Mersin UniversityCompleted
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Homology Medicines, IncWithdrawnMucopolysaccharidosis IIUnited States, Canada
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University Health Network, TorontoTerminated
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Mclean HospitalTerminated
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Carolyn LamBayer; Boston Scientific Corporation; Translational & Clinical Research by NMRC... and other collaboratorsCompletedHeart FailureTaiwan, Thailand, Korea, Republic of, Malaysia, Hong Kong, China, India, Indonesia, Japan, Philippines, Singapore
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University Hospital, GhentTerminatedInfertility | Preimplantation Genetic ScreeningBelgium
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Cure CMDUniversity of Chicago; Boston Children's Hospital; Valerion Therapeutics, LLC; Congenital...Completed
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Mayo ClinicNational Human Genome Research Institute (NHGRI)CompletedMyocardial Infarction | Coronary Artery Disease | Genomic Risk CommunicationUnited States
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Assistance Publique - Hôpitaux de ParisMinistry of Health, FranceCompleted
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Brain Neurotherapy Bio, Inc.California Institute for Regenerative Medicine (CIRM); Asklepios Biopharmaceutical...Active, not recruiting
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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Assistance Publique - Hôpitaux de ParisRecruitingSocial Cognition of Schizophrenia, Bipolas or Depressed PatientsFrance
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University Hospital, BrestRecruitingMyelodysplastic Syndromes | Myelodysplastic Syndrome With Isolated Del(5Q) | Myelodysplastic Syndrome With Del(5Q)France
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University of Alabama at BirminghamUniversity of Louisville; University of Mississippi Medical Center; Woman's Hospital... and other collaboratorsRecruitingWhole Genome SequencingUnited States
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The Guthrie ClinicActive, not recruiting
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Dana-Farber Cancer InstituteAmbry GeneticsCompletedBreast Cancer | Pancreatic Cancer | Ovarian Cancer | Metastatic Prostate CancerUnited States
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Sohag UniversityCompletedCystic FibrosisEgypt
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Nantes University HospitalActive, not recruitingHYPOCHOL : A Genetically-based Strategy to Identify New Targets in Cholesterol Metabolism (HYPOCHOL)HypobetalipoproteinemiaFrance
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University Hospital, MontpellierInstitut National de la Santé Et de la Recherche Médicale, France; Sys2Diag...Completed
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Wayne State UniversityUnknownAneuploidy | Autosomal Recessive DisorderUnited States
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University of TorontoNutrigenomix Inc.UnknownHealth BehaviorCanada
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Centre Hospitalier Universitaire de NīmesInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedDiabetic Foot | Staphylococcus AureusFrance
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National Institute for Mother and Child Health...Marie Curie Emergency Children's Hospital, Bucharest; Victor Gomoiu Children...RecruitingChronic Granulomatous DiseaseRomania
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Tobias MoserRecruitingHearing Impairment | Otoferlin-related Auditory SynaptopathyGermany
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Maastricht University Medical CenterRecruitingPost-Infarction Heart Rupture | Gene PolymorphismItaly
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Nantes University HospitalInserm UMR1087, CNRS UMR6291; Clinique des Données, CIC 1413, CHU Nantes; CIC-FEA...Recruiting
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University Hospital, LilleNot yet recruiting
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China National Center for Cardiovascular DiseasesPeking Union Medical College HospitalRecruiting
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Ain Shams UniversityCompleted
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Dana-Farber Cancer InstituteActive, not recruitingPediatric Solid TumorUnited States
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CENTOGENE GmbH RostockActive, not recruiting
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University of Ljubljana, Faculty of MedicineUniversity Medical Centre Ljubljana; Kinderkrankenhaus auf der BultCompletedFamilial Hypercholesterolemia | Polygenic HypercholesterolaemiaGermany, Slovenia