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Search clinical trials for: Lysosomal Storage Disease
Total 382007 results
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ShireCompleted
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Genzyme, a Sanofi CompanyCompletedPompe DiseaseBelgium, United States, Czechia, Germany, Italy, Taiwan
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Wuerzburg University HospitalTakedaEnrolling by invitationLysosomal Storage Diseases | Fabry Disease | Fabry Disease, Cardiac Variant | HCM - Hypertrophic Cardiomyopathy | Anderson Fabry DiseaseGermany
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Duke UniversityGenzyme, a Sanofi CompanyCompletedNeuropathy | Myopathy | Glycogen Storage Disease Type II (Late-onset Pompe Disease)United States
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University of FloridaBioMarin PharmaceuticalCompleted
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ShireCompletedGaucher Disease, Type 1Israel, Paraguay, Argentina, Russian Federation, Tunisia
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ShireCompleted
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ShireCompleted
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ShireCompletedMetachromatic Leukodystrophy (MLD)Denmark
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CEN BiotechTakeda; BioClinica, Inc.Completed
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ShireCompletedGaucher DiseaseIsrael, Romania, Serbia
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Cyclo Therapeutics, Inc.Active, not recruitingNiemann-Pick Disease, Type C1United States
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ShireCompletedMetachromatic Leukodystrophy (MLD)Australia, Denmark, Japan, France, Germany
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ShireTerminatedSanfilippo SyndromeNetherlands, United Kingdom
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ShireCompletedMucopolysaccharidosis (MPS)United Kingdom, Netherlands
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ShireCompletedLate Infantile Metachromatic LeukodystrophyDenmark
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ShireCompleted
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ShireQuintiles, Inc.Completed
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ShireCompletedSanfilippo Syndrome Type AUnited States
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ShireCompletedGaucher Disease, Type 3Egypt, India, Tunisia
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ShireCompletedHunter SyndromeSpain, United States, Canada, United Kingdom, France, Australia, Mexico
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ShireTerminatedSanfilippo Syndrome | Mucopolysaccharidosis (MPS)United States, United Kingdom, Spain, Germany, France, Italy, Netherlands
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis II (MPS II)United States, France, United Kingdom, Germany, Sweden, Spain, Brazil, Canada, Italy, Romania
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ShireCompletedGaucher Disease, Type 1United States, Israel, Argentina, India, Korea, Republic of, Paraguay, Poland, Russian Federation, Spain, Tunisia, United Kingdom
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ShireCompletedMucopolysaccharidosis IIUnited States, United Kingdom, Brazil, Germany
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ShireCompletedGaucher DiseaseUnited States, Israel, United Kingdom, Poland, Spain
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ShireCompletedFabry DiseaseUnited States, United Kingdom, Australia, Czechia, Finland, Paraguay, Poland, Slovenia
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ShireCompletedHunter SyndromeUnited States, United Kingdom
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ShireCompleted
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ShireTerminatedLate Infantile Metachromatic LeukodystrophyDenmark
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ShireCompletedGaucher Disease, Type 1Spain, Israel, United States, India, Paraguay, United Kingdom, Russian Federation, Tunisia, Argentina
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ShireCompletedSanfilippo SyndromeUnited States, Spain, United Kingdom, Argentina, France, Germany, Italy, Netherlands
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ShireCompletedHunter SyndromeUnited Kingdom, United States, Brazil
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ShireCompletedFabry DiseaseUnited States, Slovenia, Australia, Finland, Poland, Czechia, United Kingdom
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ShireCovance; PRA Health Sciences; PharmaNetCompletedMucopolysaccharidosis II | Hunter Syndrome | MPS IIBrazil, Poland, Taiwan
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Melbourne HealthSanofiWithdrawnLysosomal Storage Diseases | Fabry Disease | Niemann-Pick Disease, Type C | Gaucher DiseaseAustralia
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ShireCompletedFabry DiseaseFinland, Sweden, Germany, Belgium, Czechia, Denmark
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ShirePharmaNet; Nextrials, Inc.WithdrawnLeukodystrophy, Globoid Cell
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CENTOGENE GmbH RostockCompletedLysosomal Storage Diseases | Sphingolipidoses | Gaucher DiseaseAlbania, Greece, India, Israel, Morocco, Pakistan, Spain
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ShireNo longer available
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ShireApproved for marketingGaucher Disease, Type 1United States
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University of FloridaAmicus TherapeuticsCompletedLysosomal Storage Diseases | Glycogen Storage Disease Type II | Pompe DiseaseUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsTerminatedTay-Sachs Disease | Sandhoff Disease | GM1 Gangliosidoses | GM2 GangliosidosesUnited States
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CENTOGENE GmbH RostockShire Human Genetic Therapies, Inc.CompletedFabry Disease | Cerebrovascular AccidentAustria, Croatia, France, Germany, Poland, Portugal, Georgia
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CENTOGENE GmbH RostockShire Human Genetic Therapies, Inc.CompletedCerebrovascular AccidentAustria, Belgium, Croatia, Finland, France, Georgia, Germany, Ireland, Italy, Malta, Poland, Portugal, Spain, United Kingdom
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CENTOGENE GmbH RostockWithdrawnStroke, Acute | Cerebrovascular Accident | Cerebral StrokeGermany
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CENTOGENE GmbH RostockCompletedMorquio DiseasePakistan
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CENTOGENE GmbH RostockCompletedFabry Disease | Anderson-Fabry Disease | Fabry´s DiseaseArgentina, Belgium, Croatia, Czechia, Denmark, France, Germany, United Kingdom
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CENTOGENE GmbH RostockCompleted