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Search clinical trials for: genetic research
Total 96420 results
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Novilla PharmaceuticalsNot yet recruitingAcute Pain | Gout Flare | Acute Gouty ArthritisAustralia
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Nordlandssykehuset HFUniversity of Oslo; Norwegian University of Science and Technology; The University... and other collaboratorsRecruitingPorphyria, Acute IntermittentNorway
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingBeta-ThalassemiaUnited States
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UniQure Biopharma B.V.RecruitingFabry DiseaseUnited States
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University of California, San FranciscoJohns Hopkins University; Baylor College of Medicine; Children's Hospital of... and other collaboratorsNot yet recruiting
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruiting
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Massachusetts General HospitalPatient-Centered Outcomes Research InstituteNot yet recruitingNeurofibromatosis 1United States
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruitingFragile X Syndrome
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Yung NAQueen Mary Hospital, Hong Kong; Pamela Youde Nethersole Eastern HospitalRecruitingMuscle-Invasive Bladder Carcinoma | Muscle Invasive Bladder Urothelial CarcinomaHong Kong
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Pennington Biomedical Research CenterRecruitingBody Weight | Diet, Healthy | Metabolic DisturbanceUnited States
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Center for Strategic Planning, of the Federal Medical...National Medical Research Center for Cardiology, Ministry of Health of Russian...RecruitingMyocardial Infarction | Atherosclerosis | Atrial Fibrillation | Coronary Heart DiseaseRussian Federation
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PTC TherapeuticsRecruitingHuntington DiseaseAustralia, France, Germany, Netherlands, United Kingdom, Spain, Austria, Canada, Italy, New Zealand
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Hospital Universitari Vall d'Hebron Research InstituteERN-EuroBloodNet (European Reference Network on Rare Hematological DiseasesRecruitingLeukemia | Anemia | Iron Metabolism Disorders | Anemia, Sickle Cell | Thalassemia | Bleeding Disorder | Myeloma | Lymphoid Neoplasm | Blood Cancer | Bone Marrow Failure | Red Cell Membrane and Enzyme Abnormalities | Myeloma, MalignantSpain
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
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SanofiRecruitingDermatitis AtopicArgentina, Chile, Germany, Japan, Spain, United Kingdom, Canada, United States, Brazil, France, Turkey, Israel, Korea, Republic of, China
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Incyte CorporationRecruitingAtopic DermatitisGermany, Poland, United States, Spain, United Kingdom, Italy, Belgium, Canada, Netherlands, Australia, Bulgaria, France, Switzerland, Hungary, Korea, Republic of
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ReCode TherapeuticsRecruitingCystic FibrosisNew Zealand
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Swedish Orphan BiovitrumRecruitingHereditary Tyrosinemia, Type IChina
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Hospices Civils de LyonRecruitingPatients With PH1 Treated With Lumasiran in FranceFrance
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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AmgenRecruitingAtopic DermatitisUnited States, Canada
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SanofiRecruitingDermatitis AtopicJapan, Chile, Canada, Argentina, Brazil, France, United States, Turkey, China
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy 1France, Canada
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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Foundation For Rare Disease ResearchInstitute for Asthma & Allergy; Virant Diagnostics, Inc.; MedBio Reference Laboratories...Not yet recruitingAngioedema | Urticaria | C1 Inhibitor Deficiency | Angioedemas, Hereditary | Mastocytosis | Indolent Systemic Mastocytosis | Systemic Mastocytoses | ACE Inhibitor-Induced Angioedema
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New York Stem Cell Foundation Research InstituteRecruitingPTSD | Multiple Sclerosis | Cervical Cancer | Diabetes Mellitus, Type 2 | Diabetes Mellitus | Diabetes | Macular Degeneration | Diabetes Mellitus, Type 1 | Parkinson Disease | Amyotrophic Lateral Sclerosis | Dementia | Ovarian Cancer | Alzheimer Disease | ALS | Vulvar Cancer | Post Traumatic Stress Disorder | Lewy Body Disease and other conditionsUnited States
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New York Stem Cell Foundation Research InstituteCharcot-Marie-Tooth AssociationRecruitingHealthy | Charcot-Marie-Tooth DiseaseUnited States
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Lithuanian University of Health SciencesRecruitingInflammation | Cognitive Dysfunction | Genetic Predisposition to Disease | Endotoxemia | Major Depressive Disorder | Blood Brain Barrier DefectLithuania
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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Forma Therapeutics, Inc.Novo Nordisk A/SRecruitingSickle Cell DiseaseLebanon, Canada, Kenya, United Kingdom
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AstraZenecaNot yet recruitingHepatocellular Carcinoma | Prostate CancerUnited States
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University of CopenhagenGentofte Hospital, DenmarkRecruiting
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Quince Therapeutics S.p.A.BiotrialRecruitingAtaxia TelangiectasiaBelgium, United States, Denmark, Germany, Italy, Norway, Poland, Spain, United Kingdom
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Mario Negri Institute for Pharmacological ResearchRecruiting
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McGill University Health Centre/Research Institute...Canadian Institutes of Health Research (CIHR)RecruitingZellweger Spectrum DisorderCanada
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University of Alabama at BirminghamChildren's Hospital of Philadelphia; Congressionally Directed Medical Research...Not yet recruitingNeurofibromatosis 1 | Plexiform Neurofibroma
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Wave Life Sciences Ltd.RecruitingAlpha-1 Antitrypsin DeficiencyUnited Kingdom
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BiocadRecruitingHemophilia ARussian Federation
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Vertex Pharmaceuticals IncorporatedRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, Canada, Australia
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SanofiRecruitingDermatitis AtopicArgentina, Japan, China, Bulgaria, Czechia, Spain, United States, South Africa, United Kingdom, Portugal, Denmark, Sweden, Turkey, Italy
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University of WashingtonBreast Cancer Research FoundationNot yet recruitingAnatomic Stage III Breast Cancer AJCC v8 | Anatomic Stage IV Breast Cancer AJCC v8 | Metastatic HER2-Negative Breast Carcinoma | Metastatic Hormone Receptor-Positive Breast Carcinoma | Locally Advanced Unresectable HER2-Negative Breast Carcinoma | Locally Advanced Unresectable Hormone Receptor-Positive...United States
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ETH ZurichUniversity of Zurich; Agroscope Liebefeld-Posieux Research Station ALP; Swiss...RecruitingLactose IntoleranceSwitzerland
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AstraZenecaRecruitingNeurofibroma, PlexiformChina
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Hamilton Health Sciences CorporationCanadian Institutes of Health Research (CIHR); Population Health Research Institute and other collaboratorsNot yet recruitingArrhythmogenic Right Ventricular Cardiomyopathy | Arrhythmogenic CardiomyopathyCanada
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ACADIA Pharmaceuticals Inc.RecruitingHyperphagia in Prader-Willi SyndromeUnited States, Canada, United Kingdom
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)RecruitingChildren | Sickle Cell DiseaseCongo, The Democratic Republic of the, Angola, Kenya, Uganda
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Gianni SoraruMario Negri Institute for Pharmacological ResearchRecruitingSpinal and Bulbar Muscular AtrophyItaly
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TakedaRecruitingAlpha1-Antitrypsin DeficiencyItaly, United States, Poland, Portugal
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Clarametyx Biosciences, Inc.RecruitingCystic Fibrosis | Persistent InfectionUnited States