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Search clinical trials for: Mucopolysaccharidosis (mps) ii
Total 31666 results
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Novartis PharmaceuticalsCompletedRenal TransplantationUnited States
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TakedaTakeda Development Center Americas, Inc.RecruitingHunter Syndrome | Mucopolysaccharidosis (MPS)United States
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Lundquist Institute for Biomedical Innovation at...National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosesUnited States
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Greenwood Genetic CenterShriners Hospitals for Children; BioMarin PharmaceuticalCompletedMPS IVA | Maroteaux Lamy Syndrome | MPS VI | Morquio Syndrome AUnited States
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NovartisCompleted
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | Mucopolysaccharidosis VII | MPS VIIUnited States, Brazil, Mexico, Portugal
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Otsuka Pharmaceutical Co., Ltd.CompletedParkinson's DiseaseJapan
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Meiji Pharma Spain S.A.CompletedCOVID-19 PneumoniaSpain
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Orchard TherapeuticsRecruitingMPS-IH (Hurler Syndrome)Netherlands, United States, Italy, United Kingdom
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Cancer Advances Inc.Clinical Project Services; MPS Research UnitCompleted
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis (MPS)United States, Argentina, Mexico, Spain, United Kingdom
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Cairo UniversityNot yet recruitingMyofascial Pain Syndrome | Trigger Point Pain, Myofascial
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Auburn UniversityCompletedSkeletal Muscle
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Novartis PharmaceuticalsCompleted
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Dana-Farber Cancer InstituteCharles H. Hood FoundationRecruitingMyelodysplastic Syndromes | Leukemia | Myeloproliferative SyndromeUnited States
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Lundquist Institute for Biomedical Innovation at...Active, not recruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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Alexion PharmaceuticalsCompletedMucopolysaccharidosis IIIBUnited States, United Kingdom, Spain
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University of Milano BicoccaRecruiting
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Johannes Gutenberg University MainzUnknownMucopolysaccharidosis | Fabry DiseaseGermany
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Nanfang Hospital of Southern Medical UniversityPeking University People's Hospital; Sun Yat-sen University; Guangzhou First... and other collaboratorsUnknownThrombocytopenia | Hematological DiseasesChina
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BioMarin PharmaceuticalApproved for marketingMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, Puerto Rico
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Frank VandenabeeleJessa HospitalRecruiting
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NovartisCompleted
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Patricia I. Dickson, M.D.National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Cognitive Decline | Hurler-Scheie SyndromeUnited States
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Patricia I. Dickson, M.D.University of California, Los Angeles; FDA Office of Orphan Products Development and other collaboratorsTerminatedMucopolysaccharidosis I | Lysosomal Storage Diseases | Spinal Cord CompressionUnited States, Finland
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Novartis PharmaceuticalsWithdrawnKidney TransplantUnited States
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NovartisCompleted
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Novartis PharmaceuticalsCompletedLupus NephritisFrance, Spain, Colombia, Hungary, Italy, Germany, Greece, Taiwan, United Kingdom
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Sanguine BiosciencesDenali Therapeutics Inc.RecruitingMucopolysaccharidosis III-AUnited States
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agnes chenUniversity of California, Los Angeles; National Institute of Neurological Disorders... and other collaboratorsTerminatedMucopolysaccharidosis I | Cognitive DeclineUnited States
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Hom, Milton M., OD, FAAOAbbott Medical OpticsUnknownContact Lens Solution ToxicityUnited States
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Otsuka Pharmaceutical Co., Ltd.Completed
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Alcon ResearchCompletedMyopia | Hyperopia | Contact Lens Comfort
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ShireTerminatedSanfilippo Syndrome | Mucopolysaccharidosis (MPS)United States, United Kingdom, Spain, Germany, France, Italy, Netherlands
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Walter Reed National Military Medical CenterCompletedCoronary Artery Disease | Chest Pain
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Otsuka Pharmaceutical Co., Ltd.CompletedHealthyKorea, Republic of
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Novartis PharmaceuticalsCompletedHeart TransplantationUnited States, Australia, Argentina, Canada
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis VIUnited States
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Northside Hospital, Inc.Blood and Marrow Transplant Group of GeorgiaCompletedMultiple Myeloma | Hodgkin's Lymphoma | Non-Hodgkin's Lymphoma | Myelofibrosis | Chronic Lymphocytic Leukemia | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | CMMLUnited States
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Sangamo TherapeuticsTerminatedMucopolysaccharidosis II | MPS IIUnited States
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GC Biopharma CorpRecruitingMucopolysaccharidosis II | Hunter SyndromeKorea, Republic of
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NovartisCompleted
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Alcon ResearchCompleted
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IV A | Mucopolysaccharidosis IVAFrance, United Kingdom, Taiwan, United States, Argentina, Netherlands, Canada, Brazil, Germany, Italy
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IUnited States, Brazil, Japan
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Allievex CorporationActive, not recruitingMucopolysaccharidosis Type IIIB | MPS III BGermany, United States, Turkey, United Kingdom, Colombia, Spain, Taiwan
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Henry M. Jackson Foundation for the Advancement...National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Walter... and other collaboratorsUnknownObesity | Overweight | Binge EatingUnited States