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Search clinical trials for: Leber congenital amaurosis
Total 23937 results
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National Taiwan University HospitalEnrolling by invitationPolycystic Kidney Diseases | Muscle Loss | Polycystic Liver DiseaseTaiwan
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University of HelsinkiRoyal Children's Hospital; Murdoch Childrens Research Institute; University of... and other collaboratorsActive, not recruitingLiver Diseases | Kidney Diseases | Diabetes | Rheumatic Diseases | Inflammatory Bowel Diseases | Neurologic Disorder | Congenital Heart Disease | TransitionAustralia, Finland
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Mirum Pharmaceuticals, Inc.Completed
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University of DundeeCompletedHepatitis CUnited Kingdom
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Mirum Pharmaceuticals, Inc.Clinigen, Inc.Approved for marketingAlagille SyndromeUnited States
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Sohag UniversityCompleted
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Radboud University Medical CenterAcademisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA)CompletedPolycystic Kidney, Autosomal Dominant | Polycystic Liver DiseaseNetherlands, Spain
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Mayo ClinicCompletedCirrhosis | Congenital Heart DiseaseUnited States
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Mirum Pharmaceuticals, Inc.CompletedAlagille SyndromeFrance, Belgium, Poland, Australia, Spain, United Kingdom
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Mirum Pharmaceuticals, Inc.Lumena Pharmaceuticals, Inc.; Childhood Liver Disease Research and Education...Completed
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University of MiamiCompleted
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)CompletedAlpha 1-Antitrypsin DeficiencyAustralia, New Zealand
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Institute of Liver and Biliary Sciences, IndiaUnknownPortal Hypertension, Biliary AtresiaIndia
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National Human Genome Research Institute (NHGRI)Completed
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The Hospital for Sick ChildrenCompletedZellweger Syndrome | Peroxisome Biogenesis DisordersCanada
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Syneos HealthMerck Sharp & Dohme LLC; Sandoz; Teva Pharmaceuticals USA; Aurobindo Pharma Ltd; Zydus...TerminatedHepatitis C | Pregnancy Complications | Birth DefectsUnited States
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University Hospital, GasthuisbergThe University of Texas Health Science Center, Houston; Baylor College of Medicine and other collaboratorsCompletedCongenital Diaphragmatic Hernia | Pulmonary Hypoplasia | Fetal SurgeryUnited Kingdom, Canada, United States, Belgium, Germany, Italy, France, Australia, Poland, Spain
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Mayo ClinicCompletedMultiple Sclerosis | Rheumatoid Arthritis | Systemic Lupus Erythematosus | Uveitis | Vasculitis | Psoriasis | Graves Disease | Systemic Sclerosis | Celiac Disease | Crohn Disease | Type 1 Diabetes Mellitus | Myasthenia Gravis | Ulcerative Colitis | Dermatomyositis | Polymyositis | Vitiligo | Hepatitis, Autoimmune | Polymyalgia... and other conditionsUnited States
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Aljazeera HospitalNational Research Centre, EgyptCompleted
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Mayo ClinicCompletedAutosomal Dominant Polycystic Kidney Disease | Polycystic Liver Disease | Autosomal Dominant Polycystic Liver Disease | Somatostatin AnalogsUnited States
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Kirby InstituteTerminatedHepatitis CAustralia
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National Heart, Lung, and Blood Institute (NHLBI)CompletedDiabetes Mellitus | Heart Disease | Thalassemia | HemochromatosisUnited States
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University of OklahomaOU Medical CenterCompletedInfant, Premature, Diseases | Cholestasis | Gastroschisis | Intestinal Atresia | Short Bowel Syndrome | Cholestasis of Parenteral Nutrition | Total Parenteral Nutrition-induced CholestasisUnited States
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Aga Khan UniversityUnknownHyperglycemia | Anemia | Dyslipidemias | Oxidative Stress | Liver Dysfunction | Hemoglobin SCPakistan
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University of South FloridaNational Institutes of Health (NIH); University of Nebraska; Montclair State...CompletedZellweger SpectrumUnited States
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Novartis PharmaceuticalsCompletedNon-transfusion Dependent ThalassemiaThailand, Turkey, Italy, Greece, China, United Kingdom, Lebanon, Tunisia
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Gilead SciencesCompletedLong QT SyndromeUnited States, Romania, New Zealand, Germany
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RenJi HospitalCompletedCardiovascular Abnormalities | Primary Biliary CholangitisChina
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Tanta UniversityCompletedHepatitis C | Beta-ThalassemiaEgypt
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Hospices Civils de LyonCompletedLiver Transplant | Hereditary Haemorrhagic Telangiectasia
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Tanta UniversityCompletedBeta Thalassemia MajorEgypt
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Xinhua Hospital, Shanghai Jiao Tong University...UnknownBiliary Atresia | Hepatobiliary Disease | Neonatal CholestasisChina
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Mirum Pharmaceuticals, Inc.CompletedAlagille SyndromeUnited Kingdom
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Mirum Pharmaceuticals, Inc.Childhood Liver Disease Research and Education NetworkCompletedAlagille SyndromeUnited States, Canada
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Mirum Pharmaceuticals, Inc.CompletedAlagille Syndrome | Progressive Familial Intrahepatic CholestasisUnited States, Canada
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Assistance Publique - Hôpitaux de ParisNovartisCompletedAutosomal Dominant Polycystic Kidney DiseaseFrance
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Gilead SciencesCompletedHepatitis C Virus InfectionUnited States
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Federal Research Institute of Pediatric Hematology...UnknownAnesthesia | Pediatric Cancer | Beta-Thalassemia | Hepatic Metastases | Pediatric Tumor | Pediatric HepatoblastomaRussian Federation
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Ala'a ShararaGilead SciencesCompletedHepatitis C | ThalassemiaLebanon
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Stanford UniversityCompletedAlagille SyndromeUnited States
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Tanta UniversityCompletedBeta Thalassemia MajorEgypt
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Tanta UniversityCompletedBeta Thalassemia MajorEgypt
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Northwestern UniversityUniversity of Colorado, DenverCompletedCardiovascular Disease | Liver Disease
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Cairo UniversityUnknownBeta Thalassemia Major AnemiaEgypt
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Assiut UniversityUnknown
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University of Nevada, Las VegasFogarty International Center of the National Institute of HealthUnknownHepatitis B | HIV | Sickle Cell DiseaseNigeria
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University Medical Center GroningenRadboud University Medical Center; Erasmus Medical Center; Leiden University...UnknownAutosomal Dominant Polycystic Kidney Disease (ADPKD)Netherlands
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Assiut UniversityUnknown
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Novartis PharmaceuticalsCompletedThalassemia, Non-transfusional-dependent Thalassemia (NTDT), Myeloplastic Dysplasia (MDS), Other AnemiaAustralia
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Mahidol UniversityCompletedFibrosis | Hepatitis C | ThalassemiaThailand