Clinical Trials Sponsored by Foundation for Rare Diseases

Total 497 results

National Center for Research Resources (NCRR)
Virginia Commonwealth University

Completed

Study of Individualized Instruction Versus Pamphlet in Systemic Lupus Erythematosus

Systemic Lupus Erythematosus
National Center for Research Resources (NCRR)
University of Texas

Completed

Study of a Phenylalanine Restricted Diet During Pregnancy to Prevent Symptoms in Offspring of Patients With Phenylketonuria

Phenylketonuria
National Center for Research Resources (NCRR)
National Institute of Allergy and Infectious Diseases (NIAID)

Completed

Phase III Randomized, Controlled Study of Ganciclovir for Symptomatic Congenital Cytomegalovirus Infection

Cytomegalovirus Infections
National Center for Research Resources (NCRR)
National Institute of Allergy and Infectious Diseases (NIAID)

Completed

Phase III Randomized, Placebo-Controlled Study of Acyclovir Oral Suspension for Neonatal Herpes Simplex Virus Infection Limited to the Skin, Eyes, and Mouth

Herpes Simplex
National Center for Research Resources (NCRR)
National Institute of Allergy and Infectious Diseases (NIAID)

Completed

Phase I/II Study of Human Anti-Cytomegalovirus (CMV) Monoclonal Antibody MSL-109 in Newborns With Symptomatic Congenital CMV Infection Without Central Nervous System Disease

Cytomegalovirus Infections
University Ghent
Research Foundation Flanders; Flemish Agency for Care and Health

Completed

Promoting Healthy Lifestyle Behaviors in Schoolchildren: an Online Video Intervention for Parents (Movie Models)

Physical Activity | Parenting | Parents | Sedentary Behavior | Healthy Diet | Primary Schoolchildren

Belgium
Adwin Life Care
Center For Homeopathy Research, India; Sonal Foundation, India

Completed

Impact of Homeopathy for Persistent Insomnia in Patients With Cancer

Cancer | Chronic Insomnia

India
New Mexico Cancer Care Alliance
Christus Stehlin Foundation for Cancer Research

Completed

Phase I and Pharmacology Study of Camptothecin-20-O-Propionate Hydrate (CZ48) in Patients With Solid Tumors or Lymphoma

Advanced Solid Tumors | Lymphomas

United States
National Center for Research Resources (NCRR)
National Institute of Allergy and Infectious Diseases (NIAID)

Completed

Phase I/II Study of High-Dose Acyclovir for Central Nervous System or Disseminated Neonatal Herpes Simplex Virus Infection

Herpes Simplex
University of Tartu
Estonian Science Foundation; European Society for Paediatric Infectious Diseases

Completed

Management of Early Onset Neonatal Septicaemia: Selection of Optimal Antibacterial Regimen for Empiric Treatment

Early Onset Neonatal Sepsis

Estonia
University Hospital, Basel, Switzerland
Swiss Foundation for the Study of Muscular Diseases

Completed

Longitudinal Imaging in Patients With Large Vessel Vasculitis to Predict Further Disease Course

Giant Cell Arteritis | Large Vessel Giant Cell Arteriitis

Switzerland
International Centre for Diarrhoeal Disease Research...
CARE Bangladesh; Gram Bikash Kendra (GBK); CARE USA

Recruiting

Evaluation of Tipping Point

Child Marriage

Bangladesh
University of British Columbia
Rare Disease Foundation, Vancouver, Canada; Saudi Arabian Cultural Bureau,...

Completed

Protein Requirements in Children With Phenylketonuria (PKU)

Phenylketonuria

Canada
Elizabeth Glaser Pediatric AIDS Foundation
Centers for Disease Control and Prevention

Completed

Enhanced Adherence Counselling, Pre-Post Study

HIV Infection

Kenya
Uppsala University
Swedish Society for Medical Research; Swedish Parkinson's Disease Foundation

Completed

Different Dyskinesias in Parkinson's Disease and Their Relation to Levodopa Pharmacokinetics (DYSK-PD-2007)

Parkinson Disease | Dyskinesias

Sweden
International Centre for Diarrhoeal Disease Research...
Children's Investment Fund Foundation

Recruiting

Multiple Micronutrient Supplementation (MMS) Evaluation Among Bangladeshi Pregnant Women

Infant, Low Birth Weight

Bangladesh
International Centre for Diarrhoeal Disease Research...
UNICEF; UBS Optimus Foundation

Unknown

Effectiveness Trial of Day-care vs. Usual Care of Severe Pneumonia & Malnutrition in Children (Day-care)

Pneumonia Childhood

Bangladesh
Uppsala University
Swedish Society for Medical Research; Swedish Parkinson's Disease Foundation

Completed

Pharmacokinetics of Levodopa/Carbidopa Infusion With and Without Oral Catechol-O-methyl Transferase (COMT) Inhibitors (DuoCOMT)

Parkinson Disease

Sweden
National Center for Research Resources (NCRR)
Vanderbilt University Medical Center

Completed

Phase II Randomized, Double-Blind, Placebo-Controlled Study of Intravenous Mucoid Exopolysaccharide Pseudomonas Aeruginosa Immune Globulin for Cystic Fibrosis

Bacterial Infections | Cystic Fibrosis
National Center for Research Resources (NCRR)
Baylor College of Medicine

Completed

Study of the Nutritional, Metabolic, and Body Composition Profile in Children and Adolescents With Epidermolysis Bullosa

Epidermolysis Bullosa
National Center for Research Resources (NCRR)
Baylor College of Medicine

Completed

Phase II Randomized Study of Leuprolide Vs Oral Contraceptive Therapy Vs Leuprolide and Oral Contraceptive Therapy for Ovarian Hyperandrogenism

Hyperandrogenism
National Center for Research Resources (NCRR)
Children's Hospital of Philadelphia

Completed

Diagnostic Pilot Study of Dual Energy Absorptiometry in the Detection of Osteopenia or Osteoporosis in Patients With Thalassemia Major

Osteoporosis | Osteopenia | Thalassemia Major
M.D. Anderson Cancer Center
National Cancer Institute (NCI); Texas Appropriation for Rare and Aggressive...

Recruiting

Biospecimen and Medical Data Collection and Tumor Biopsy in Creating Research Tissue Registry in Patients With Inflammatory or Invasive Breast Cancer

Invasive Breast Carcinoma | Inflammatory Breast Carcinoma | Second Primary Malignant Neoplasm

United States
National Center for Research Resources (NCRR)
University of North Carolina

Completed

Multicenter Study of Nontuberculous Mycobacteria in Cystic Fibrosis Patients

Cystic Fibrosis | Atypical Mycobacterium Infection
University Hospital, Bordeaux
Reference Centre for Rare Diseases Malformations Congenital Heart Complexes...

Not yet recruiting

Asynchrony in Operated Tetralogy of Fallot (FALLOT-XI)

Tetralogy of Fallot

France
National Center for Research Resources (NCRR)
Baylor College of Medicine

Completed

Phase IV Study of Chronic Infusional Epoprostenol for Severe Primary Pulmonary Hypertension

Hypertension, Pulmonary
National Center for Research Resources (NCRR)
University of North Carolina

Completed

Phase I Pilot Study of Ad5-CB-CFTR, an Adenovirus Vector Containing the Cystic Fibrosis Transmembrane Conductance Regulator Gene, in Patients With Cystic Fibrosis

Cystic Fibrosis
National Center for Research Resources (NCRR)
Baylor College of Medicine

Completed

Phase II Study of the Effect of Leuprolide Acetate and Spironolactone on Insulin Resistance in Hyperandrogenic Women With Polycystic Ovarian Disease or Hyperandrogenism Insulin Resistance Acanthosis Nigricans Syndrome

Polycystic Ovary Syndrome | Acanthosis Nigricans
National Center for Research Resources (NCRR)
University of North Carolina

Completed

Phase I/II Study of Monoclonal Factor IX Concentrate for Factor IX Deficiency

Hemophilia B | Factor IX Deficiency
National Center for Research Resources (NCRR)
University of North Carolina

Completed

Phase I Study of Human Von Willebrand Factor for Von Willebrand's Disease

Von Willebrand's Disease
Huashan Hospital
China Alliance for Rare Diseases; National Center for Neurological Disorders... and other collaborators

Recruiting

Myasthenia Gravis Registry in China

Myasthenia Gravis

China
National Institute of Allergy and Infectious Diseases...
HIV Vaccine Trials Network; IPPOX Foundation; EuroVacc Foundation; Global Solutions...

Withdrawn

Evaluating the Safety and Immune Response to Two HIV Vaccine Regimens in Healthy, HIV-Uninfected Adults in the United States and South Africa

HIV Infections
Elizabeth Glaser Pediatric AIDS Foundation
Centers for Disease Control and Prevention; Ministry of Health, Malawi; Cooperative...

Completed

Adaptation and Evaluation of the PMTCT CSC in Dedza and Ntcheu Districts, Malawi

HIV/AIDS | Infant Morbidity

Malawi
D'Or Institute for Research and Education
Centers for Disease Control and Prevention; Oswaldo Cruz Foundation

Completed

Brazil ICU Encephalitis Surveillance

Encephalitis | Meningitis | Prognosis | Intensive Care Neurological Disorder | Meningitis/Encephalitis | Central Nervous System Infections and Inflammations

Brazil
Drugs for Neglected Diseases
Universiteit Antwerpen; PENTA Foundation; St George's, University of London

Completed

NeoAMR Observational Study in Neonatal Sepsis

Neonatal SEPSIS

Bangladesh, Uganda, Thailand, South Africa, Italy, Greece, India, Brazil, China, Kenya, Vietnam
Mitsubishi Tanabe Pharma Corporation
The Research Foundation for Microbial Diseases of Osaka University

Completed

Confirmatory Study of BK1310 in Healthy Infants

Pertussis | Tetanus | Diphtheria | Bacterial Meningitis | Poliomyelitis

Japan
Mitsubishi Tanabe Pharma Corporation
The Research Foundation for Microbial Diseases of Osaka University

Completed

Safety and Efficacy of BK1310 Intramuscular Injection in Healthy Infants

Immunization

Japan
Mitsubishi Tanabe Pharma Corporation
The Research Foundation for Microbial Diseases of Osaka University

Completed

Study of BK1301 (DTaP Vaccine) as a Booster in Adolescents

Pertussis | Tetanus | Diphtheria

Japan
Mitsubishi Tanabe Pharma Corporation
The Research Foundation for Microbial Diseases of Osaka University

Completed

Phase 3 Study of BK1310 in Healthy Infants

Immunization; Infection

Japan
National Center for Research Resources (NCRR)
National Institute of Allergy and Infectious Diseases (NIAID); Rockefeller...

Completed

Phase II Placebo Controlled Study of Thalidomide in Patients With Mycobacterial and HIV Infections

HIV Infections | Mycobacterium Infections | Tuberculosis
National Center for Research Resources (NCRR)
University of California, Los Angeles

Completed

Phase III Randomized, Double-Blind, Placebo-Controlled Study of Dehydroepiandrosterone Replacement for Primary Adrenal Insufficiency

Addison's Disease
National Center for Research Resources (NCRR)
University of California, San Diego

Completed

Evaluation of Fanconi Syndrome and Cystinosis

Fanconi Syndrome | Cystinosis
National Center for Research Resources (NCRR)
University of California, Los Angeles

Completed

Study of the Effect of Four Methods of Cardiopulmonary Resuscitation Instruction on Psychosocial Response of Parents With Infants at Risk of Sudden Death

Pulmonary Hypertension | Respiratory Distress Syndrome | Bronchopulmonary Dysplasia
National Center for Research Resources (NCRR)
Oregon Health and Science University

Completed

Purification of Testis-Stimulating Factor in Precocious Puberty

Precocious Puberty
National Center for Research Resources (NCRR)
University of California, San Diego

Completed

Phase II Pilot Study of Aminoimidazole Carboxamide Riboside (AICAR), a Precursor of Purine Synthesis, for Lesch-Nyhan Disease

Lesch-Nyhan Syndrome
International Centre for Diarrhoeal Disease Research...
Bill and Melinda Gates Foundation

Recruiting

Maternal Probiotic Intervention to Improve Gut Health (MPIGH)

Environmental Enteric Dysfunction | Gut Microbiota Dysbiosis

Bangladesh
International Centre for Diarrhoeal Disease Research...
Bill and Melinda Gates Foundation

Active, not recruiting

Saving Lives With Better Gestational Age Estimation

Premature Birth

Bangladesh
Vanderbilt University
Centers for Disease Control and Prevention; Marshfield Clinic Research Foundation

Completed

Factors Associated With Maintenance of Antibody Responses to Influenza Vaccine in Older, Community-Dwelling Adults

Aging
International Centre for Diarrhoeal Disease Research...
Bill and Melinda Gates Foundation

Completed

Immunological and Clinical Responses to Zinc in Children With Diarrhoea

Diarrhoea

Bangladesh
Children's Hospital Medical Center, Cincinnati
National Center for Research Resources (NCRR); Rare Diseases Clinical Research...

Completed

Multicenter International Cross-Sectional Evaluation of Pulmonary Alveolar Proteinosis Trial

Pulmonary Alveolar Proteinosis

United States, Germany, Italy, Japan

Clinical Trials Sponsored by Foundation for Rare Diseases

Sponsors and Collaborators

Medical Conditions

Drug Interventions

CROs by country

CROs in China

Conditions

Rare Diseases

Drug Interventions

Dietary Supplements

Sponsor/Collaborators

Locations