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Search clinical trials for: Lysosomal storage disease (LSD)
Total 383724 results
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Fundación Española de Hematología y HemoterapíaRecruitingGaucher Disease | Acid SphingoMyelinase DeficiencySpain
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Cystinose StiftungCystinosis Research Network; Leben eben! Cystinose-Selbsthilfe e.V.Recruiting
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Fondazione Don Carlo Gnocchi OnlusAssociazione Italiana Glicogenosi (AIG); Associazione Riabilitatori Insufficienza... and other collaboratorsRecruitingGlycogen Storage Disease Type II | Pompe Disease (Late-onset)Italy
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Medical University of ViennaRecruitingPompe Disease | McArdle DiseaseAustria
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Eline C. B. EskesRecruiting
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Eline C. B. EskesRecruitingAsmd, Visceral TypeNetherlands
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Institut National de la Santé Et de la Recherche...Recruiting
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University of California, San FranciscoRecruiting
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Bio Sidus SARecruiting
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University of MinnesotaRecruitingGaucher DiseaseUnited States
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Cystinose StiftungScreening Laboratory Hannover; Pediatry Kastanienhof Koeln; Medical Genetics... and other collaboratorsRecruitingCystinosis | Primary HyperoxaluriaGermany
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudNot yet recruitingSanfilippo Syndrome Type CUnited States, France
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Assiut UniversityNot yet recruiting
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GeneCradle IncRecruitingPompe Disease Infantile-OnsetChina
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Massachusetts General HospitalRecruiting
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Forge Biologics, IncRecruitingKrabbe DiseaseUnited States
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Albina Nowak, MDNot yet recruiting
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Chiesi Farmaceutici S.p.A.ICON plcRecruiting
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Lysosomal and Rare Disorders Research and Treatment...Team SanfilippoRecruitingSanfilippo Syndrome | MPS3United States
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Mackay Memorial HospitalRecruiting
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Children's Hospital Medical Center, CincinnatiSanofiRecruitingFabry DiseaseUnited States
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Immusoft of CA, Inc.RecruitingMucopolysaccharidosis IH/S | Mucopolysaccharidosis ISUnited States
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Yonsei UniversityRecruitingFabry DiseaseKorea, Republic of
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TakedaNot yet recruiting
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University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital for... and other collaboratorsRecruiting
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Eunice Kennedy Shriver National Institute of Child...RecruitingNiemann-Pick Disease Type C1 | Juvenile Neuronal Ceroid Lipofuscinosis | Smith-Lemli-Opitz Syndrome | Creatine Transporter DeficiencyUnited States
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Fundación Española de Hematología y HemoterapíaRecruitingNiemann-Pick Diseases | Gaucher Disease | Splenomegaly | Acid SphingoMyelinase Deficiency | ASMDSpain
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Masonic Cancer Center, University of MinnesotaRecruitingMucopolysaccharidosis Type I | Hematopoietic Cell TransplantationUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingNiemann-Pick Disease, Type CUnited States
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University of MinnesotaRecruitingGaucher Disease, Type 3United States
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Seventh Medical Center of PLA General HospitalGeneCradle Therapeutics, IncRecruiting
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Assistance Publique - Hôpitaux de ParisCystinosis Research FoundationRecruiting
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New York Stem Cell Foundation Research InstituteSilverstein FoundationRecruitingHealthy | Parkinson Disease | Gaucher Disease | GBA Gene MutationUnited States
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Sanguine BiosciencesDenali Therapeutics Inc.RecruitingMucopolysaccharidosis III-AUnited States
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Alice BertainaCalifornia Institute for Regenerative Medicine (CIRM)RecruitingCKD Stage 4 | Cystinosis | FSGS | SLE Nephritis | SIODUnited States
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TakedaTakeda Development Center Americas, Inc.RecruitingHunter Syndrome | Mucopolysaccharidosis (MPS)United States
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National Taiwan University HospitalRecruitingStroke | Magnetic Resonance Imaging | Fabry Disease | Cerebral Small Vessel Diseases | Cadasil | HTRA1-Related Autosomal Dominant Cerebral Angiopathy | COL4A1-Related Brain Small Vessel Disease With Haemorrhage | Next-generation SequencingTaiwan
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CANbridge (Suzhou) Bio-pharma Co., Ltd.RecruitingGaucher Disease, Type 1 | Gaucher Disease, Type 3China
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Centre for Analytical Biochemistry and Biomedical...University of GiessenRecruiting
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingLate-Onset Pompe Disease | Lysosomal DiseaseUnited States
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GC Biopharma CorpRecruitingMucopolysaccharidosis II | Hunter SyndromeKorea, Republic of
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University of Roma La SapienzaAlexion PharmaceuticalsRecruitingNon-Alcoholic Fatty Liver DiseaseItaly
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Academisch Medisch Centrum - Universiteit van Amsterdam...RecruitingFabry Disease | Fabry Disease, Cardiac VariantNetherlands
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Universidade do PortoHospital da Luz, Lisboa; Hospital Pedro Hispano; Centro Hospitalar de Leiria; Centro... and other collaboratorsRecruitingFabry DiseasePortugal
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis IIUnited States, Spain, United Kingdom, Czechia, France, Canada, Italy, Belgium, Netherlands, Germany, Argentina, Sweden, Turkey, Brazil, Colombia