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Search clinical trials for: Metabolic abnormalities
Total 77171 results
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Hospices Civils de LyonRecruitingFibrous Dysplasia of BoneFrance
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ETH ZurichUniversity of Zurich; Agroscope Liebefeld-Posieux Research Station ALP; Swiss...RecruitingLactose IntoleranceSwitzerland
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St. Joseph's Hospital and Medical Center, PhoenixTexas Tech UniversityNot yet recruitingCognitive Dysfunction | Neurodegenerative Disease, Hereditary | Cognitive Impairment, Mild | Amyloid Plaque | Inflammation, Brain
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Minoryx Therapeutics, S.L.RecruitingX-linked AdrenoleukodystrophyFrance
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ACADIA Pharmaceuticals Inc.RecruitingHyperphagia in Prader-Willi SyndromeUnited States, Canada, United Kingdom
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...Not yet recruiting
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BioMarin PharmaceuticalPicnicHealthRecruitingAchondroplasiaUnited States
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Qilu Hospital of Shandong UniversityRecruitingFabry Disease | Hypertrophic Cardiomyopathy | Left Ventricular HypertrophyChina
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Gianni SoraruMario Negri Institute for Pharmacological ResearchRecruitingSpinal and Bulbar Muscular AtrophyItaly
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Assistance Publique - Hôpitaux de ParisNot yet recruitingMulti-organ Failure After Severe TraumaFrance
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Assiut UniversityNot yet recruiting
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Verve Therapeutics, Inc.Not yet recruitingHeterozygous Familial Hypercholesterolemia | Premature Coronary Heart Disease
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University of CincinnatiRecruiting
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He HuangLingyi Biotech Co., Ltd.Recruiting
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Royal Marsden NHS Foundation TrustRecruitingLynch Syndrome | Familial Adenomatous Polyposis | Hereditary Diffuse Gastric Cancer | Peutz-Jeghers Syndrome | Cowden Syndrome | Li Fraumeni Syndrome | MutYH-associated Polyposis | SMAD4 Gene MutationUnited Kingdom
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University of BonnRecruitingHypophosphatasiaGermany
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Karolinska InstitutetRecruitingCardiovascular Diseases | Dyslipidemias | Hereditary DiseasesSweden
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Women and Infants Hospital of Rhode IslandRecruitingPregnancy Complications | Gestational Diabetes | Fetal Macrosomia | Pregnancy in DiabeticUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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University College London HospitalsCure Parkinson'sRecruitingParkinson DiseaseUnited Kingdom
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy
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Orchard TherapeuticsRecruitingMPS-IH (Hurler Syndrome)Netherlands, United States, Italy, United Kingdom
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Amir MoheetRecruitingCystic Fibrosis | Cystic Fibrosis-related DiabetesUnited States
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Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Netherlands
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ModernaTX, Inc.RecruitingPhenylketonuriaUnited States, Australia
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Assistance Publique - Hôpitaux de ParisNot yet recruitingHemophilia A | Hemophilia B | Cystic Fibrosis | Sickle Cell Disease | Muscular Dystrophy, Duchenne | Fragile X Syndrome | Huntington Disease | Myotonic Dystrophy | Autosomal Recessive Polycystic Kidney Disease | Neurofibromatosis-Noonan Syndrome | Muscular Dystrophy, Becker | Invasive PreNatal Diagnosis in a... and other conditionsFrance
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Mitsubishi Tanabe Pharma America Inc.RecruitingErythropoietic Protoporphyria (EPP) | X-Linked Protoporphyria (XLP)United States, Spain, France, Japan, United Kingdom, Italy, Australia, Poland, Bulgaria, Czechia, Netherlands
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Foundation for Prader-Willi ResearchRTI InternationalRecruitingPrader-Willi SyndromeUnited States
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Jiangsu HengRui Medicine Co., Ltd.Not yet recruitingGout With Hyperuricemia in Adults
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Assistance Publique - Hôpitaux de ParisRecruiting
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PYC TherapeuticsRecruitingOptic Atrophies, Hereditary | Autosomal Dominant Optic Atrophy | Optic Atrophy, Autosomal Dominant | Kjer Optic AtrophyAustralia
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Azienda Ospedaliero-Universitaria di ModenaRecruitingIron Overload | Hemochromatosis | Thalassemia Major | Thalassemia Intermedia | EndocrinopathyItaly
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Peking University Third HospitalPeking UniversityRecruitingHeart Failure | Percutaneous Coronary Intervention | Cardiometabolic Syndrome | Structural Heart AbnormalityChina
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McMaster UniversityNot yet recruitingObesity | Lysosomal Storage Diseases | Muscle Loss | Glycogen Storage Disease Type II | Pompe Disease | Nutrition Poor | Glycogen Storage Disease Type II, Adult | Glycogen Storage Disease Type II Late Onset
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Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand, Canada
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Martin DichgansRecruitingCerebral Amyloid AngiopathyGermany
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Lille Catholic UniversityUniversity of Lille Nord de FranceNot yet recruitingPulmonary Disease, Chronic Obstructive | Pulmonary FibrosisCanada, France
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First Affiliated Hospital Xi'an Jiaotong UniversityRecruitingHomozygous Familial HypercholesterolemiaChina
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Vanderbilt University Medical CenterRecruitingDuchenne Muscular DystrophyUnited States
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Assistance Publique - Hôpitaux de ParisMinistry of Health, FranceRecruitingObesity, Morbid | ARDS, HumanFrance
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Amicus TherapeuticsRecruitingPompe DiseaseUnited States, Germany
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Lysosomal and Rare Disorders Research and Treatment...RecruitingBone Diseases | Gaucher DiseaseUnited States
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Gustave Roussy, Cancer Campus, Grand ParisMerck Sharp & Dohme LLCNot yet recruiting
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Oulu University HospitalUniversity of Oulu; Academy of Finland; Roche Diagnostics; PerkinElmer, Inc.; Sigrid... and other collaboratorsRecruitingCardiovascular Diseases | Polycystic Ovary Syndrome | Iron-deficiency | Pre-Eclampsia | Intrauterine Growth Restriction | Hypertensive Disorder of Pregnancy | Proteinuria in PregnancyFinland
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AceLink Therapeutics, Inc.Tigermed Consulting Co., LtdRecruiting
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Verve Therapeutics, Inc.Not yet recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Hospices Civils de LyonNot yet recruitingLowry Wood Syndrome | Roifman Syndrome | Taybi Linder Syndrome | Microcephalic Osteodysplastic Primordial Dwarfism Types I and IIIFrance
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Novozymes A/SAnalyze & RealizeNot yet recruiting
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Centre Hospitalier Universitaire de la RéunionRecruitingLipodystrophy | Dunnigan SyndromeRéunion