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Search clinical trials for: Late Onset Lysosomal Acid Lipase Deficiency (CESD)
Total 42347 results
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedTay Sachs Disease | Sandhoff Disease | Late Onset Tay Sachs DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe DiseaseUnited States
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Genzyme, a Sanofi CompanyApproved for marketingGlycogen Storage Disease Type II | Glycogenosis 2
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States, Israel, France, United Kingdom
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, Taiwan, Israel, United Kingdom, France
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUnknown
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Massachusetts General HospitalAlexion PharmaceuticalsUnknownCholesterol Ester Storage Disease | Lysosomal Acid Lipase DeficiencyUnited States
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Assy NimerUnknownNon-alcoholic Fatty Liver Disease | Cholesterol Ester Storage DiseaseIsrael
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The Hospital for Sick ChildrenCompletedGangliosidoses, GM2 | Tay-Sachs Disease | Sandhoff DiseaseCanada
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GeneCradle IncRecruitingPompe Disease (Late-onset)China
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Chung-Hsing WangSanofiNot yet recruiting
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iECURE, Inc.RecruitingUrea Cycle Disorders, Inborn | Ornithine Transcarbamylase Deficiency | Ornithine Transcarbamylase Deficiency Disease | Ornithine Carbamoyltransferase Deficiency (Disorder)United Kingdom
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Richard FryeAutism Discovery and Treatment FoundationRecruitingEpilepsy | Neurodevelopmental Disorders | Autism Spectrum Disorder | Down Syndrome | Mitochondrial Encephalomyopathies | Pediatric Acute-Onset Neuropsychiatric Syndrome | Cerebral Folate Deficiency | Pediatric Autoimmune Neuropsychiatric Disorder Associated With Streptococcal InfectionUnited States
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Princess Anna Mazowiecka Hospital, Warsaw, PolandMedical University of WarsawNot yet recruitingNephrolithiasis | Vitamin D Deficiency | Metabolic Bone Disease | Osteopenia of Prematurity | Late-Onset Neonatal SepsisPoland
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SanofiPulse Infoframe Ltd.RecruitingNiemann-Pick Diseases | Acid Sphingomyelinase DeficiencyUnited States
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Huashan HospitalNot yet recruitingPompe Disease (Late-onset)China
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National Institute for Mother and Child Health...Marie Curie Emergency Children's Hospital, Bucharest; Victor Gomoiu Children...RecruitingChronic Granulomatous DiseaseRomania
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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Fundación Española de Hematología y HemoterapíaRecruitingGaucher Disease | Acid SphingoMyelinase DeficiencySpain
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ViiV HealthcareNot yet recruitingHIV Infections | HIVSpain, Poland, France, Israel, Belgium, Portugal, Germany, Italy, Argentina, Greece, Japan, Ireland, Switzerland, United Kingdom, Denmark, Sweden, Mexico
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Fondazione Don Carlo Gnocchi OnlusAssociazione Italiana Glicogenosi (AIG); Associazione Riabilitatori Insufficienza... and other collaboratorsRecruitingGlycogen Storage Disease Type II | Pompe Disease (Late-onset)Italy
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Eline C. B. EskesRecruitingAsmd, Visceral TypeNetherlands
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Hospital Universitari Vall d'Hebron Research InstituteRecruiting
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Fundación Española de Hematología y HemoterapíaRecruitingNiemann-Pick Diseases | Gaucher Disease | Splenomegaly | Acid SphingoMyelinase Deficiency | ASMDSpain
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Seventh Medical Center of PLA General HospitalGeneCradle Therapeutics, IncRecruiting
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingLate-Onset Pompe Disease | Lysosomal DiseaseUnited States
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University of Roma La SapienzaAlexion PharmaceuticalsRecruitingNon-Alcoholic Fatty Liver DiseaseItaly
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SanofiRecruitingAcid Sphingomyelinase Deficiency (ASMD)France
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LMU KlinikumRecruitingPompe Disease (Late-onset) | FSHD | Spinal Muscular Atrophy Type 3 | Inclusion Body MyositisGermany
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The Aurum Institute NPCJohns Hopkins University; Weill Medical College of Cornell University; University...RecruitingPregnancy | HIV Seropositivity | Tuberculosis InfectionSouth Africa
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University of Erlangen-Nürnberg Medical SchoolRecruitingPompe Disease (Late-onset) | Pompe Disease | Pompe's Disease Juvenile Onset | Pompe Disease Infantile-OnsetGermany
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National Taiwan University HospitalRecruiting
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Rigshospitalet, DenmarkDanish Research Center for Magnetic ResonanceRecruitingGlycogen Storage Disease | Pompe Disease (Late-onset) | McArdle DiseaseDenmark
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SanofiRecruitingAcid SphingoMyelinase Deficiency | Gaucher Disease, SplenomegalyFrance
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Children's Hospital Medical Center, CincinnatiUniversity of Cincinnati; Cloudnine Hospital, Bangalore, IndiaRecruitingLate-Onset Neonatal SepsisIndia
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Université de SherbrookeInstitut de Recherches Cliniques de MontrealRecruitingLipoprotein Lipase DeficiencyCanada
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, United Kingdom
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Amicus TherapeuticsRecruitingPompe Disease (Late-onset)United States, Taiwan, Japan, Australia, Canada
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University of Colorado, DenverNational Heart, Lung, and Blood Institute (NHLBI); Duke University; National...RecruitingObesity | AsthmaUnited States
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Albert Einstein College of MedicineNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National...RecruitingGlucose Metabolism Disorders | Type 2 Diabetes Mellitus | Glucose, High BloodUnited States
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Children's Hospital of PhiladelphiaEli Lilly and Company; University of Pennsylvania; Takeda; National Institute of... and other collaboratorsRecruitingMucopolysaccharidoses | Leukoencephalopathies | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2... and other conditionsUnited States
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National Institute of Allergy and Infectious Diseases...Eunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingHIV InfectionUnited States, Puerto Rico, Argentina, Brazil, Haiti, Kenya, Malawi, South Africa, Tanzania, Thailand, Uganda, Zambia, Zimbabwe
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingPompe DiseaseUnited States
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...RecruitingEnd Stage Liver Disease | Mitochondrial Diseases | Acute Liver Failure | Respiratory Chain Deficiencies, Mitochondrial | Disorder of Fatty Acid OxidationUnited States, Canada
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Passage Bio, Inc.Active, not recruitingGM1 Gangliosidosis | GM1 Gangliosidosis, Type I | GM1 Gangliosidosis, Type 2 | Beta-Galactosidase-1 (GLB1) DeficiencyUnited States, Canada, United Kingdom, Turkey, Brazil
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Children's Hospital of PhiladelphiaIllumina, Inc.Active, not recruitingMucopolysaccharidoses | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2 Gangliosidosis | Zellweger... and other conditionsUnited States
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AEterna ZentarisNovo Nordisk A/SActive, not recruitingGrowth Hormone DeficiencyUnited States, Italy, Turkey, Georgia, Romania, Poland, Armenia, Germany, Serbia, Slovakia, Slovenia
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Massachusetts General HospitalActive, not recruiting
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II;Pompe's DiseaseCzechia, Taiwan, Belgium, Germany, Korea, Republic of, United States, Argentina, Australia, Austria, Brazil, Canada, Denmark, France, Hungary, Italy, Japan, Mexico, Netherlands, Poland, Portugal, Russian Federation, Spain, Switzerland, Turk... and more