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Search clinical trials for: Acid Lipase Deficiency
Total 35923 results
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National Institute of Allergy and Infectious Diseases...ViiV HealthcareRecruitingHIV InfectionsUnited States, Puerto Rico
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Unity Health TorontoCanadian Institutes of Health Research (CIHR); CIHR Canadian HIV Trials NetworkRecruiting
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University of California, San FranciscoMassachusetts General HospitalRecruitingCardiovascular Diseases | HIV Infections | DyslipidemiasUnited States
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ANRS, Emerging Infectious DiseasesRecruiting
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Children's Hospital of PhiladelphiaEli Lilly and Company; University of Pennsylvania; Takeda; National Institute of... and other collaboratorsRecruitingMucopolysaccharidoses | Leukoencephalopathies | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2... and other conditionsUnited States
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Travere Therapeutics, Inc.RecruitingNatural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)Homocystinuria Due to CBS DeficiencyIreland, Qatar, United States, United Kingdom
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University...Recruiting
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Assistance Publique - Hôpitaux de ParisRecruiting
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Mayo ClinicRecruitingCystinuria | Hyperoxaluria | Dent Disease | Lowe Syndrome | Adenine Phosphoribosyltransferase DeficiencyUnited States, Canada, Iceland, Israel
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Tel-Aviv Sourasky Medical CenterRambam Health Care Campus; Rabin Medical Center; Sheba Medical Center; Soroka University...Not yet recruitingLynch Syndrome I (Site-specific Colonic Cancer)Israel
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Pascoe Pharmazeutische Praeparate GmbHRecruitingChronic Disease | Acute Disease | Vitamin C DeficiencyGermany
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National Institute of Allergy and Infectious Diseases...Eunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingHIV InfectionUnited States, Puerto Rico, Argentina, Brazil, Haiti, Kenya, Malawi, South Africa, Tanzania, Thailand, Uganda, Zambia, Zimbabwe
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Gilead SciencesRecruitingHIV Infections | Acquired Immune Deficiency Syndrome (AIDS)United States, South Africa, Argentina, Panama, Thailand, Zimbabwe, United Kingdom, Uganda
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Johns Hopkins UniversityNational Cancer Institute (NCI); National Institutes of Health (NIH); ChiRhoClin...RecruitingLynch Syndrome | Pancreas Cancer | Gene Mutation | Peutz-Jeghers Syndrome (PJS) | Germline Mutation CarrierUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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National Cancer Institute (NCI)RecruitingMDS | Immunodeficiency | GATA2United States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial Disorders | Mitochondrial Genetic Disorders | Disorder of Mitochondrial Respiratory Chain Complexes | Deletion and Duplication of Mitochondrial DNAUnited States, Canada
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingPompe DiseaseUnited States
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingLiver Diseases | Alpha 1-Antitrypsin Deficiency | Alagille SyndromeUnited States, Canada
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Genzyme, a Sanofi CompanyRecruitingPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Glycogenesis 2 Acid Maltase DeficiencyCroatia, United States, Italy, Belgium, Czechia
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University of ZurichRecruitingHIV InfectionsSwitzerland
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University of FloridaRecruitingAlpha-1 Antitrypsin DeficiencyUnited States
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Genzyme, a Sanofi CompanyRecruitingGlycogen Storage Disease Type II | Pompe DiseaseHungary, Croatia, Serbia, United States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Denmark, France, Germany, Greece, Hong Kong, India, Indonesia, Israel, Italy, Japan, Jordan, Korea, Republic of, Kuwait and more
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The University of Texas Health Science Center at...National Center for Research Resources (NCRR)RecruitingGrowth Hormone Deficiency | Chromosome Aberrations | HypomyelinationUnited States
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National Human Genome Research Institute (NHGRI)RecruitingPulmonary Fibrosis | Healthy Volunteers | Hermansky-Pudlak Syndrome (HPS)United States
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National Human Genome Research Institute (NHGRI)RecruitingHermansky-Pudlak Syndrome (HPS)United States
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Thomas BenfieldCompletedCardiovascular Diseases | HIV Infections | Hiv | Weight Change, Body | HIV Lipodystrophy | HIV CardiomyopathyDenmark
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Travere Therapeutics, Inc.Enrolling by invitation
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Janssen Sciences Ireland UCActive, not recruitingHIV Infections | HIV-1United States, France, Spain, South Africa, Canada, Argentina, Thailand, Brazil, Romania, Panama, Puerto Rico
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Janssen Sciences Ireland UCActive, not recruitingHuman Immunodeficiency Virus Type 1Portugal, South Africa, Thailand, Uganda, Spain
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Children's Hospital of PhiladelphiaIllumina, Inc.Active, not recruitingMucopolysaccharidoses | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2 Gangliosidosis | Zellweger... and other conditionsUnited States
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Tuberculosis Research Centre, IndiaUnited States Agency for International Development (USAID)CompletedTuberculosis | Human Immunodeficiency VirusIndia
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National Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Stage III Colon Cancer AJCC v8 | Colon Adenocarcinoma | DNA Repair DisorderUnited States, Puerto Rico, Germany
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National Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Colon Mucinous Adenocarcinoma | Colon Signet Ring Cell Adenocarcinoma | Stage IIA Colon Cancer AJCC v7 | Stage IIB Colon Cancer AJCC v7 | Stage IIC Colon Cancer AJCC v7United States, Canada, Puerto Rico, Peru, South Africa
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National Institute of Allergy and Infectious Diseases...ViiV HealthcareCompletedHIV InfectionsUnited States, Puerto Rico
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National Institute of Allergy and Infectious Diseases...ViiV HealthcareActive, not recruitingHIV InfectionsThailand, United States, Botswana, Uganda, South Africa
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Chelsea and Westminster NHS Foundation TrustGilead Sciences; Imperial College LondonTerminatedHuman Immunodeficiency VirusUnited Kingdom
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BayerActive, not recruitingPrevention of Vitamin Deficiency During and/or Before PregnancyRussian Federation, Kazakhstan, Uzbekistan
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University Medical Centre LjubljanaCompletedBody Weight | IVF | Nutrient Deficiency | Dietary Vitamin B12 Deficiency Anemia | Dietary Folate Deficiency AnemiaSlovenia
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University College DublinViiV Healthcare; Mater Misericordiae University HospitalTerminatedHuman Immunodeficiency VirusIreland
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University of Novi Sad, Faculty of Sport and Physical...Completed
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University of California, DavisPenn State University; University of Ghana; Newcastle University; Helen Keller...Active, not recruitingIron-deficiency | Anemia | Vitamin A Deficiency | Vitamin B 12 Deficiency | Folate Deficiency | Zinc DeficiencyGhana
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University of British ColumbiaHelen Keller International; NCHADS - Ministry of Health of Cambodia; BC Children... and other collaboratorsCompletedInflammation | Anemia | Anemia, Iron Deficiency | Intestinal Inflammation | Intestine; ComplaintsCambodia
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University of California, DavisUniversity of California, San Francisco; Ethiopian Public Health Institute; Nutrition...CompletedFolate Deficiency | Iodine Deficiency | Anemia, Macrocytic | Anemia Deficiency | Salt IntakeEthiopia
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University of WashingtonBill and Melinda Gates FoundationCompletedHIV InfectionsKenya, Malawi, South Africa, Swaziland, Uganda, Zambia, Zimbabwe
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University of California, San FranciscoGilead Sciences; ViiV HealthcareActive, not recruiting
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Institut PasteurUniversity of Copenhagen; Institut CochinCompletedDiarrhea | InfantileFrance, New Caledonia, Central African Republic
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University of NebraskaUniversity of Colorado, Denver; University of Pittsburgh; Children's Hospital...Completed
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Medical University of ViennaCompletedHyperemesis Gravidarum | Nausea Gravidarum | Vitamin C DeficiencyAustria