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Search clinical trials for: Expanded access
Total 3661 results
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University of MiamiTemporarily not availableStroke, Ischemic | Stroke, Acute | Mesenchymal Stem Cells | Acute Ischemic Stroke | Stroke/Brain AttackUnited States
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Janssen-Cilag, S.A.Completed
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Catalyst Pharmaceuticals, Inc.No longer availableLambert-Eaton Myasthenic Syndrome | Congenital Myasthenic Syndrome | Nystagmus, AcquiredUnited States
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Humacyte, Inc.AvailableVascular Diseases | End Stage Renal Disease on Dialysis | Vascular System Injuries
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Relmada Therapeutics, Inc.AvailableDepression | Major Depressive Disorder
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PfizerIn Expanded Access, treating physicians are the SponsorsAvailable
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Celcuity, Inc.AvailableBreast Neoplasm Malignant FemaleUnited States
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St. Jude Children's Research HospitalAvailableHead and Neck Neoplasms | Central Nervous System TumorUnited States
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xCuresCancer CommonsAvailableExpanded Access to Ulixertinib (BVD-523) in Patients With Advanced MAPK Pathway-Altered MalignanciesMelanoma | Head and Neck Cancer | Glioblastoma | Hepatocellular Carcinoma | Gastric Cancer | Colorectal Cancer | Pancreatic Cancer | Esophageal Cancer | Small Bowel Cancer | Ovarian Cancer | Non Small Cell Lung Cancer | Cholangiocarcinoma | Bladder Cancer | Thyroid Cancer | ERK Mutation | MAPK Gene Mutation | KRAS Activating... and other conditionsUnited States
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Children's Hospital Medical Center, CincinnatiNo longer availableNeuroblastoma | Pheochromocytoma | ParagangliomaUnited States
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Ascendis Pharma Bone Diseases A/SClinigen Healthcare LtdAvailable
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Tasly Pharmaceuticals, Inc.Tasly Pharmaceutical Group Co., LtdNo longer available
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AVM Biotechnology IncAvailableCancer | Breast Cancer | Glioblastoma | Gastric Cancer | Pancreatic Cancer | Hodgkin Lymphoma | Ovarian Cancer | Prostate Cancer | Acute Leukemia | Non-hodgkin Lymphoma | Squamous Cell Carcinoma | Tumor, Solid | Tumor, Brain | Spindle Cell Sarcoma
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Gamida Cell ltdActive, not recruitingHematological MalignanciesUnited States
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Amicus TherapeuticsAvailablePompe Disease Infantile-OnsetTaiwan, United States, Italy
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Amicus TherapeuticsAvailable
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ShireTakeda Development Center Americas, Inc.No longer availableAngioedema | Hereditary Angioedema (HAE)United States, Canada, Germany, Hungary, Spain
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PfizerNo longer availableSickle Cell DiseaseUnited States
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John MarisAvailableNeuroblastoma | Childhood Metastatic PheochromocytomaUnited States
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Lynkcell EuropeAvailableKidney Cancer | Clear Cell Kidney Cancer | Kidney Cancer With PBRM1/BAP1/VHL/SETD2 Mutations
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TVAX BiomedicalAvailable
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Regeneron PharmaceuticalsAvailable
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Genelux CorporationTemporarily not availableAdvanced Stage Cancer (Solid Tumor Disease for 4 Patients) | Acute Myeloid Leukemia (6 Patients)United States
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TakedaCompletedHereditary AngioedemaJapan
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The University of Texas Health Science Center at...Temporarily not availableGastrointestinal Stromal Tumor
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Atara BiotherapeuticsNo longer availableLymphoproliferative Disorders | Stem Cell Transplant Complications | Epstein-Barr Virus (EBV) Infections | EBV+ Associated Lymphoma | EBV+ Associated Post-transplant Lymphoproliferative Disease (EBV+ PTLD) | Epstein-Barr Viremia | Lymphoma, AIDS-related | Epstein-Barr Virus-associated Lymphoproliferative... and other conditions
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Seres Therapeutics, Inc.Approved for marketingClostridioides Difficile Infection
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availablePrimary Lateral Sclerosis, Adult, 1United States
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Jonathan GerberNo longer availableCOVID | Corona Virus Infection | Sars-CoV2United States
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GenmabAbbVieApproved for marketingPrimary Mediastinal Large B-cell Lymphoma (PMBCL) | Large B-cell Lymphoma | Diffuse Large B-Cell Lymphoma, Not Otherwise Specified | High Grade B-cell Lymphoma (HGBCL) | Grade 3B Follicular Lymphoma
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Mirati Therapeutics Inc.Approved for marketingMetastatic Cancer | Advanced Cancer | Malignant NeoplasmUnited States
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Morand Piert, MDNo longer availableProstate Adenocarcinoma
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Basilea PharmaceuticaAvailableIntrahepatic Cholangiocarcinoma
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Mesoblast International SàrlAvailableMultisystem Inflammatory Syndrome in Children (MIS-C) Associated With Coronavirus Disease (COVID-19)
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availableParkinson DiseaseUnited States
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availableSystem; Lupus ErythematosusUnited States
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I-Mab Biopharma US LimitedNo longer availableCancerUnited States
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Santhera PharmaceuticalsNo longer availableLeber's Hereditary Optic Neuropathy
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Santhera PharmaceuticalsNo longer availableDuchenne Muscular DystrophyUnited States
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Tisch Multiple Sclerosis Research Center of New...No longer available
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Northwell HealthCohen Children's Medical CenterAvailableNeuroblastoma | PheochromocytomaUnited States
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TakedaAvailableThrombotic Thrombocytopenic Purpura (TTP)
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Sellas Life Sciences GroupAvailableAcute Myeloid Leukemia | Myelodysplastic Syndromes
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Chiesi Farmaceutici S.p.A.Chiesi USA, Inc.AvailableFabry DiseaseUnited States
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Stealth BioTherapeutics Inc.AvailableMitochondrial Diseases | Barth Syndrome