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Search clinical trials for: Enzyme Replacement Therapy
Total 95139 results
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | Mucopolysaccharidosis VII | MPS VIIUnited States, Brazil, Mexico, Portugal
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | MPS VII | MPS 7United States
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University of California, San FranciscoCompleted
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University of Roma La SapienzaUnknownGastro Esophageal Reflux | Bariatric Surgery Candidate | Barrett EsophagusItaly
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HK inno.N CorporationCompletedHelicobacter Pylori InfectionKorea, Republic of
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St. Antonius HospitalCompletedMyocardial Infarction | Stroke | Bleeding | Aortic Valve DiseaseNetherlands, Belgium, Czechia, Luxembourg
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University of RostockUnknownAcute Kidney Injury | Renal Replacement TherapyGermany
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BayerJanssen Research & Development, LLCTerminatedTranscatheter Aortic Valve ReplacementBelgium, France, Germany, Spain, United States, Switzerland, Canada, Austria, United Kingdom, Korea, Republic of, Denmark, Italy, Netherlands, Poland, Czechia, Sweden, Norway
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University Hospital TuebingenWithdrawnAcute Kidney Insufficiency | Anti-Infective Agent ToxicityGermany
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencySpain, Germany, Italy, United States, Croatia, Canada, Russian Federation, Denmark, United Kingdom, Belgium, Mexico, Australia, Netherlands, Brazil, Turkey
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Baylor Research InstituteShireUnknownQuality of Life | Renal Insufficiency | Cardiac EventUnited States
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | Mucopolysaccharidosis VII | MPS VIISpain, United States, Portugal
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedKrabbe Disease | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)United States
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PfizerWithdrawnType 1 Gaucher DiseaseUnited States
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Iowa City Veterans Affairs Medical CenterUS Department of Veterans AffairsCompleted
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Mark Vander WegIowa City VA Health Care SystemUnknownNicotine Dependence | Smokeless TobaccoUnited States
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Duke UniversityCompletedSchizophrenia | Cigarette SmokingUnited States
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Dwight Koeberl, M.D., Ph.D.Completed
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Johns Hopkins UniversityGlaxoSmithKlineCompletedPulmonary Embolism | Deep Venous ThrombosisUnited States
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National Taiwan University HospitalActelionUnknown
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MedImmune LLCNational Heart, Lung, and Blood Institute (NHLBI)CompletedCoronary Artery Disease | AtherosclerosisUnited States
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Novartis PharmaceuticalsCompletedHemodialysis | Renal Replacement Therapy | End Stage Renal Disease (ESRD) | Renal Transplantation | Chronic Kidney Disease (CKD)Germany, United States, Belgium, Italy, Spain, Croatia, Taiwan, Australia, Austria, Greece, Korea, Republic of, Lebanon, Czechia, Israel, Netherlands, Slovenia, Switzerland, Thailand, Norway, Turkey, Sweden, Argentina, Brazil, Japan, Se... and more
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Seoul National University HospitalPharmbio Korea Co., Ltd.CompletedPancreaticoduodenectomyKorea, Republic of
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Ultragenyx Pharmaceutical IncCompleted
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia
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University of FloridaAmicus TherapeuticsTerminatedPompe Disease | Hypersensitivity Reaction
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ActelionCompletedGaucher Disease Type 1United States, Taiwan, Canada, Spain, Australia, France, Brazil, Hungary, Czechia, Germany, Italy, Netherlands, United Kingdom
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Claudio Mendes PannutiCompleted
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Amicus TherapeuticsCompletedFabry DiseaseFrance, Austria, United States, Belgium, Japan, United Kingdom, Denmark, Brazil, Australia, Italy
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Ulla Feldt-RasmussenCompleted
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Ulla Feldt-RasmussenCompleted
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PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain
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PfizerCompletedGaucher DiseaseChile, United Kingdom, Canada, Spain, Israel, United States, Australia, South Africa
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Masonic Cancer Center, University of MinnesotaTerminatedHurler Syndrome | Mucopolysaccharidosis Type IH | MPS IUnited States
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited States
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University Hospital Inselspital, BerneRigshospitalet, Copenhagen, Denmark (Prof. Moller, Dr. Krag)CompletedCritical Illness | Acute Kidney Injury | Renal Replacement Therapy | End-stage Renal Disease | Proton Pump InhibitorDenmark, Switzerland
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VA Office of Research and DevelopmentCompleted
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PfizerNo longer availableGaucher DiseaseUnited States, Israel
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Hanlim Pharm. Co., Ltd.CompletedHealthy Male VolunteersKorea, Republic of
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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Idorsia Pharmaceuticals Ltd.Completed
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University Hospital, RouenUnknownAnderson-Fabry DiseaseFrance
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Anthera PharmaceuticalsCompletedCystic Fibrosis | Exocrine Pancreatic InsufficiencyUnited States, Hungary, Israel, Poland, Spain, Czechia
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Anthera PharmaceuticalsCompletedCystic Fibrosis | Exocrine Pancreatic InsufficiencyUnited States
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Nadia Ali, PhDBioMarin PharmaceuticalCompletedMorquio A Syndrome | Mucopolysaccharidosis IV AUnited States
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Taipei Veterans General Hospital, TaiwanUnknownCompare the Response Rate of Atypical GERD After PPI TherapyTaiwan
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Chulalongkorn UniversityCompleted
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Northern Orthopaedic Division, DenmarkAalborg University; Association of Danish Physiotherapists; The Danish Rheumatism... and other collaboratorsCompletedOsteoarthritis of the KneeDenmark
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Janssen Research & Development, LLCCompletedPain | OsteoarthritisUnited States, Australia, Poland, Korea, Republic of, Canada, Germany, Hungary, Spain, Czechia, Sweden, United Kingdom
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Jed E. RoseNational Institute on Drug Abuse (NIDA); Philip Morris USA, Inc.CompletedNicotine DependenceUnited States