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Search clinical trials for: X-linked agammaglobulinemia
Total 168 results
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Assistance Publique - Hôpitaux de ParisCompletedX-linked Severe Combined ImmunodeficiencyFrance
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BiogenCompleted
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Baxalta now part of ShireCompletedPrimary Immunodeficiency Diseases (PID) | Hypogammaglobulinemia | AgammaglobulinemiaFinland, Sweden
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Kedrion S.p.A.CompletedPrimary Immunodeficiency | Hypogammaglobulinemia | Agammaglobulinemia | Antibody DeficiencyUnited States, Canada
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University of FloridaAudentes TherapeuticsCompletedX-linked Myotubular MyopathyUnited States
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Hospices Civils de LyonCompleted
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedErythropoietic Protoporphyria | EPP | X-linked Protoporphyria | XLPUnited States
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Mazandaran University of Medical SciencesUnknownMultiple Sclerosis | HypogammaglobulinemiaIran, Islamic Republic of
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Advanced Neurosciences InstituteNovel Pharmaceutics InstituteUnknownMultiple Sclerosis | Infection, Bacterial | Immunodeficiency | HypogammaglobulinemiaUnited States
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Bicetre HospitalUnknownRare Diseases | X-linked HypophosphatemiaFrance
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHyperparathyroidism | Hypophosphatemia, FamilialUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...CompletedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia | Hemophagocytic Lymphohistiocytosis (HLH) | Non Hodgkins Lymphoma | Familial Hemophagocytic Lymphohistiocytosis (FLH) | Viral-associated Hemophagocytic Syndrome (VAHS) | X-linked Lymphoproliferative...United States
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Brigham and Women's HospitalCompletedInfection | Immune Deficiency | Hypogammaglobulinemia | Septic Arthritis | Mycoplasma HominisUnited States
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National Human Genome Research Institute (NHGRI)Withdrawn
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National Eye Institute (NEI)CompletedRetinoschisis | X-LinkedUnited States
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Shenzhen Geno-Immune Medical InstituteUnknown
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Onofre, Aurora Pujol, M.D.Instituto de Salud Carlos III; Fundacion Hesperia; ELA España AssociationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophySpain
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University Health Network, TorontoCSL BehringCompletedHypogammaglobulinemiaCanada
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedFatigue | Thrombocytopenia | Fever | Chronic Lymphocytic Leukemia | Lymphadenopathy | Small Lymphocytic Lymphoma | Hypogammaglobulinemia | Lymphocytosis | Night Sweats | ParaproteinemiaUnited States
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Columbia UniversityGrifols Therapeutics LLCCompletedLung Transplantation | HypogammaglobulinemiaUnited States
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Peking Union Medical College HospitalUnknownX-linked HypophosphatemiaChina
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Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyUnited States
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NeuroVia, Inc.UnknownX-Linked AdrenoleukodystrophyUnited States
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Valerion Therapeutics, LLCInstitut de Myologie, France; GenethonCompletedMyotubular MyopathyFrance, Belgium, United States, Canada, Germany, Italy, Spain
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Cure CMDUniversity of Michigan; Congenital Muscle Disease International RegistrCompleted
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University of MinnesotaNo longer availableX-linked AdrenoleukodystrophyUnited States
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Applied Genetic Technologies CorpFoundation Fighting BlindnessCompletedX-linked Retinoschisis | XLRSUnited States
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Edimer PharmaceuticalsActive, not recruitingX-linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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Soma JyonouchiBaylor College of MedicineCompletedX-linked Thrombocytopenia | Wiskott-Aldrich Syndrome (WAS)United States
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Great Ormond Street Hospital for Children NHS Foundation...UnknownX-linked Severe Combined ImmunodeficiencyUnited Kingdom
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Hospices Civils de LyonUnknownX-linked Mental RetardationFrance
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GlaxoSmithKlineCompletedAcute HIT II (Heparin-induced Thrombocytopenia Type II)
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National Institute of Allergy and Infectious Diseases...CompletedGenetic Diseases, X-Linked | Lymphoproliferative Disease | X-Linked Lymphoproliferative DiseaseUnited States
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHypophosphatemic Rickets, X Linked DominantUnited States
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University of Alabama at BirminghamGrifols Biologicals, LLCCompletedCongenital Heart Disease | HypogammaglobulinemiaUnited States
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O & O Alpan LLCUnknownAutoimmune Diseases | Hypogammaglobulinemia | Inflammatory Diseases | Primary Immune Deficiencies | Common Variable Immune DeficienciesUnited States
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Kyowa Kirin Co., Ltd.CompletedX-linked Hypophosphatemic Rickets/OsteomalaciaJapan, Korea, Republic of
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Children's Hospital Los AngelesLucile Packard Children's HospitalTerminatedMetabolic Diseases | Stem Cell Transplantation | Chronic Granulomatous Disease | Bone Marrow Transplantation | Thalassemia | Wiskott-Aldrich Syndrome | Genetic Diseases | Peripheral Blood Stem Cell Transplantation | Pediatrics | Diamond-Blackfan Anemia | Allogeneic Transplantation | Combined Immune Deficiency | X-linked Lymphoproliferative Disease
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Children's Hospital Los AngelesCompletedGranuloma | Anemia | Thrombocytopenia | Neutropenia | Sickle Cell Disease | Thalassemia | Niemann-Pick Disease | Wiskott-Aldrich Syndrome | Osteopetrosis | Fucosidosis | Chediak Higashi Syndrome | Hurler DiseaseUnited States
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Turku University HospitalUnknown
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Bicetre HospitalCompletedX Linked Hypophosphatemic Rickets
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National Institute of Allergy and Infectious Diseases...TerminatedGrowth Failure | X-linked Severe Combined Immunodeficiency (XSCID) | Growth Hormone ResistenceUnited States
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ANRS, Emerging Infectious DiseasesCompleted
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Retina Foundation of the SouthwestDSM Nutritional Products, Inc.; Foundation Fighting BlindnessCompletedRetinitis Pigmentosa | X-linked Genetic DiseasesUnited States
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Shanghai Children's Medical CenterUnknownAgammaglobulinemia, BTKChina
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FFF EnterprisesOMRIX BiopharmaceuticalsCompletedImmunologic Deficiency SyndromesUnited States, Canada
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Thomas S. ScanlanWithdrawnAdrenomyeloneuropathy | X-Linked AdrenoleukodystrophyUnited States
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University Hospital ErlangenEdimer PharmaceuticalsCompletedX-linked Hypohidrotic Ectodermal DysplasiaGermany
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Edimer PharmaceuticalsCompletedX-linked Hypohidrotic Ectodermal DysplasiaUnited States