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Search clinical trials for: Inborn errors of Metabolism
Total 434386 results
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...Recruiting
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UniQure Biopharma B.V.RecruitingFabry DiseaseUnited States
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S.LAB (SOLOWAYS)Center of New Medical TechnologiesRecruiting
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Brunel UniversityRoyal Free Hospital NHS Foundation TrustRecruiting
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Chung-Hsing WangSanofiNot yet recruiting
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iECURE, Inc.RecruitingUrea Cycle Disorders, Inborn | Ornithine Transcarbamylase Deficiency | Ornithine Transcarbamylase Deficiency Disease | Ornithine Carbamoyltransferase Deficiency (Disorder)United Kingdom
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Hospices Civils de LyonNot yet recruitingX-Linked Hypophosphatemic Rickets
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Travere Therapeutics, Inc.Recruiting
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UNICANCERServierNot yet recruitingMetastatic Colorectal Cancer | Metastatic Gastroesophageal Adenocarcinoma | DPD Deficiency
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Swedish Orphan BiovitrumRecruitingHereditary Tyrosinemia, Type IChina
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Hospices Civils de LyonRecruitingPatients With PH1 Treated With Lumasiran in FranceFrance
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University of CambridgeSanofiRecruiting
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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Shanghai Vitalgen BioPharma Co., Ltd.RecruitingGlutaric Acidemia Type I | Glutaric Aciduria Type IChina
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University of PennsylvaniaRecruitingLCAT DeficiencyUnited States
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Rocket Pharmaceuticals Inc.Recruiting
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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Diakonhjemmet HospitalRecruiting
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Children's Hospital of Fudan UniversityNot yet recruiting
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Thammasat UniversityNot yet recruiting
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New York Stem Cell Foundation Research InstituteRecruitingPTSD | Multiple Sclerosis | Cervical Cancer | Diabetes Mellitus, Type 2 | Diabetes Mellitus | Diabetes | Macular Degeneration | Diabetes Mellitus, Type 1 | Parkinson Disease | Amyotrophic Lateral Sclerosis | Dementia | Ovarian Cancer | Alzheimer Disease | ALS | Vulvar Cancer | Post Traumatic Stress Disorder | Lewy Body Disease and other conditionsUnited States
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Kyowa Kirin Korea Co., Ltd.RecruitingFGF23-related Hypophosphataemic Rickets and OsteomalaciaKorea, Republic of
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Grace Science, LLCRecruitingNGLY1 DeficiencyUnited States
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Hospital Affiliated to the Institute of Neurology...Not yet recruitingHepatolenticular Degeneration; WilsonChina
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SanofiPulse Infoframe Ltd.RecruitingNiemann-Pick Diseases | Acid Sphingomyelinase DeficiencyUnited States
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McGill University Health Centre/Research Institute...Canadian Institutes of Health Research (CIHR)RecruitingZellweger Spectrum DisorderCanada
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University of California, Los AngelesNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Not yet recruiting
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Chiesi Farmaceutici S.p.A.Not yet recruiting
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis Type IIIAUnited States
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Huashan HospitalNot yet recruitingPompe Disease (Late-onset)China
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Assiut UniversityNot yet recruiting
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ETH ZurichUniversity of Zurich; Agroscope Liebefeld-Posieux Research Station ALP; Swiss...RecruitingLactose IntoleranceSwitzerland
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Minoryx Therapeutics, S.L.RecruitingX-linked AdrenoleukodystrophyFrance
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...Not yet recruiting
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Qilu Hospital of Shandong UniversityRecruitingFabry Disease | Hypertrophic Cardiomyopathy | Left Ventricular HypertrophyChina
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Verve Therapeutics, Inc.Not yet recruitingHeterozygous Familial Hypercholesterolemia | Premature Coronary Heart Disease
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He HuangLingyi Biotech Co., Ltd.Recruiting
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University of BonnRecruitingHypophosphatasiaGermany
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy
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Orchard TherapeuticsRecruitingMPS-IH (Hurler Syndrome)Netherlands, United States, Italy, United Kingdom
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Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Netherlands
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ModernaTX, Inc.RecruitingPhenylketonuriaUnited States, Australia
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Jiangsu HengRui Medicine Co., Ltd.Not yet recruitingGout With Hyperuricemia in Adults
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Assistance Publique - Hôpitaux de ParisRecruiting
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Azienda Ospedaliero-Universitaria di ModenaRecruitingIron Overload | Hemochromatosis | Thalassemia Major | Thalassemia Intermedia | EndocrinopathyItaly
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McMaster UniversityNot yet recruitingObesity | Lysosomal Storage Diseases | Muscle Loss | Glycogen Storage Disease Type II | Pompe Disease | Nutrition Poor | Glycogen Storage Disease Type II, Adult | Glycogen Storage Disease Type II Late Onset
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Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand, Canada
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Martin DichgansRecruitingCerebral Amyloid AngiopathyGermany
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First Affiliated Hospital Xi'an Jiaotong UniversityRecruitingHomozygous Familial HypercholesterolemiaChina