- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Congenital Myasthenic Syndrome
Total 44400 results
-
Assistance Publique - Hôpitaux de ParisNot yet recruitingPeriodontitis | Trisomy 21France
-
Children's Hospital Medical Center, CincinnatiRecruitingFragile X SyndromeUnited States
-
Fondazione Policlinico Universitario Agostino Gemelli...University of Florence; Campus Bio-Medico UniversityNot yet recruitingRare Diseases | Congenital DisordersItaly
-
Institut National de la Santé Et de la Recherche...RecruitingNeurofibromatosis Type 1 | Ichthyosis | Ectodermal Dysplasia | Albinism | Pemphigus | Mucous Membrane Pemphigoid | Inherited Epidermolysis Bullosa | Palmoplantar Keratoderma | Incontinentia PigmentiFrance
-
M.D. Anderson Cancer CenterRecruitingVon Hippel Lindau DiseaseUnited States
-
Centre Hospitalier Universitaire DijonNot yet recruitingKosaki Overgrowth Syndrome | Penttinen SyndromeFrance
-
Institut National de la Santé Et de la Recherche...RecruitingPrader-Willi Syndrome | Angelman Syndrome | Beckwith-Wiedemann Syndrome | Pseudohypoparathyroidism | Silver Russell Syndrome | Transient Neonatal Diabetes Mellitus | Temple Syndrome | Kagami-Ogata Syndrome | Familial Precocious PubertyFrance
-
Academisch Medisch Centrum - Universiteit van Amsterdam...Netherlands Organisation for Scientific ResearchRecruiting
-
Maimonides Medical CenterFoundation for Prader-Willi ResearchRecruitingBody Weight | Hyperphagia | Prader-Willi Syndrome | Mood | Behavior | Excessive Daytime SleepinessUnited States
-
Brigham and Women's HospitalFoundation for Prader-Willi ResearchRecruiting
-
University of ArizonaNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...RecruitingMedications for Obstructive Sleep Apnea to Improve Cognition in Children With Down Syndrome (MOSAIC)Obstructive Sleep Apnea | Down SyndromeUnited States
-
Rambam Health Care CampusRecruitingBronchiectasis | Cystic Fibrosis | Bronchiolitis Obliterans | Primary Ciliary Dyskinesia | Primary Immune DeficiencyIsrael
-
Institut National de la Santé Et de la Recherche...Recruiting
-
Instituto de fertilidad humana, InSerUniversity of Alabama at Birmingham; Colmédicos S.A.S.; ABAD LaboratorioRecruitingEndocrine System Diseases | Polycystic Ovary Syndrome | HyperandrogenismColombia
-
Cairo UniversityRecruiting
-
Third Military Medical UniversityNot yet recruitingPrimary Aldosteronism Due to Aldosterone Producing Adenoma | Primary Aldosteronism Due to Adrenal Hyperplasia (Bilateral)China
-
UMC UtrechtEindhoven University of TechnologyRecruiting22q11.2 Deletion Syndrome | Adolescent Idiopathic ScoliosisNetherlands
-
Tao ZhangRecruitingHypospadias | Caudal Block | Pediatrics | Postoperative Analgesia | S-ketamineChina
-
Maastricht University Medical CenterZonMw: The Netherlands Organisation for Health Research and DevelopmentRecruitingHemodialysis Access Failure | Arteriovenous Fistula | Vascular Access Complication | Arteriovenous Graft | Dialysis Access Malfunction | Central Venous Catheter Related Bloodstream InfectionNetherlands
-
Thryv Therapeutics, Inc.Recruiting
-
Crinetics Pharmaceuticals Inc.RecruitingCongenital Adrenal Hyperplasia | Classic Congenital Adrenal HyperplasiaBrazil, India, United States, Argentina, Italy, United Kingdom
-
Cairo UniversityRecruiting
-
Hereditary Neuropathy FoundationRecruitingCharcot-Marie-Tooth Disease | Charcot-Marie-Tooth Disease, Type IA | Charcot-Marie-Tooth Disease Type 2A | Charcot-Marie-Tooth | Charcot-Marie-Tooth Disease, Type IB | Charcot-Marie-Tooth Disease Type 2 | Charcot-Marie-Tooth Disease, Type 2C | Charcot-Marie-Tooth Disease Type 2A2B | Charcot-Marie-Tooth... and other conditionsUnited States
-
Assistance Publique - Hôpitaux de ParisNot yet recruiting
-
Maxima Medical CenterRecruitingChronic Pain Syndrome | Nerve Entrapment Syndrome | Anterior Cutaneous Nerve Entrapment SyndromeNetherlands
-
Istituto Ortopedico RizzoliRecruitingCollagen Diseases | Joint Hypermobility | Hypermobility Syndrome | Laxity of Ligament | Danlos Disease, EhlersItaly
-
Jazz PharmaceuticalsRecruitingTuberous Sclerosis Complex Associated Neuropsychiatric DiseaseUnited States, United Kingdom, Poland
-
Cairo UniversityRecruiting
-
CHU de Quebec-Universite LavalRecruiting
-
Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Finland, Switzerland, Netherlands, Portugal
-
Cairo UniversityRecruiting
-
Roopa Kanakatti Shankar, MBBS, MSRecruiting
-
Innovation Research & TrainingRecruiting
-
Betta Pharmaceuticals Co., Ltd.Not yet recruitingRenal Cell Carcinoma | Solid Tumor | Von Hippel-Lindau DiseaseChina
-
University Hospital, ToulouseNot yet recruiting
-
Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingCornelia de Lange SyndromeUnited States
-
National Heart, Lung, and Blood Institute (NHLBI)RecruitingSteroid-refractory Diamond-Blackfan Anemia (DBA)United States
-
Peking Union Medical College HospitalRecruiting
-
Baylor College of MedicineSouthern Star Research Pty Ltd.Recruiting
-
Franziska WachterHarvard Clinical and Translational Science Center (Harvard Catalyst)RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | MDS | Aml | Myeloid Neoplasm | Myeloid Malignancies | Inherited Bone Marrow Failure SyndromeUnited States
-
Children's Hospital of Fudan UniversityRecruitingPrader-Willi SyndromeChina
-
Quoin PharmaceuticalsRecruitingNetherton SyndromeUnited States
-
Tianjin First Central HospitalNot yet recruitingDesflurane | Biliary Atresia | Pediatric Acute Respiratory Distress SyndromeChina
-
Cardiff UniversityUniversity of CanterburyRecruitingCleft Lip and Palate | Parenting | Neurofibromatoses | Skin Condition | Alopecia | Craniofacial | Limb DifferenceUnited Kingdom
-
The Third Xiangya Hospital of Central South UniversityNot yet recruitingCharcot-Marie-Tooth Disease (CMT)
-
Istituto Auxologico ItalianoRecruitingPrader-Willi SyndromeItaly
-
Institut Jerome LejeuneRecruitingGenetic Markers and Biomarkers in Patients With Intellectual Disabilities of Genetic Origin (BioJeL)Intellectual Disability | Down SyndromeFrance
-
Institut Jerome LejeuneRecruiting