- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Niemann-Pick Disease B
Total 492012 results
-
Alexion PharmaceuticalsCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited Kingdom, France, United States, Egypt, Ireland
-
Eunice Kennedy Shriver National Institute of Child...Washington University School of Medicine; Weill Medical College of Cornell...CompletedNeimann-Pick DiseaseUnited States
-
Masonic Cancer Center, University of MinnesotaCompletedNiemann-Pick Disease | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | GM1 Gangliosidosis | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Tay Sachs Disease | Sandhoff DiseaseUnited States
-
Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
-
National Eye Institute (NEI)CompletedNiemann Pick DiseasesUnited States, United Kingdom
-
KemPharm Denmark A/SCompletedNiemann-Pick Disease, Type CSpain, France, United Kingdom, Switzerland, Denmark, Poland, Italy, Germany
-
O & O Alpan LLCUnknownFabry Disease | Niemann-Pick Disease | Gaucher Disease | Pompe Disease | Lysosomal Storage DisordersUnited States
-
University Hospital, GrenobleTerminatedPsychiatric Adults PatientsFrance
-
Children's Hospital Los AngelesCompletedGranuloma | Anemia | Thrombocytopenia | Neutropenia | Sickle Cell Disease | Thalassemia | Niemann-Pick Disease | Wiskott-Aldrich Syndrome | Osteopetrosis | Fucosidosis | Chediak Higashi Syndrome | Hurler DiseaseUnited States
-
Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedNiemann-Pick Disease, Type CUnited States
-
Genzyme, a Sanofi CompanyCompletedHuman Acid Sphingomyelinase DeficiencyUnited Kingdom, United States
-
Genzyme, a Sanofi CompanyTerminatedNiemann-Pick Disease | Acid Sphingomyelinase DeficiencyUnited States
-
AldagenTerminatedMucopolysaccharidosis | Inborn Errors of Metabolism | Lysosomal Storage Disorders | Inherited Metabolic Diseases | Peroxisomal Storage DiseasesUnited States
-
Eunice Kennedy Shriver National Institute of Child...Washington University School of Medicine; University of Oxford; National Human...CompletedNiemann-Pick Disease, Type CUnited States
-
National Center for Complementary and Integrative...WithdrawnHyperglycemia | HIV Infections | Hypercholesterolemia | HypertriglyceridemiaUnited States
-
National Taiwan University HospitalCompleted
-
ActelionCompleted
-
Fred Hutchinson Cancer CenterNational Center for Complementary and Integrative Health (NCCIH)Completed
-
National Institute of Neurological Disorders and...CompletedBrain Neoplasm | Alzheimer's Disease | Niemann Pick DiseaseUnited States
-
Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
-
Vertex Pharmaceuticals IncorporatedNot yet recruiting
-
University of BonnRecruitingGiant Cell Arteritis | Polymyalgia RheumaticaGermany
-
Lund UniversityProbi ABNot yet recruiting
-
Ray Therapeutics, Inc.Not yet recruitingRetinitis PigmentosaUnited States
-
National Institute of Allergy and Infectious Diseases...National Institutes of Health (NIH); University of Washington; Harvard School... and other collaboratorsNot yet recruiting
-
First Affiliated Hospital of Zhejiang UniversityThe First Affiliated Hospital of Zhengzhou University; Shenzhen Second People... and other collaboratorsNot yet recruitingEmergencies | Airway Remodeling | Hypoxemia | Sedation ComplicationChina
-
Kuopio University HospitalNot yet recruiting
-
Riphah International UniversityRecruiting
-
Xinjiang Medical UniversityRecruitingCardiovascular Diseases | Coronary Artery Disease | Heart FailureChina
-
Mingfu WuPeking Union Medical College Hospital; Peking University Third Hospital; Southwest... and other collaboratorsRecruitingPelvic Organ Prolapse | Pelvic Floor DisordersChina
-
Akamis BioNot yet recruitingLocally Advanced Rectal Cancer (LARC)
-
Riphah International UniversityNot yet recruiting
-
Riphah International UniversityNot yet recruiting
-
Riphah International UniversityRecruiting
-
Elizabeth Austen LawsonNot yet recruitingOxytocin Deficiency | Arginine Vasopressin Deficiency
-
Istanbul University - Cerrahpasa (IUC)Not yet recruitingRheumatic Diseases | Pediatric ALL | Children, OnlyTurkey
-
Katrina Atef HabashyAssiut UniversityNot yet recruitingChronic Rhinosinusitis With Nasal Polyps
-
Riphah International UniversityRecruiting
-
Democritus University of ThraceRecruitingRefractive Errors | Cataract | Presbyopia | PseudophakiaGreece
-
Tongji HospitalThe First People's Hospital of Jingzhou; Wuhan Central Hospital; Wuhan No.1 Hospital and other collaboratorsRecruitingSystemic Lupus ErythematosusChina
-
Shanghai Chest HospitalNot yet recruiting
-
Riphah International UniversityNot yet recruiting
-
Riphah International UniversityRecruitingCervico-Brachial NeuralgiaPakistan
-
Assistance Publique - Hôpitaux de ParisNot yet recruitingBypass Bariatric SurgeryFrance
-
Kaplan Medical CenterRecruitingOsteoarthritis ThumbIsrael
-
Riphah International UniversityRecruiting
-
Istituto Ortopedico RizzoliI.R.C.C.S Ospedale Galeazzi-Sant'AmbrogioNot yet recruiting
-
Sven Schneider, MDNot yet recruitingAllergic Rhinitis | Allergic ConjunctivitisAustria
-
Merck Sharp & Dohme LLCGOG Foundation; European Network of Gynaecological Oncological Trial Groups...Not yet recruiting
-
Sun Yat-sen UniversityNot yet recruitingAtrial Fibrillation New Onset