- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Heredodegenerative Disorders of the Nervous System
Total 474719 results
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National Cancer Institute (NCI)RecruitingNeurofibromatosis 1 | Noonan Syndrome | Legius Syndrome | Cardiofaciocutaneous Syndrome | Costello SyndromeUnited States
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PTC TherapeuticsRecruitingA Study to Evaluate the Safety and Efficacy of PTC518 in Participants With Huntington's Disease (HD)Huntington DiseaseUnited States, Austria, Spain, United Kingdom, Australia, France, Germany, Netherlands, Italy, New Zealand, Canada
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The University of Texas Health Science Center,...RecruitingHuntington DiseaseUnited States
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Weill Medical College of Cornell UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingMyocardial Fibrosis | Cardiomyopathies | Friedreich Ataxia | Cardiac HypertrophyUnited States
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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Advice Pharma Group srlRecruitingDiabetes | Chronic Kidney Diseases | Tuberous Sclerosis | Albuminuria | Treatment Adherence | Arterial Hypertension | Treatment Adherence and Compliance | Nephronophthisis | Polycystic Kidney | Chronic Glomerulonephritis | Cystic Kidney Diseases | Cortical Cystic Disease | Cystic DiseasesItaly
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University of UtahAlbert Einstein College of Medicine; University of MiamiNot yet recruitingTourette Syndrome in ChildrenUnited States
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Ohio State UniversityHuntington's Disease Society of AmericaRecruiting
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Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRecruitingPyruvate Dehydrogenase Complex Deficiency | Pyruvate Dehydrogenase E1 Alpha Deficiency | Pyruvate Dehydrogenase E1-Beta Deficiency | Pyruvate Dehydrogenase E2 Deficiency | Pyruvate Dehydrogenase Phosphatase DeficiencyUnited Kingdom
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UniQure Biopharma B.V.RecruitingHuntington DiseasePoland, United Kingdom, Germany
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OrphalanErgomedRecruitingWilson's DiseaseSpain, United Kingdom, Belgium, Germany, Poland, France, Saudi Arabia
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Cairo UniversityRecruitingEntrapment NeuropathiesEgypt
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Fondation Ophtalmologique Adolphe de RothschildRecruiting
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Neurogene Inc.RecruitingNeuronal Ceroid Lipofuscinosis CLN5United States, United Kingdom
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AO GENERIUMRecruitingMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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Centre Leon BerardRecruitingNeurofibroma | Neurofibroma, PlexiformFrance
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Xuanwu Hospital, BeijingRecruitingGait | Motor FunctionChina
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Tasly Pharmaceuticals, Inc.Not yet recruitingTourette Syndrome in Children | Tourette Syndrome in AdolescenceUnited States
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Fondation Ophtalmologique Adolphe de RothschildRecruiting
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Tasly Pharmaceuticals, Inc.Not yet recruitingTourette SyndromeUnited States
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SciSparcNot yet recruiting
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.Not yet recruitingType I NeurofibromatosisChina
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Sage TherapeuticsRecruitingHuntington's DiseaseUnited States, Australia, Canada, United Kingdom
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Tasly GeneNet Pharmaceuticals Co., LtdRecruitingCharcot-Marie-Tooth Type 1AChina
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University Hospital of North NorwayRecruitingLower Back Pain | Abdominal Pain | Nerve Compression SyndromeNorway
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Université du Québec à ChicoutimiRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
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Noema Pharma AGRecruitingTuberous Sclerosis ComplexUnited States, Turkey, Poland, Spain, United Kingdom, India, Italy, Israel
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Marquette UniversityUniversity of UtahRecruitingTourette Disorder | Persistent Tic DisordersUnited States
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Wave Life Sciences Ltd.RecruitingHuntington DiseaseCanada, Spain, Australia, Denmark, Netherlands, Poland, United Kingdom, France, Germany, Italy
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Zarife SahenkRecruitingCharcot-Marie-Tooth Disease | Peripheral Neuropathy | Chronic Inflammatory Demyelinating PolyneuropathyUnited States
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National Human Genome Research Institute (NHGRI)RecruitingDiabetes | Undiagnosed Diseases | Inherited Metabolic Disorders | Batten's Disease | Tay SachsUnited States
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
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Katarzyna KotulskaRecruitingTuberous Sclerosis ComplexPoland
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Zynerba Pharmaceuticals, Inc.RecruitingFragile X SyndromeUnited States, Australia, United Kingdom, Ireland
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Viking Therapeutics, Inc.RecruitingAdrenomyeloneuropathy Form (AMN) of X-linked Adrenoleukodystrophy (X-ALD)United States, France, Germany, Italy, United Kingdom
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy | Kennedys DiseaseUnited States
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Institut National de la Santé Et de la Recherche...Imagine InstituteRecruiting
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Wuhan Neurophth Biotechnology Limited CompanyRecruitingLeber's Hereditary Optic Neuropathy (LHON)China
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... and other collaboratorsRecruiting
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...RecruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Progressive Muscular Atrophy | Hereditary Spastic ParaplegiaUnited States, South Africa
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Nova Mentis Life Science CorpFourthWall TestingRecruitingAutism Spectrum Disorder | Fra(X) SyndromeUnited States
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University of Wisconsin, MilwaukeeNF Midwest; NF NortheastRecruitingSocial Skills | Neurofibromatosis 1United States
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Akcea TherapeuticsUnited BioSource, LLCRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, France, Greece, Italy, Spain, Canada, Germany, Portugal
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Ionis Pharmaceuticals, Inc.RecruitingAlexander DiseaseUnited States, United Kingdom, Australia, Canada, Israel, Italy, Japan, Netherlands
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Myrtelle Inc.RecruitingCanavan DiseaseUnited States
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National Cancer Institute (NCI)RecruitingNeurofibromatosis 1United States
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Polaryx Therapeutics, Inc.Not yet recruitingJuvenile Neuronal Ceroid Lipofuscinosis
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Universitätsklinikum Hamburg-EppendorfRecruitingBatten Disease | Neuronal Ceroid Lipofuscinosis | CLN1 Disease | CLN2 Disease | CLN3 Disease | CLN4 Disease | CLN5 Disease | CLN6 Disease | CLN7 Disease | CLN8 Disease | CLN10 Disease | CLN11 Disease | CLN12 Disease | CLN13 Disease | CLN14 DiseaseGermany