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Search clinical trials for: Beta Thalassemia
Total 8716 results
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Regeneron PharmaceuticalsNot yet recruitingNon-transfusion Dependent Beta-thalassemia (NTDT)
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Assiut UniversityNot yet recruiting
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Children's Hospital of PhiladelphiaNot yet recruiting
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Editas Medicine, Inc.Not yet recruitingSickle Cell Disease | Hemoglobinopathies | Transfusion-dependent Beta-Thalassemia
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Bioray LaboratoriesXiangya Hospital of Central South University; The 923rd Hospital of Joint Logistics...Recruiting
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Lantu BiopharmaNot yet recruitingBeta-Thalassemia
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Kind Pharmaceuticals LLCNot yet recruiting
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Bioray LaboratoriesXiangya Hospital of Central South University; Sun Yat-Sen Memorial Hospital... and other collaboratorsNot yet recruiting
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CorrectSequence Therapeutics Co., LtdRecruitingBeta-Thalassemia MajorChina
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Kanglin Biotechnology (Hangzhou) Co., Ltd.Not yet recruitingTransfusion-dependent Beta-ThalassemiaChina
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingBeta-ThalassemiaUnited States
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Institute of Hematology & Blood Diseases Hospital...Kanglin BiotechRecruitingTransfusion-dependent Beta-ThalassemiaChina
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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Hematology department of the 920th hospitalRecruiting
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Azienda Ospedaliero-Universitaria di ModenaRecruitingIron Overload | Hemochromatosis | Thalassemia Major | Thalassemia Intermedia | EndocrinopathyItaly
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Bristol-Myers SquibbRecruitingMyelodysplastic Syndrome | Beta ThalassemiaKorea, Republic of
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Marwa Hassan Abdelhamed HassanAssiut UniversityNot yet recruitingEvaluate Bone Denisty Changes in Children With Beta Thalassemia Major
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Children's Hospital of Fudan UniversityCorrectSequence Therapeutics Co., LtdRecruiting
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Institute of Hematology & Blood Diseases Hospital...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingThalassemia Major | Thalassemia, BetaChina
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityNot yet recruitingAcute Leukemia | Thalassemia MajorChina
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Institute of Hematology & Blood Diseases HospitalRecruitingGene Therapy | Transfusion-dependent Beta-ThalassemiaChina
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National Heart, Lung, and Blood Institute (NHLBI)Not yet recruitingSickle Cell Disease | Sickle Cell Disorders | Hb-SS Disease | Hemoglobin S | Disease Sickle Cell Anemia | Hemoglobin Beta Thalassemia DiseaseUnited States
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Assiut UniversityNot yet recruitingSickle Cell Disease, Beta Thalassemia Intermedia
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Shenzhen HemogenRecruiting
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Institute of Hematology & Blood Diseases HospitalR&D Kanglin BiotechRecruitingTransfusion-dependent Beta-ThalassemiaChina
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Queen's University, BelfastBelfast Health and Social Care TrustRecruiting
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Cyprus Institute of Neurology and GeneticsRecruitingSickle Cell Disease | Hemoglobinopathies | Thalassemia Alpha | Thalassemia, BetaUnited States, Denmark, Spain, Belgium, Portugal, Congo, The Democratic Republic of the, Greece, Argentina, Brunei Darussalam, Cyprus, Israel, Italy, Nigeria, Malaysia, Angola, Pakistan
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Assiut UniversityNot yet recruitingThalassemia Major
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Shanghai BDgene Co., Ltd.Ruijin HospitalNot yet recruiting
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Shanghai BDgene Co., Ltd.Shanghai Children's Medical CenterNot yet recruiting
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First Affiliated Hospital of Guangxi Medical UniversityGenmedicn Biopharma Ltd.RecruitingTransfusion Dependent Beta-ThalassemiaChina
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Shenzhen HemogenRecruiting
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Memorial Sloan Kettering Cancer CenterRecruitingSickle Cell Disease | Thalassemia | Thalassemia, BetaUnited States
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Pharmacosmos A/SICON plcRecruitingBeta Thalassemia Major AnemiaDenmark
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Sanguine BiosciencesRecruitingHeart Diseases | Stroke | Lymphoma | Multiple Sclerosis | Kidney Diseases | Diabetes | Leukemia | Age-Related Macular Degeneration | Cancer | Arthritis | Schizophrenia | Thyroid Diseases | Parkinson Disease | Hepatitis | Vasculitis | Psoriasis | Asthma | Amyloidosis | Fibromyalgia | Graves Disease | Alzheimer Disease | Celiac Disease | Cirr... and other conditionsUnited States
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Tanta UniversityRecruitingBeta Thalassemia With Increased Tricuspid Regurgitant Jet VelocityEgypt
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Bristol-Myers SquibbRecruiting
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University Hospital of FerraraRecruiting
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Cairo UniversityRecruitingPulmonary Function | Physical Fitness | β-ThalassemiaEgypt
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Italy, Germany, Saudi Arabia
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Sun Yat-sen UniversityRecruitingThalassemia Major | Transfusion-dependent AnemiaChina
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Editas Medicine, Inc.RecruitingHemoglobinopathies | Thalassemia Major | Thalassemia Intermedia | Transfusion Dependent Beta ThalassemiaUnited States, Canada
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Assiut UniversityNot yet recruiting
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Anemia | Beta ThalassemiaUnited States
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, Germany, Italy, United Kingdom, Canada
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Assiut UniversityNot yet recruiting
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Assiut UniversityRecruiting
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Assiut UniversityNot yet recruiting