- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials Sponsored by FDA Office of Orphan Products Development
Total 141 results
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University of MichiganCompleted
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University of PennsylvaniaTerminatedOrnithine Transcarbamylase Deficiency Disease
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University of TennesseeFDA Office of Orphan Products DevelopmentCompleted
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University of ArizonaFDA Office of Orphan Products DevelopmentTerminated
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Boston Children's HospitalFDA Office of Orphan Products DevelopmentActive, not recruiting
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Aegerion Pharmaceuticals, Inc.FDA Office of Orphan Products DevelopmentCompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, South Africa
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National Jewish HealthCompletedMycobacterium Avium-intracellulare Infection
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Johns Hopkins UniversityCompletedCerebral HemorrhageUnited States
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Holles Laboratories, Inc.Completed
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NeuroHealing Pharmaceuticals Inc.FDA Office of Orphan Products DevelopmentSuspended
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The Cleveland ClinicCompleted
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FDA Office of Orphan Products DevelopmentBoston Children's HospitalCompleted
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Johns Hopkins UniversityCompletedEpilepsy | Cysticercosis
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Bellus Health IncFDA Office of Orphan Products DevelopmentCompletedGastrointestinal Diseases | Kidney Diseases | Rheumatoid Arthritis | Nephrotic Syndrome | Secondary (AA) Amyloidosis | Familial Mediterranean SyndromeUnited States, Israel, Finland, France, Italy, Lithuania, Netherlands, Poland, Russian Federation, Spain, Turkey, United Kingdom
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Boston Children's HospitalFDA Office of Orphan Products DevelopmentTerminated
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Emmaus Medical, Inc.FDA Office of Orphan Products DevelopmentCompletedSickle Cell Anemia | ThalassemiaUnited States
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IWK Health CentreCompletedPertussis | Whooping Cough
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Ohio State UniversityCompletedMuscular Dystrophy, Facioscapulohumeral
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FDA Office of Orphan Products DevelopmentLeadiant Biosciences, Inc.Completed
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Boston Children's HospitalCompletedSickle Cell AnemiaUnited States
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The Cleveland ClinicTerminated
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Seattle Children's HospitalCompletedPain | Infant, Newborn, Diseases
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Massachusetts General HospitalCompleted
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University of North CarolinaCompleted
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FDA Office of Orphan Products DevelopmentChildren's Hospital of PhiladelphiaCompleted
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FDA Office of Orphan Products DevelopmentUniversity of North CarolinaCompleted
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Children's Hospital of PhiladelphiaCompleted
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Children's Hospital of PhiladelphiaCompleted
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Medical College of WisconsinFDA Office of Orphan Products DevelopmentTerminatedHemangiomaUnited States
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University of North CarolinaCompletedSickle Cell AnemiaUnited States
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FDA Office of Orphan Products DevelopmentUniversity of Massachusetts, WorcesterCompletedJuvenile Rheumatoid Arthritis
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University of North CarolinaCompletedOsteoporosis | Cystic FibrosisUnited States
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Children's Hospital Los AngelesCompletedThrombosis | Heparin-induced ThrombocytopeniaUnited States
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Brigham and Women's HospitalCompletedErythropoietic Protoporphyria
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FDA Office of Orphan Products DevelopmentCase Western Reserve UniversityCompleted
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FDA Office of Orphan Products DevelopmentCase Western Reserve UniversityCompleted
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Case Western Reserve UniversityTerminated
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M.D. Anderson Cancer CenterCompletedLymphoproliferative Disorders | Leukemia | Hematologic Neoplasms | Leukemia, Lymphocytic, ChronicUnited States
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George BrewerFDA Office of Orphan Products DevelopmentCompletedPrimary Biliary CirrhosisUnited States
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FDA Office of Orphan Products DevelopmentUniversity of Illinois at ChicagoCompleted
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University of California, San DiegoCompletedLactic AcidosisUnited States
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Memorial Hospital of Rhode IslandCompleted
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Retina Foundation of the SouthwestCompleted
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FDA Office of Orphan Products DevelopmentMedical University of South CarolinaCompleted
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California Department of Health ServicesCompletedBotulism | Infant BotulismUnited States
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University of California, San FranciscoFDA Office of Orphan Products DevelopmentCompleted
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University of California, San FranciscoFDA Office of Orphan Products DevelopmentTerminatedPersistent Corneal Epithelial Defects
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State University of New YorkCompletedDupuytren's Contracture
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State University of New YorkCompletedDupuytren's ContractureUnited States
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Children's Hospital Medical Center, CincinnatiCompletedTourette Syndrome