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Search clinical trials for: Congenital Muscular Dystrophy
Total 21693 results
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Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
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Sarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
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Weill Medical College of Cornell UniversityThe Rogosin InstituteEnrolling by invitationAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Ondokuz Mayıs UniversityCompletedDuchenne Muscular Dystrophy (DMD)Turkey
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Solid Biosciences Inc.CompletedDuchenne Muscular DystrophyUnited States
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Assistance Publique - Hôpitaux de ParisNational Research Agency, FranceCompletedRheumatoid Arthritis | Uveitis | Vasculitis | Type 1 Diabetes | Crohn's Disease | Myositis | Healthy Volunteer | Ankylosing Spondylitis | FMF | Systemic Lupus Erythematosus/Antiphospholipid Syndrome | Cryopyrin-Associated Periodic Syndromes /TNF-receptor Associated Periodic Syndrome | Ulcerative Rectocolitis | Unclassified...France
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Ambulation Difficulty | Ambulation Disorder, NeurologicTurkey
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Daiichi Sankyo Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyJapan
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IRCCS San Camillo, Venezia, ItalyUniversita di Verona; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico and other collaboratorsEnrolling by invitationCalpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2AItaly
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey
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Terumo Medical CorporationCompletedBenign Prostatic Hyperplasia | Arteriovenous Malformations | Uterine Fibroid | Hypervascular TumorsUnited States
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy 1Netherlands
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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DynacureTerminatedCentronuclear MyopathyFrance, Netherlands, United Kingdom, Belgium, Denmark, Germany
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Noel JabbourNational Institute on Deafness and Other Communication Disorders (NIDCD)TerminatedCleft Palate | Tube Disorders Eustachian | Velopharyngeal Incompetence Due to Cleft Palate | Velopharyngeal InsufficiencyUnited States
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Sarepta Therapeutics, Inc.Nationwide Children's HospitalCompleted
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Brock UniversityCompletedMultiple Sclerosis | Inflammation | Muscular Dystrophies | Spinal Cord Injuries | Diet HabitCanada
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Vastra Gotaland RegionEnrolling by invitationMusculoskeletal Diseases | Neuromuscular Diseases | Centronuclear Myopathy | Nemaline Myopathy | Congenital Myopathy | Myosin Storage MyopathySweden
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Umeå UniversityEnrolling by invitation
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Élise DuchesneMuscular Dystrophy CanadaCompletedAutosomal Recessive Spastic Ataxia of Charlevoix-SaguenayCanada
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Universidad de AlmeriaCompletedNeurologic Disorder | Pediatric Disorder | Duchenne | Sensorimotor Disorder NosSpain
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Taipei Medical University Shuang Ho HospitalUniversity of Southern CaliforniaEnrolling by invitationChronic Kidney Diseases | Autosomal Dominant Polycystic Kidney DiseaseTaiwan
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University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
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University of Castilla-La ManchaUniversidad San Jorge; Hospital Nacional de Parapléjicos de ToledoCompletedMuscle Tone AbnormalitiesSpain
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National Neuroscience InstituteNanyang Technological University; Institute for Infocomm Research; Institute... and other collaboratorsActive, not recruitingMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Tetraplegia | Tetraplegia/Tetraparesis | Locked-in SyndromeSingapore
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Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
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Santhera PharmaceuticalsNo longer availableDuchenne Muscular DystrophyUnited States
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Alexandria UniversityCompletedMuscle Weakness | Neck Pain | Forward Head Posture | Neck Syndrome | Brace | Deformity of Spine | Deformity | Postural KyphosisEgypt
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Edgewise Therapeutics, Inc.CompletedNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Healthy VolunteerUnited States
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Cairo UniversityCompletedMuscular Dystrophy, Duchenne TypeEgypt
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Gazi UniversityCompletedPrimary Ciliary DyskinesiaTurkey
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Hacettepe UniversityCompletedPrimary Ciliary Dyskinesia | Kartagener Syndrome | Immotile Cilia SyndromeTurkey
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Galapagos NVTerminatedAutosomal Dominant Polycystic Kidney DiseaseBelgium, Netherlands, Italy, Spain, Czechia, Germany, Poland
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University of Colorado, DenverPKD FoundationCompletedPolycystic Kidney, Autosomal DominantUnited States
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GenethonActive, not recruitingLGMD2IDenmark, France, United Kingdom
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PfizerCompletedDuchenne Muscular DystrophyChina
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ML Bio Solutions, Inc.Virginia Commonwealth UniversityCompletedMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, Denmark
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NRG OncologyNational Cancer Institute (NCI)Active, not recruitingStage II Prostate Adenocarcinoma | Stage III Prostate Adenocarcinoma | Stage I Prostate AdenocarcinomaUnited States, Canada, Puerto Rico
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Synchron Medical, Inc.WithdrawnParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Neurologic Disorder | Spinal Muscular Atrophy | Spinal Cord Injury | Stroke, Lacunar | Upper Limb Injury | Paralysis; Stroke | Stroke, BrainstemAustralia
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Delta University for Science and TechnologyCompletedIdiopathic Spinal DeformitiesEgypt
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National Taipei University of Nursing and Health...Taipei Veterans General Hospital, Taiwan; Taiwan Nurses AssociationEnrolling by invitationArteriovenous Fistula | Isometric ExerciseTaiwan
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ReveraGen BioPharma, Inc.University of Pittsburgh; Newcastle University; European Union; Cooperative International...CompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, United Kingdom, Spain, Netherlands, Sweden, Czechia, Australia, Greece, Israel
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Barrow Neurological InstituteALS Association; Muscular Dystrophy Association; Synapse BiomedicalCompletedAmyotrophic Lateral Sclerosis (ALS)United States
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Nippon Shinyaku Co., Ltd.Active, not recruiting
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Institut de Myologie, FranceDynacureCompletedCentronuclear MyopathyFrance, Belgium, Germany, Italy, Spain
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Haukeland University HospitalExtrastiftelsenCompleted
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ENCellCompletedDuchenne Muscular DystrophyKorea, Republic of