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Search clinical trials for: Metachromatic leukodystrophy (MLD)
Total 125 results
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Forge Biologics, IncActive, not recruiting
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruiting
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Leipzig University Medical CenterEuropean Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyGermany
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Khondrion BVJulius Clinical; ProPharma Group; CertaraCompletedMitochondrial Diseases | Mitochondrial DNA tRNALeu(UUR) m.3243A<G Mutation | Maternally Inherited Diabetes and Deafness (MIDD) | Mitochondrial Encephalomyopathy, Lactic Acidosis and Stroke Like Episodes (MELAS) | Chronic Progressive External Ophthalmoplegia (CPEO)Netherlands, Denmark, United Kingdom, Germany
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Passage Bio, Inc.SuspendedLeukodystrophy, Globoid CellUnited States, Brazil, Netherlands, United Kingdom, Canada, Israel
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Mirum Pharmaceuticals, Inc.Completed
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Kintara Therapeutics, Inc.Active, not recruitingGlioma | Glioblastoma | Brain Cancer | Glioblastoma Multiforme | GBMUnited States
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DelMar Pharmaceuticals, Inc.TerminatedGlioma | Glioblastoma | Brain Cancer | Glioblastoma Multiforme | GBMUnited States
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Kintara Therapeutics, Inc.Sun Yat-sen UniversityActive, not recruitingGlioma | Glioblastoma | Brain Cancer | Glioblastoma Multiforme | GBMChina
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CENTOGENE GmbH RostockWithdrawnKrabbe DiseaseEgypt, Germany, India, Sri Lanka
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Joanne Kurtzberg, MDDuke University; Miltenyi Biotec, Inc.AvailableHematologic Malignancies | Immune Deficiencies | Inborn Errors of Metabolism DisordersUnited States
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Primus PharmaceuticalsTerminatedIrritant Contact DermatitisUnited States
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser... and other collaboratorsCompletedX-linked AdrenoleukodystrophyUnited States
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ShirePharmaNet; Nextrials, Inc.WithdrawnLeukodystrophy, Globoid Cell
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Washington University School of MedicineCompletedVasculopathy, Retinal, With Cerebral Leukodystrophy | Cerebroretinal Vasculopathy, HereditaryUnited States
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedKrabbe Disease | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)United States
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Baylor Research InstituteCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyUnited States
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National Human Genome Research Institute (NHGRI)CompletedLeukodystrophy | LeukoencephalopathyUnited States
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Zymenex A/SCompletedInfantile Globoid Cell LeukodystrophyUnited States
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National Institute of Neurological Disorders and...CompletedLysosomal Storage DiseaseUnited States, France, Israel, Netherlands
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Children's Hospital Los AngelesCompletedGranuloma | Anemia | Thrombocytopenia | Neutropenia | Sickle Cell Disease | Thalassemia | Niemann-Pick Disease | Wiskott-Aldrich Syndrome | Osteopetrosis | Fucosidosis | Chediak Higashi Syndrome | Hurler DiseaseUnited States
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Assistance Publique - Hôpitaux de ParisEuropean Leukodystrophy AssociationWithdrawnDeficiency Disease | Canavan Disease | Infantile | Aspartoacylase | Leukodystrophy, Spongiform
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National Institute of Neurological Disorders and...CompletedHealthy | Motor Neuron Disease | Lysosomal Storage Disease | Movement Disorder | Demyelinating DiseaseUnited States
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National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiCompletedMetabolism, Inborn Errors | Leukodystrophy, Globoid Cell | Tay-Sachs Disease | Porphyria, ErythropoieticUnited States