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Search clinical trials for: Hereditary Transthyretin Amyloidosis
Total 3474 results
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University of MessinaUniversità degli Studi di Ferrara; University of Pavia; Careggi Hospital; Fondazione...UnknownPatient-Reported Outcome Measures in Wild-Type and Variant Cardiac Transthyretin Amyloidosis (ITALY)Transthyretin AmyloidosisItaly
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Prothena Biosciences LimitedTerminatedAmyloidogenic Transthyretin (ATTR) AmyloidosisUnited States, Spain, Sweden, Portugal
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Alnylam PharmaceuticalsCompletedTTR-mediated AmyloidosisUnited States, Canada, United Kingdom
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Fábio FernandesPfizerUnknown
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Novartis PharmaceuticalsCompletedHereditary Periodic Fevers | Systemic Juvenile Idiopathic ArthritisFrance
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University of MessinaCampisi MariapaolaUnknownCardiac AmyloidosisItaly
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GlaxoSmithKlineTerminated
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Thibaud DamyCompletedCardiac Amyloidosis | Hypertrophic Cardiomyopathy (HCM) | Amyloidosis in Transthyretin (TTR)France
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Ionis Pharmaceuticals, Inc.Approved for marketingAmyloidosis, Hereditary
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinNew Zealand, United States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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Boston UniversityCorino Therapeutics, Inc.CompletedTransthyretin Amyloidosis | Amyloidosis, Leptomeningeal, Transthyretin-RelatedUnited States
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PfizerCompletedTransthyretin (TTR) Amyloid CardiomyopathyUnited States, Spain, Czechia, Canada, Belgium, Netherlands, Germany, Japan, France, United Kingdom, Brazil, Italy, Sweden
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Alnylam PharmaceuticalsCompletedATTR Amyloidosis | Transthyretin (TTR)-Mediated Amyloidosis | Familial Amyloidotic Polyneuropathy (FAP) | Familial Amyloid NeuropathiesFrance, Germany, Portugal, United Kingdom, Sweden, Spain
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Rabin Medical CenterUnknown
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Novartis PharmaceuticalsCompletedPeriodic Fevers SyndromeJapan
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Novartis PharmaceuticalsCompletedHereditary Periodic FeversBelgium, Italy, Japan, Russian Federation, Turkey, Spain, Germany, United Kingdom, France, United States, Ireland, Israel, Canada, Hungary, Netherlands, Switzerland
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University Hospital Center of MartiniqueCompletedLeft Ventricular HypertrophyGuadeloupe, Martinique
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Boston UniversityCompleted
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Boston UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Food and Drug...CompletedFamilial Amyloid Polyneuropathy | Familial AmyloidosisUnited States, Italy, Japan, Sweden, United Kingdom
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SOM Innovation Biotech SAHospital Vall d'HebronCompleted
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Brigham and Women's HospitalGlaxoSmithKline; Ionis Pharmaceuticals, Inc.Withdrawn
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Alnylam PharmaceuticalsCompletedFamilial Amyloidotic Cardiomyopathy (FAC)United States, France, Spain, United Kingdom, Belgium, Brazil
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Umeå UniversityCompletedTransthyretin Amyloidosis | CardiomyopathySweden
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Heidelberg UniversityCharite University, Berlin, Germany; University of Kiel; Ludwig-Maximilians -... and other collaboratorsUnknownAmyloidosis | Acute Myocarditis | Dilated Cardiomyopathies | Hypertrophic Cardiomyopathies | Left Ventricular Myocardial Noncompaction Cardiomyopathy | Arrhythmogenic Right Ventricular CardiomyopathiesGermany
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IRCCS Policlinico S. MatteoCompletedTransthyretin AmyloidosisItaly
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PfizerCompletedTransthyretin Familial Amyloid PolyneuropathyJapan
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Umeå UniversityCompleted
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Alnylam PharmaceuticalsCompletedA Study of the Safety, Tolerability and Pharmacokinetics of ALN-TTR02 in Japanese Healthy VolunteersTransthyretin (TTR)-Mediated AmyloidosisUnited Kingdom
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PfizerCompletedTransthyretin-associated Amyloidosis With PolyneuropathyUnited States, France, Germany, Italy
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PfizerCompleted
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Alnylam PharmaceuticalsCompletedTransthyretin Mediated Amyloidosis (ATTR)United Kingdom, France, Portugal, Sweden
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Timothy PoteruchaPfizer; American Heart Association; Eidos Therapeutics, a BridgeBio companyRecruiting
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Ascidian Therapeutics, IncRecruitingStargardt Disease | Stargardt Disease 1 | Juvenile Macular Degeneration | Cone Rod DystrophyUnited States
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Peter TimoneyInflammasome TherapeuticsNot yet recruiting
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KalVista Pharmaceuticals, Ltd.Not yet recruiting
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Acibadem UniversityBoston Children's Hospital; Ege UniversityRecruitingPTEN Hamartoma Tumor Syndrome | Macrocephaly Autism SyndromeTurkey
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Ray Therapeutics, Inc.Not yet recruitingRetinitis PigmentosaUnited States
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PYC TherapeuticsNot yet recruitingAutosomal Dominant Optic Atrophy | Kjer Optic Atrophy | OPA1 Gene Mutation | Hereditary Optic Atrophies
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Helse Møre og Romsdal HFNot yet recruitingCarpal Tunnel Syndrome | Cardiac Amyloidosis | ATTR Amyloidosis Wild Type | ATTR Gene Mutation
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Yongyong MARecruiting
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PYC TherapeuticsNot yet recruitingEye Diseases | Retinal Degeneration | Retinal Dystrophies | Retinal Disease | Retinitis Pigmentosa 11United States
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Ataturk UniversityRecruiting
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London North West Healthcare NHS TrustRecruitingLynch Syndrome | Polyposis Syndrome, Hereditary Mixed, 1 | Polyposis Syndrome, Hereditary Mixed, 2United Kingdom
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Ascidian Therapeutics, IncRecruitingStargardt Disease | Stargardt Disease 1 | Juvenile Macular Degeneration | Cone Rod DystrophyUnited States
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Radboud University Medical CenterNot yet recruitingPheochromocytoma | Paraganglioma
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Splice BioRecruitingStargardt Disease | Stargardt's Disease | STGD1 | StargardtUnited States
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Universitätsklinikum Hamburg-EppendorfRecruitingFamilial Adenomatous Polyposis | Adenomatous Polyposis Coli | Duodenal AdenomaGermany
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IRCCS San RaffaeleRecruitingHereditary NeuropathyItaly
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Gérond'ifNot yet recruitingCardiac AmyloidosisFrance
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University of North Carolina, Chapel HillNorth Carolina Translational and Clinical Sciences InstituteNot yet recruitingColorectal Cancer | Rectal Cancer | Rectal Neoplasms | Colon Cancer | Colon Adenocarcinoma | Colon Rectal Cancer | Hereditary Nonpolyposis Colon CancerUnited States