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Search clinical trials for: Inherited mitochondrial disease
Total 383377 results
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BiogenNot yet recruiting
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); North American...RecruitingMitochondrial Diseases | Mitochondrial Myopathies | MELAS | Mitochondrial Encephalomyopathies | MERRFUnited States
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East Kent Hospitals University NHS Foundation TrustNot yet recruitingHaemophiliaUnited Kingdom
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...DAMOR Farmaceutici S.p.a.Recruiting
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TiumBio Co., Ltd.RecruitingHemophilia A | Hemophilia B | Blood Coagulation DisordersKorea, Republic of
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IRCCS San RaffaeleAzienda Socio Sanitaria Territoriale della Valle OlonaRecruitingMultiple SclerosisItaly
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Friedreich's Ataxia Research AllianceRecruitingFriedreich AtaxiaUnited States, Canada, New Zealand, Australia, France, Austria, Belgium, Brazil, Czechia, Germany, Greece, Ireland, Italy, Spain, United Kingdom, India, Netherlands
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Minovia Therapeutics Ltd.RecruitingMitochondrial Diseases | Pearson SyndromeIsrael
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Stanford UniversityNot yet recruitingLiver Failure | Liver Cirrhosis | Hemophilia A | Hemophilia B | Hemophilia | Liver Transplant Disorder | Coagulation Factor DeficiencyUnited States
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Second Affiliated Hospital, School of Medicine,...Not yet recruiting
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Jiangsu Gensciences lnc.RecruitingHemophilia | Hemophilia A With Inhibitor | Male | Hemophilia B With InhibitorChina
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CSL BehringRecruiting
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University Hospital, AngersNot yet recruitingNicotinamide Adverse Reaction
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CSL BehringRecruiting
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University of Nevada, Las VegasRecruitingDown SyndromeUnited States
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Xiangya Hospital of Central South UniversityRecruitingPost Stroke EpilepsyChina
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Hoffmann-La RocheRecruitingHemophilia ASpain, Canada, United States, New Zealand, Italy, Poland
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Hasan Kalyoncu UniversityNot yet recruitingHemophilia A | Hemophilia B | HemophiliaTurkey
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Assiut UniversityNot yet recruitingHemophilia A | Hemophilia B
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Tri-Service General HospitalRecruitingSevere Hemophilia A Without InhibitorTaiwan
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University Hospital, ToulouseNot yet recruiting
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Fondazione G.B. Bietti, IRCCSRecruitingMacular Edema | Inherited Retinal Dystrophy | Laser RetinopathyItaly
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Stephanie B. Seminara, MDRecruitingKallmann Syndrome | Hypogonadotropic Hypogonadism | Delayed Puberty | Reproductive DisorderUnited States
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Maastricht UniversityRecruitingMitochondrial MyopathiesNetherlands
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Heinrich-Heine University, DuesseldorfRecruitingHeart Failure | Mitochondrial Diseases | Insulin Resistance | Diabetic Cardiomyopathies | Type2diabetesGermany
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Janssen Research & Development, LLCRecruitingInherited Retinal DiseasesUnited States, Korea, Republic of, Canada, Spain, Denmark, Germany, France, Italy, Austria, United Kingdom, Israel, Brazil
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Institut National de la Santé Et de la Recherche...RecruitingNeurofibromatosis Type 1 | Ichthyosis | Ectodermal Dysplasia | Albinism | Pemphigus | Mucous Membrane Pemphigoid | Inherited Epidermolysis Bullosa | Palmoplantar Keratoderma | Incontinentia PigmentiFrance
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German Center for Neurodegenerative Diseases (DZNE)McMaster University; Sorbonne UniversityRecruitingFriedreich AtaxiaAustria, Germany, France
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OctapharmaNot yet recruitingHemophilia ASpain, France, Finland, Germany, Italy, Serbia
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OctapharmaRecruitingSevere Hemophilia ASpain, Croatia, Italy, North Macedonia, Serbia
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St. Jude Children's Research HospitalNot yet recruiting
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Dignity Health Medical FoundationDolly Roy MD PhD (author); J. Michael Menke (statistician); Sabeen Lulu MD (Principal...Not yet recruitingMultiple Sclerosis | Relapse
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingHereditary Transthyretin AmyloidosisItaly
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Xue-chun LuRecruiting
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Oregon Health and Science UniversityVanderbilt University Medical CenterNot yet recruitingBleeding Disorder | Von Willebrand Diseases | Heavy Menstrual Bleeding
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University of ArkansasRecruitingNeurofibromatosis 1United States
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SanofiRecruitingHemophilia AUnited States
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West Kazakhstan Medical UniversityRecruitingOrnithine Transcarbamylase Deficiency | Biotinidase Deficiency | Citrullinemia | Glutaric Acidemia Type II | Argininosuccinic Aciduria | Maple Syrup Urine Disease | Primary Carnitine Deficiency | Homocystinuria | Carnitine Palmitoyltransferase II Deficiency | Arginase Deficiency | Very Long-chain Acyl-CoA... and other conditionsKazakhstan
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HuidaGene Therapeutics Co., Ltd.Cholgene Therapeutics, Inc.RecruitingLeber Congenital Amaurosis | Inherited Retinal Diseases Caused by RPE65 MutationsUnited States, China
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Hereditary Neuropathy FoundationRecruitingCharcot-Marie-Tooth Disease | Charcot-Marie-Tooth Disease, Type IA | Charcot-Marie-Tooth Disease Type 2A | Charcot-Marie-Tooth | Charcot-Marie-Tooth Disease, Type IB | Charcot-Marie-Tooth Disease Type 2 | Charcot-Marie-Tooth Disease, Type 2C | Charcot-Marie-Tooth Disease Type 2A2B | Charcot-Marie-Tooth... and other conditionsUnited States
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East Kent Hospitals University NHS Foundation TrustGreat Ormond Street Hospital for Children NHS Foundation Trust; University...RecruitingHemophilia | Musculoskeletal Diseases or Conditions | Child, OnlyUnited Kingdom
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Universitair Ziekenhuis BrusselNot yet recruiting
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Hasan Kalyoncu UniversityNot yet recruitingHemophilia B | Hemophilia | Hemophilia A, SevereTurkey
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Institute of Hematology & Blood Diseases Hospital...Sinocelltech Ltd.RecruitingHemophilia A With InhibitorChina
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Bahçeşehir UniversityRecruitingHemophilia A | Hemophilia BTurkey
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Institut National de la Santé Et de la Recherche...Not yet recruiting
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University Hospital, Clermont-FerrandRecruitingPulmonary Disease, Chronic Obstructive | Oxygen Deficiency | Mitochondrial AlterationFrance
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University Hospital, GrenobleRecruiting
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I.R.C.C.S. Fondazione Santa LuciaUniversità Foro Italico Roma; CNR PisaNot yet recruitingParkinson Disease | Metabolic Disease | Gait Analysis | Therapy, Directly Observed
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Institute of Hematology & Blood Diseases HospitalRecruiting