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- US Clinical Trials Registry
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Search clinical trials for: Glycogen Storage Disorders
Total 146189 results
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Duke UniversityWithdrawnPompe Disease (Late-onset)United States
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Idorsia Pharmaceuticals Ltd.CompletedFabry DiseaseUnited States, Spain, Belgium, Australia, Austria, Canada, Germany, Ireland, Italy, Netherlands, Norway, Poland, Switzerland, United Kingdom
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Ari ZimranPfizerActive, not recruitingGaucher Disease, Type 3Israel, Turkey, India
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Talaris Therapeutics Inc.Duke UniversityNo longer availableMetachromatic LeukodystrophyUnited States
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseCanada, Russian Federation, Tunisia
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CENTOGENE GmbH RostockTerminatedDeafness | Immunodeficiency | Mental Retardation | Gingival Hypertrophy | Skeletal Abnormalities | Facial DysmorphismGermany, Switzerland
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University of UtahGenzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States
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ActelionCompleted
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TakedaCompletedMucopolysaccharidosis (MPS)Brazil
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Seattle Children's HospitalCompletedMental Health Disorders | Suicide or Selfinflicted Injury by Firearms and ExplosivesUnited States
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REGENXBIO Inc.CompletedMucopolysaccharidosis IIBrazil, United States, United Kingdom
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SanofiCompletedGaucher Disease | SplenomegalyFrance
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International Centre for Diarrhoeal Disease Research...University of California, Berkeley; Emory University; University of California... and other collaboratorsActive, not recruiting
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIChina
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IRCCS Fondazione Stella MarisCompletedHereditary Spastic ParaparesisItaly
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Genzyme, a Sanofi CompanyTerminatedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Israel
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University of FloridaLacerta TherapeuticsCompletedPompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedPompe Disease | Glycogen Storage Disease Type II (GSD II)United States, Russian Federation, United Kingdom, Bulgaria, India, Ukraine
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
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University Medical Center GroningenUltragenyx Pharmaceutical IncCompletedGlycogen Storage Disease Type IANetherlands
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ShireCompletedGaucher DiseaseUnited States, Spain, United Kingdom, Israel
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Reneo Pharma LtdCompletedMcArdle DiseaseSpain, United Kingdom
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Institut National de la Santé Et de la Recherche...Assistance Publique - Hôpitaux de Paris; European Leukodystrophy AssociationActive, not recruitingMetachromatic LeukodystrophyFrance
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Areeg El-GharbawyUltragenyx Pharmaceutical IncCompletedGlycogen Storage Disease Type IUnited States
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Amicus TherapeuticsCompletedFabry DiseaseUnited Kingdom, United States
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Chiesi SA/NVEnrolling by invitationNephropathic CystinosisBelgium
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Idorsia Pharmaceuticals Ltd.CompletedGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Gaucher Disease, Type 2 | AB Variant Gangliosidosis GM2United States, Spain, Germany, Italy, Belgium, Brazil, France, Portugal, Switzerland, United Kingdom
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Manchester University NHS Foundation TrustNorfolk and Norwich University Hospitals NHS Foundation TrustCompletedPulmonary SarcoidosisUnited Kingdom
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Duke UniversityCompleted
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Manchester University NHS Foundation TrustNorthern Care Alliance NHS Foundation TrustCompletedFabry DiseaseUnited Kingdom
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Massachusetts General HospitalCompletedFabry Disease | Mitochondrial Disease | Small Fiber Neuropathy | Ehlers Danlos SyndromeUnited States
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Children's Hospital of Fudan UniversityFirst Affiliated Hospital, Sun Yat-Sen University; Wuhan Union Hospital, China and other collaboratorsWithdrawn
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IRCCS Eugenio MedeaUniversity of Pisa; University of MessinaCompleted
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Hasan Kalyoncu UniversityCompleted
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REGENXBIO Inc.Enrolling by invitation
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Cyclo Therapeutics, Inc.CompletedNiemann-Pick Disease, Type C1Israel, Sweden, United Kingdom
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University of DundeeUniversity of OxfordCompletedEvaluation of Lithium as a Glycogen-Synthase-Kinase-3 (GSK-3) Inhibitor in Mild Cognitive ImpairmentMild Cognitive Impairment
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ShireCompletedFabry DiseaseCanada, United States
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Duke UniversityCompleted
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Vtesse, LLC, a Mallinckrodt Pharmaceuticals CompanyCompletedNiemann-Pick Disease, Type C1United States
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ShireCompleted
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Genzyme, a Sanofi CompanyCompletedPompe DiseaseBelgium, United States, Czechia, Germany, Italy, Taiwan
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Duke UniversityGenzyme, a Sanofi CompanyCompletedNeuropathy | Myopathy | Glycogen Storage Disease Type II (Late-onset Pompe Disease)United States
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ShireCompletedGaucher Disease, Type 1Israel, Paraguay, Argentina, Russian Federation, Tunisia
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ShireCompleted
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ShireCompleted
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ShireCompletedMetachromatic Leukodystrophy (MLD)Denmark
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CEN BiotechTakeda; BioClinica, Inc.Completed
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ShireCompletedGaucher DiseaseIsrael, Romania, Serbia