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Search clinical trials for: Glycogen Storage Disorders
Total 146052 results
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AO GENERIUMRecruitingMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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SanofiRecruitingFabry DiseaseChina, Finland, Germany, Norway, United Kingdom, United States, Denmark, Austria, Greece, Romania, Argentina, Brazil, Canada, Japan, Mexico, Poland, Italy, France, Turkey, Australia, Switzerland
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University of Alabama at BirminghamNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingType 2 DiabetesUnited States
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ModernaTX, Inc.RecruitingGlycogen Storage DiseaseUnited States, Canada
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University Hospital Center of MartiniqueRecruiting
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University of Erlangen-Nürnberg Medical SchoolRecruitingPompe Disease (Late-onset) | Pompe Disease | Pompe's Disease Juvenile Onset | Pompe Disease Infantile-OnsetGermany
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National Institute of Allergy and Infectious Diseases...RecruitingCrohn's Disease | Glycogen Metabolism | Inflammatory Bowel Disease (IBD)United States
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Maastricht UniversityRecruiting
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TakedaRecruiting
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Chang Gung Memorial HospitalRecruitingFabry DiseaseTaiwan
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Consorci Sanitari de l'Alt Penedès i GarrafRecruitingLiver Diseases | Type 1 Diabetes | Non-alcoholic Fatty Liver Disease | Glycogen HepatopathySpain
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Istanbul University - Cerrahpasa (IUC)The Scientific and Technological Research Council of TurkeyRecruitingStroke | Multiple Sclerosis | Parkinson DiseaseTurkey
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Taipei Veterans General Hospital, TaiwanNot yet recruitingGlycogen Storage Disease Type II
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Hong Kong Children's HospitalRecruitingGlycogen Storage Disease Type IBHong Kong
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National Taiwan University HospitalRecruiting
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Duke UniversityRecruiting
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Central Hospital, Nancy, FranceRecruitingPompe's Disease Juvenile OnsetFrance
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Rigshospitalet, DenmarkDanish Research Center for Magnetic ResonanceRecruitingGlycogen Storage Disease | Pompe Disease (Late-onset) | McArdle DiseaseDenmark
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Assistance Publique - Hôpitaux de ParisRecruitingAdrenoleukodystrophy | Adrenomyeloneuropathy | Metachromatic Leukodystrophy | Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaFrance
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SanofiRecruitingGlycogen Storage Disease Type IIBelgium, United States, China, Germany, Italy, Netherlands, Spain, Taiwan, United Kingdom
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University of Sao Paulo General HospitalPfizerRecruiting
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University of California, San FranciscoRecruitingSphingolipidoses | Enzyme DeficiencyUnited States
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University Health Network, TorontoUniversity of Colorado, Denver; Mayo Clinic; Icahn School of Medicine at Mount... and other collaboratorsRecruiting
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Hospital Clinico Universitario de SantiagoAlvaro Hermida (Co-IP); Susana Belen Bravo; Maria Teresa Cardoso; Cristobal Colon... and other collaboratorsRecruiting
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SanofiRecruitingGlycogen Storage Disease Type IIBelgium, United States, Italy, Spain, Taiwan, United Kingdom, Netherlands, France, Germany
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SanofiRecruitingAcid SphingoMyelinase Deficiency | Gaucher Disease, SplenomegalyFrance
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Albina Nowak, MDSwiss National Science FoundationRecruiting
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Amicus TherapeuticsRecruitingGlycogen Storage Disease Type II Infantile OnsetUnited States, Taiwan, France, Germany, Italy, United Kingdom
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Assiut UniversityNot yet recruitingPsychiatric Problem | Wolman Disease
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Rambam Health Care CampusRecruitingPompe Disease Infantile-OnsetIsrael
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Binghamton UniversityState University of New York - Upstate Medical UniversityNot yet recruitingPoisoning | Safety Issues | Accidents Injury
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Yonsei UniversityRecruitingFabry DiseaseKorea, Republic of
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Duke UniversitySanofiRecruiting
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SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt)RecruitingGangliosidoses | Galactosialidosis | Sialidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Morquio B Disease | Gm2-Gangliosidosis, Variant B1 | GM2 Activator DeficiencyGermany
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Universitätsklinikum Hamburg-EppendorfRecruitingBatten Disease | Neuronal Ceroid Lipofuscinosis | CLN1 Disease | CLN2 Disease | CLN3 Disease | CLN4 Disease | CLN5 Disease | CLN6 Disease | CLN7 Disease | CLN8 Disease | CLN10 Disease | CLN11 Disease | CLN12 Disease | CLN13 Disease | CLN14 DiseaseGermany
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JCR Pharmaceuticals Co., Ltd.RecruitingMucopolysaccharidosis IIUnited States, Germany, Spain, France, Brazil, Argentina, Turkey, United Kingdom, Poland, Italy
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Serhat Gumrukcu, MD PhDFrida Therapeutics LLCRecruiting
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Duke UniversityKriya TherapeuticsRecruitingGlycogen Storage Disease VI | GLYCOGEN STORAGE DISEASE IXa1 | GLYCOGEN STORAGE DISEASE IXa2 | Glycogen Storage Disease IXB | Glycogen Storage Disease IXC | GSD 9 (All Subtypes) | GSD 6United States
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Institut National de la Santé Et de la Recherche...Not yet recruitingFabry Disease
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Sun Yat-sen UniversityRecruitingBreast Cancer | Cognitive Impairment | Brain Metastases | Radiotherapy Side Effect | Gangliosidosis, GM1China
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Shaare Zedek Medical CenterRecruitingParkinson Disease | Gaucher Disease | GBA Gene MutationIsrael
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Amicus TherapeuticsRecruiting
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Boston Children's HospitalRecruiting
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, United Kingdom
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PfizerArena is a wholly owned subsidiary of PfizerRecruitingCrohn's DiseaseUnited States, Korea, Republic of, Netherlands, Colombia, Israel, Italy, Lebanon, Mexico, Poland, Spain, Turkey, Australia, Georgia, Czechia, Belgium, Germany, South Africa, Greece, Russian Federation, United Kingdom, Croatia, Serbia and more
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Pacific Parkinson's Research CentreUniversity of British Columbia; Oregon Health and Science University; University... and other collaboratorsRecruitingParkinson Disease | Gaucher Disease | GBA Gene MutationUnited States, Canada
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University of PennsylvaniaPassage Bio, Inc.RecruitingGM1 GangliosidosisUnited States, Turkey, Brazil, Canada, United Kingdom
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Amicus TherapeuticsRecruitingFabry DiseaseSpain, United States, Japan, Australia, France, Portugal
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Fondazione SISA (Societa Italiana per lo Studio...Recruiting
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National Human Genome Research Institute (NHGRI)Sio Gene TherapiesRecruitingGangliosidosis | Lysosomal Diseases | GM1United States