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Search clinical trials for: cerebral metabolism
Total 59233 results
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Andrea GropmanChildren's National Research InstituteCompletedOrnithine Transcarbamylase Deficiency
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Phrapokklao Hospital,ThailandCompletedStroke | Hypertension | Type2diabetesThailand
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Khondrion BVJulius Clinical; ProPharma Group; CertaraCompletedMitochondrial Diseases | Mitochondrial DNA tRNALeu(UUR) m.3243A<G Mutation | Maternally Inherited Diabetes and Deafness (MIDD) | Mitochondrial Encephalomyopathy, Lactic Acidosis and Stroke Like Episodes (MELAS) | Chronic Progressive External Ophthalmoplegia (CPEO)Netherlands, Denmark, United Kingdom, Germany
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SanofiCompletedFabry DiseaseUnited Arab Emirates
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Loma Linda UniversityEnrolling by invitationTraumatic Brain InjuryUnited States
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metaX Institut fuer Diatetik GmbHBirmingham Children's HospitalCompletedPhenylketonurias | Hyperphenylalaninaemia | Tetrahydrobiopterin DeficiencyUnited Kingdom
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University of North Carolina, Chapel HillNational Human Genome Research Institute (NHGRI); East Carolina University; Mission...Active, not recruitingNeuromuscular Diseases | Movement Disorders | Intellectual Disability | Autism Spectrum Disorder | Microcephaly | Hearing Loss | Genetic Disease | Inborn Errors of Metabolism | Epilepsy; Seizure | Brain Malformation | Hypotonia | Development Delay | Chromosome Abnormality | Dysmorphic Features | Skeletal Dysplasia | Congenital... and other conditionsUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II Pompe DiseaseUnited States, Belgium, Denmark, France, Germany, Netherlands, United Kingdom
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Maastricht University Medical CenterThe Peanut Institute Foundation (TPIF)Active, not recruitingCerebral Blood Flow | Cognitive Performance | Brain Vascular Function | Brain Insulin SensitivityNetherlands
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Emma Marie Caroline SlackUniversity Children's HospitalCompletedInborn Errors of Metabolism | Propionic Aciduria | Methylmalonic Aciduria | Urea Cycle DisorderSwitzerland
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Marinella TemprosaNational Institute on Aging (NIA)Enrolling by invitationDiabetes | Dementia | PreDiabetes | Alzheimer Disease | Dementia, VascularUnited States
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University of Texas Southwestern Medical CenterEnrolling by invitationBrain MetabolismUnited States
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Hacettepe UniversityCompletedCaregiver Burden | Life Stress | Psychological Well-BeingTurkey
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Assistance Publique - Hôpitaux de ParisCompleted
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Azafaros A.G.Active, not recruitingNiemann-Pick Disease, Type C | GM2 GangliosidosisBrazil
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TakedaActive, not recruiting
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SanofiActive, not recruitingGaucher's Disease Type III | Gaucher's Disease Type ICanada, Argentina, France, Italy, Japan, Russian Federation, Spain, Sweden, Turkey, United Kingdom
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Children's Hospital of Orange CountyActive, not recruitingNeuronal Ceroid-Lipofuscinoses | Neuronal Ceroid Lipofuscinosis CLN2 | Spinocerebellar Ataxia, Autosomal Recessive 7United States
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Lumos PharmaActive, not recruitingGrowth Hormone DeficiencyUnited States, Australia, Israel, New Zealand, Poland, Ukraine
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Vitaflo International, LtdCompleted
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Vitaflo International, LtdJohannes Gutenberg University Mainz; Kreiskliniken ReutlingenCompleted
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Vitaflo International, LtdCompletedAlkaptonuria | Tyrosinemias | Tyrosinemia, Type I | Tyrosinemia, Type II | Tyrosinemia, Type IIIUnited Kingdom
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Vitaflo International, LtdOregon Health and Science UniversityCompleted
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Vitaflo International, LtdArla FoodsCompletedPhenylketonuriasUnited Kingdom, Denmark
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustCompletedPhenylketonuria | Inborn Errors of MetabolismUnited Kingdom
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Vitaflo International, LtdCompleted
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Vitaflo International, LtdActive, not recruiting
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Vitaflo International, LtdActive, not recruiting
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Masonic Cancer Center, University of MinnesotaTerminatedSickle Cell Disease | Thalassemia | Cerebral Adrenoleukodystrophy | Inherited Metabolic Disorders | High Risk Hematologic DisordersUnited States
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SanofiCompletedPompe Disease | Mucopolysaccharidosis Type I (MPS I)Italy
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OPKO Health, Inc.Active, not recruitingSafety and Efficacy Phase 3 Study of Long-acting hGH (MOD-4023) in Growth Hormone Deficient ChildrenPediatric Growth Hormone DeficiencyIsrael, United States, India, Korea, Republic of, Australia, Taiwan, Spain, Argentina, Belarus, Bulgaria, Canada, Colombia, Georgia, Greece, Mexico, New Zealand, Poland, Russian Federation, Ukraine, United Kingdom
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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ShireTerminated
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Central Jutland Regional HospitalOdense University HospitalEnrolling by invitationHypertension | Diabetes | Peripheral Arterial Disease | Aging | Carotid Atherosclerosis | Aortic Aneurysm, Abdominal | Arrythmia | Mass ScreeningDenmark
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Ain Shams UniversityCompletedMyocardial Infarction | Diabetes Mellitus, Type 2 | Myocardial Remodeling, VentricularEgypt
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Canadian Network for Observational Drug Effect...Canadian Institutes of Health Research (CIHR); Drug Safety and Effectiveness...CompletedMyocardial Infarction | Heart Failure | Ischemic Stroke | Type2 Diabetes | Cardiovascular Death | All-Cause MortalityCanada
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BioMarin PharmaceuticalActive, not recruitingPhenylketonuria (PKU)United States, Germany
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Genzyme, a Sanofi CompanyActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States, Argentina, Czechia, Portugal, Russian Federation, Turkey, United Kingdom, Brazil, France, Germany, Italy, Japan, Spain
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SanofiCompleted
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TakedaCompleted
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Passage Bio, Inc.SuspendedLeukodystrophy, Globoid CellUnited States, Brazil, Netherlands, United Kingdom, Canada, Israel
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AVROBIOTerminatedGaucher DiseaseUnited States, Canada
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Orchard TherapeuticsOspedale San RaffaeleActive, not recruitingLysosomal Storage Diseases | Metachromatic LeukodystrophyItaly
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TakedaActive, not recruiting
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Mandos LLCTerminatedNiemann-Pick Type C DiseaseUnited States
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Johns Hopkins UniversityEnrolling by invitationEpilepsy | Coronary Disease | Cardiovascular Disease | Hypercholesterolemia | Heart Disease | Cerebrovascular Disease | Seizure | Carotid Intimal Medial Thickness 1United States
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Travere Therapeutics, Inc.Active, not recruiting