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Search clinical trials for: Severe Congenital Neutropenia
Total 18023 results
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Editas Medicine, Inc.RecruitingSickle Cell Disease | HemoglobinopathiesUnited States, Canada
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Kamau TherapeuticsRecruitingSickle Cell DiseaseUnited States
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Mark Walters, MDUniversity of California, Berkeley; University of California, Los AngelesNot yet recruiting
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Hanmin LeeRecruitingCongenital Diaphragmatic HerniaUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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University of ChicagoRecruitingSickle Cell DiseaseUnited States
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Mitchell CairoRecruitingHodgkin Lymphoma | Sickle Cell Disease | Acute Leukemia | Beta-Thalassemia | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Diamond Blackfan Anemia | Amegakaryocytic Thrombocytopenia | KostmannUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Michael A BelfortBaylor College of MedicineRecruitingCongenital Diaphragmatic HerniaUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingMyelodysplastic Syndromes | Fanconi Anemia | Severe Aplastic AnemiaUnited States
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Rodrigo RuanoRecruitingBladder Outlet Obstruction | Lower Urinary Tract Obstructive Syndrome | Lower Urinary Tract Obstruction, Congenital | Bladder Outflow ObstructionUnited States
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Washington University School of MedicineRecruitingHemoglobinopathies | Bone Marrow Failure Syndromes | Metabolic Disorders | Non-malignant Disorders | Severe Sickle Cell Disease | Immunologic DisordersUnited States
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The University of Texas Health Science Center,...RecruitingCluster Headache | Trigeminal Neuralgia | Hemicrania Continua | Paroxysmal Hemicrania | SUNCT | Cluster Headaches and Other Trigeminal Autonomic CephalgiasUnited States
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Johns Hopkins UniversityRecruitingCongenital Diaphragmatic HerniaUnited States
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Children's Hospital of PhiladelphiaRecruitingFetoscopic Endoluminal Tracheal Occlusion in Severe Left Congenital Diaphragmatic Hernia (CHOP_FETO)Congenital Diaphragmatic Hernia | Pulmonary HypoplasiaUnited States
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Johns Hopkins UniversityRecruitingWounds and Injuries | Amputation | Amputation, Traumatic | Urologic Surgical Procedures, Male | Amputation, Traumatic/Surgery | Penis/Transplantation | Penis/Surgery | Penis/InjuriesUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingAplastic Anemia | Dyskeratosis CongenitaUnited States
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Children's Hospital Medical Center, CincinnatiMemorial Sloan Kettering Cancer Center; Fred Hutchinson Cancer CenterRecruitingFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Severe Marrow FailureUnited States
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Centre Hospitalier Universitaire, AmiensRecruitingArteriovenous MalformationsFrance, Belgium
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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Washington University School of MedicineRecruitingSevere Combined Immunodeficiency | Chronic Granulomatous Disease | DiGeorge Syndrome | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | X-linked Lymphoproliferative Syndrome | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | IPEX | Autoimmune Lymphoproliferative Syndrome | Common Variable... and other conditionsUnited States
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Cure CMDRecruitingEmery-Dreifuss Muscular Dystrophy | Congenital Myasthenic Syndrome | Limb-Girdle Muscular Dystrophy | Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency | Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy and Abnormal Glycosylation of Dystroglycan With Severe Epilepsy) and other conditionsUnited States
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Center for International Blood and Marrow Transplant...National Marrow Donor ProgramRecruitingAutoimmune Diseases | Hodgkin Lymphoma | Hematologic Malignancies | Acute Lymphoblastic Leukemia (ALL) | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Inherited Disorders of Metabolism | Inherited Abnormalities of Platelets | Histiocytic Disorders | Acute Myelogenous Leukemia (AML or ANLL) | Other Acute... and other conditionsUnited States
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National Institute of Allergy and Infectious Diseases...University of ChicagoRecruitingToxoplasmosisUnited States
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Spectrum Pharmaceuticals, IncActive, not recruitingBreast Cancer | NeutropeniaUnited States
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Hematological DiseasesUnited States, Belgium, Canada, France, Germany, Italy, United Kingdom
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X4 PharmaceuticalsActive, not recruiting
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National Cancer Institute (NCI)SuspendedDown Syndrome | Recurrent B Acute Lymphoblastic LeukemiaUnited States, Canada, Puerto Rico, Australia
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Medical College of WisconsinNational Heart, Lung, and Blood Institute (NHLBI); Dana-Farber Cancer Institute and other collaboratorsCompletedSickle Cell DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaCompletedEpidermolysis BullosaUnited States
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Vanderbilt University Medical CenterAminu Kano Teaching Hospital; Murtala Muhammad Specialist HospitalCompletedSickle Cell Anemia | Severe Acute MalnutritionNigeria, United States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Bellicum PharmaceuticalsTerminatedHemoglobinopathies | Hemophagocytic Lymphohistiocytosis | Metabolic Disorders | Primary Immune Deficiency Disorders | Inherited Bone Marrow Failure SyndromeUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Congenital Hemolytic AnemiaUnited States
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bluebird bioCompletedSickle Cell DiseaseUnited States
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National University of Ireland, Galway, IrelandKarolinska University Hospital; Galway University Hospitals; Kerckhoff Heart... and other collaboratorsEnrolling by invitationAortic Stenosis | Transcatheter Aortic Valve Replacement | Bicuspid Aortic Valve | Transcatheter Aortic Valve ImplantationSweden, Ireland, Germany
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Hydrocephalus and Neuroscience InstituteCompletedFolic Acid Deficiency | Neural Tube Defects | Spina Bifida | Anencephaly-Spina BifidaUnited States
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Rhythm Pharmaceuticals, Inc.CompletedBardet Biedl Syndrome (BBS) | Alström Syndrome (AS)United States, United Kingdom, France, Canada, Puerto Rico, Spain
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruiting
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The University of Texas Health Science Center,...University of California, San FranciscoActive, not recruitingMigraine | Cluster Headache | Trigeminal Autonomic Cephalgia | Hemicrania Continua | Paroxysmal Hemicrania | SUNCT | Short-Lasting Unilateral Neuralgiform Headache With Conjunctival Injection and TearingUnited States
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Sangamo TherapeuticsActive, not recruiting
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Paul SzabolcsEnrolling by invitationChronic Granulomatous Disease (CGD) | Wiskott-Aldrich Syndrome | Severe Chronic Neutropenia | Severe Combined Immunodeficiency (SCID) | Immunodeficiency With Predominant T-cell Defect, Unspecified | Hyper IgE Syndromes | Hyper IgM Deficiencies | Mendelian Susceptibility to Mycobacterial Disease | Common...United States
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Michael A BelfortBaylor College of MedicineCompletedCongenital Diaphragmatic HerniaUnited States
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BioMendics, LLCCompletedEpidermolysis Bullosa SimplexUnited States
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Centre Hospitalier Intercommunal CreteilAssociation Clinique Thérapeutique Infantile du val de Marne; KeocytActive, not recruitingSickle Cell DiseaseFrance
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Daniel BenjaminEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedHeart Failure | Epilepsy | Pain | Pneumonia | Sepsis | Inflammation | Hypertension | Chronic Kidney Diseases | Hemophilia | Schizophrenia | Central Nervous System Infections | Nosocomial Pneumonia | Insomnia | Anxiety | Bipolar Disorder | Neutropenia | Staphylococcal Infections | Bradycardia | Seizures | Urinary Tract Infections | Pulmonary... and other conditionsUnited States, Canada, United Kingdom, Israel, Singapore
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Anterogen Co., Ltd.CompletedDystrophic Epidermolysis BullosaKorea, Republic of
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Anterogen Co., Ltd.CompletedDystrophic Epidermolysis BullosaKorea, Republic of
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Enzychem Lifesciences CorporationCompletedFebrile NeutropeniaKorea, Republic of