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Search clinical trials for: Onasemnogene Abeparvovec-xioi
Total 35 results
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular Atrophy Type IKorea, Republic of, Taiwan, Japan
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Novartis Gene TherapiesTerminatedSpinal Muscular AtrophyUnited States
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular AtrophyUnited States, United Kingdom, Australia, Belgium, Canada, Japan
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Novartis Gene TherapiesCompletedGene Therapy | SMA - Spinal Muscular AtrophyUnited States
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Novartis Gene TherapiesActive, not recruitingSpinal Muscular Atrophy 1United States
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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Novartis Gene TherapiesCompletedSMAFrance, United Kingdom, Italy, Belgium
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Novartis PharmaceuticalsRecruitingSpinal Muscular AtrophiesBrazil
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Novartis PharmaceuticalsRecruitingSpinal Muscular Atrophy (SMA)Spain, Canada, Taiwan, Belgium, Malaysia, China, Japan, Italy, Singapore, United Kingdom, France, Australia, Thailand, Denmark, United States
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Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
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Novartis PharmaceuticalsActive, not recruitingBiallelic RPE65 Mutation-associated Retinal DystrophyJapan
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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Spark TherapeuticsActive, not recruitingLeber Congenital AmaurosisUnited States
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Spark TherapeuticsCompleted
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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Novo Nordisk A/SEnrolling by invitationCongenital Bleeding Disorder | Congenital FXIII DeficiencyJapan
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Medical University of GrazActive, not recruiting
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencySpain, United States, Canada, Italy, United Kingdom, Hungary
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom, Israel, United States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyFrance, United States, Israel, Spain, Switzerland, Germany, Canada, Japan, United Kingdom, Italy, Finland, Austria
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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Universidad de GranadaUnknown
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Novo Nordisk A/STerminatedInflammation | Ulcerative ColitisPoland, Croatia, Denmark, Bulgaria, Hungary, Ukraine, Russian Federation
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St. Justine's HospitalCompletedRespiratory FailureCanada
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Masaryk Hospital Krajská zdravotní a.s.CompletedCoagulation Disorder | Multiple Trauma | Coagulation Defect; Acquired | Coagulation Factor DeficiencyCzechia
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St. Justine's HospitalCompleted
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Ajou University School of MedicineIlsung Pharmaceuticals CO.,LTD.CompletedSpinal Anesthesia | Autonomic Nervous SystemKorea, Republic of
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University College, LondonCSL BehringUnknown
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Hospitales Universitarios Virgen del RocíoCompletedCoagulation Disorder | CarcinomatosisSpain
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Fondation Ophtalmologique Adolphe de RothschildActive, not recruitingReproducibility, Internal Consistency, Relevance and Discriminatory Performance of the TestsFrance
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Brugmann University HospitalCompleted
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Postgraduate Institute of Medical Education and...RecruitingCoagulation Disorder | Cirrhosis, Liver | Variceal HemorrhageIndia
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University of WashingtonNational Cancer Institute (NCI)CompletedStage IIB Lung Non-Small Cell Carcinoma AJCC v7 | Stage IIIA Lung Non-Small Cell Cancer AJCC v7 | Stage IIIB Lung Non-Small Cell Cancer AJCC v7United States
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Ironwood Pharmaceuticals, Inc.Medpace, Inc.TerminatedGout | Chronic Kidney Disease (CKD)United States, Hungary, Poland, Czechia
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University of PernambucoCompletedDental CariesBrazil