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Search clinical trials for: Philadelphia chromosome
Total 18068 results
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ACADIA Pharmaceuticals Inc.Completed
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Memorial Sloan Kettering Cancer CenterNovartis Pharmaceuticals; Incyte CorporationActive, not recruiting
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedBlast Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive | Recurrent Chronic Myelogenous Leukemia, BCR-ABL1 Positive | Refractory Chronic Myelogenous Leukemia, BCR-ABL1 Positive | Blasts More Than 5 Percent of Bone Marrow Nucleated Cells | B Acute Lymphoblastic Leukemia With t(9;22)(q34... and other conditionsUnited States
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsActive, not recruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Switzerland, Germany
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Rennes University HospitalNovartis; Ministry of Health, FranceCompletedAcute Lymphoblastic Leukemia | Philadelphia ChromosomeFrance
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Nemours Children's ClinicGenentech, Inc.CompletedHypogonadism | Turner Syndrome | Premature Ovarian FailureUnited States, Chile
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Bristol-Myers SquibbCompleted
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SWOG Cancer Research NetworkNational Cancer Institute (NCI)CompletedRecurrent Adult Burkitt Lymphoma | Recurrent Adult Acute Lymphoblastic Leukemia | B-cell Adult Acute Lymphoblastic Leukemia | Acute Leukemias of Ambiguous Lineage | Philadelphia Chromosome Positive Adult Precursor Acute Lymphoblastic LeukemiaUnited States
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Amicus TherapeuticsCompletedFabry DiseaseJapan, Taiwan, Turkey, United States, Brazil
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Novartis PharmaceuticalsNo longer availableChronic Myelogenous Leukemia (CML)
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Children's Hospital of PhiladelphiaUniversity of Pennsylvania; National Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health (NIH) and other collaboratorsCompletedObstructive Sleep Apnea | Down SyndromeUnited States
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Santhera PharmaceuticalsNo longer availableDuchenne Muscular DystrophyUnited States
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PfizerCompletedMyeloid LeukemiaUnited Kingdom
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Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
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UNC Lineberger Comprehensive Cancer CenterCompletedChronic Myeloid Leukemia | Chronic Myeloid Leukemia, Chronic Phase | CML, Chronic Phase | CML - Philadelphia Chromosome | CML (Chronic Myelogenous LeukemiaUnited States
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OHSU Knight Cancer InstituteTerminated
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Korea Otsuka Pharmaceutical Co., Ltd.Active, not recruitingChronic Myeloid Leukemia | Philadelphia Chromosome-positive Acute Lymphoblastic LeukemiaKorea, Republic of
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University of PennsylvaniaSequenom, Inc/Laboratory Corporation of America HoldingsCompleted
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Ultragenyx Pharmaceutical IncTerminatedCreatine Deficiency, X-linkedUnited States, Canada
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)TerminatedRecurrent B Acute Lymphoblastic Leukemia | Refractory B Acute Lymphoblastic Leukemia | Philadelphia Chromosome NegativeUnited States
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REGENXBIO Inc.Withdrawn
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States
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Jazz PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Spain, Italy, United Kingdom
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Idorsia Pharmaceuticals Ltd.CompletedFabry DiseaseUnited States, Spain, Belgium, Australia, Austria, Canada, Germany, Ireland, Italy, Netherlands, Norway, Poland, Switzerland, United Kingdom
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Novartis PharmaceuticalsNo longer availableAcute Lymphoblastic Leukemia (ALL)
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Jazz PharmaceuticalsGW PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Canada, Italy, Spain, United Kingdom, Australia
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Institute of Hematology & Blood Diseases HospitalCompletedAcute,Leukemia, LymphoidChina
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Astellas Gene TherapiesCompletedMales With X-linked Myotubular Myopathy (XLMTM)United States, United Kingdom
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PETHEMA FoundationTerminatedPhiladelphia Chromosome-negative or BCR-ABL-negative, CD19-positive ALLSpain
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Levo Therapeutics, Inc.CompletedPrader-Willi SyndromeUnited States, Canada, Australia
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CSL BehringCompletedHemophilia BUnited States, Australia, Japan, France, Philippines, Spain, Czechia, Israel, Canada, Germany, Austria, Bulgaria, Italy, Malaysia, South Africa
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Bristol-Myers SquibbCompletedChronic Myeloid Leukemia | Philadelphia Chromosome | Chronic Myeloid Leukemia in Chronic PhaseChina
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States, Canada, Australia, United Kingdom, Germany, Ireland, Israel, Sweden
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Ariad PharmaceuticalsCompletedChronic Myeloid Leukemia (CML) | Philadelphia Chromosome Positive Acute Lymphoblastic Leukemia (Ph+ ALL)Japan
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ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
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National Cancer Institute (NCI)CompletedB-cell Adult Acute Lymphoblastic Leukemia | Acute Undifferentiated Leukemia | Philadelphia Chromosome Positive Adult Precursor Acute Lymphoblastic Leukemia | B-cell Childhood Acute Lymphoblastic Leukemia | L1 Childhood Acute Lymphoblastic Leukemia | L2 Childhood Acute Lymphoblastic Leukemia | T-cell... and other conditionsUnited States
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Incyte Biosciences BeneluxCompletedChronic Myeloid Leukemia | CML | Philadelphia Chromosome-positive Acute Lymphoblastic Leukemia | Ph+ ALLBelgium
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University of Maryland, BaltimoreChildren's Hospital of PhiladelphiaWithdrawnOsteoporosis Pseudoglioma SyndromeUnited States
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, Canada, China, France, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, Italy, Japan, South Africa, Spain, Taiwan
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Aevi Genomic Medicine, LLC, a Cerecor companyCompleted22q11.2 Deletion SyndromeUnited States
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Brigham and Women's HospitalChildren's Hospital of Philadelphia; University of Michigan; University of Texas... and other collaboratorsCompletedSleep Disordered Breathing | Down SyndromeUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedSecondary Acute Myeloid Leukemia | Childhood Acute Erythroleukemia (M6) | Childhood Acute Megakaryocytic Leukemia (M7) | Childhood Acute Monoblastic Leukemia (M5a) | Childhood Acute Monocytic Leukemia (M5b) | Childhood Acute Myeloblastic Leukemia With Maturation (M2) | Childhood Acute Myeloblastic... and other conditionsUnited States, Canada, Australia, Puerto Rico
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Goethe UniversityCompletedPhiladelphia Positive Acute Lymphoblastic LeukemiaGermany
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Gruppo Italiano Malattie EMatologiche dell'AdultoActive, not recruitingAcute Lymphoid Leukemia | Philadelphia Chromosome-Negative B-Cell PrecursorItaly
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PfizerDevelopmental Therapeutics ConsortiumTerminatedPreviously Treated PH + CMLSpain, United States, Austria, Sweden, Germany, France, Italy, Norway
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Santhera PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Austria, France, Germany, Italy, Spain, Switzerland
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Santhera PharmaceuticalsTerminatedDuchenne Muscular Dystrophy (DMD)United States, Spain, Netherlands, Sweden, Germany, France, Belgium, United Kingdom, Italy, Ireland, Switzerland, Austria, Bulgaria, Hungary, Israel
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University of Southern CaliforniaNational Cancer Institute (NCI); Vasgene Therapeutics, Inc; Whittier FoundationTerminatedAcute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome | Recurrent Adult Acute Myeloid Leukemia | Secondary Acute Myeloid Leukemia | Refractory Acute Myeloid Leukemia | Philadelphia Chromosome Positive | Recurrent Acute Lymphoblastic Leukemia | Refractory Acute Lymphoblastic Leukemia and other conditionsUnited States
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Novo Nordisk A/SCompletedHaemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BFrance, United States, India, Mexico, United Kingdom, Netherlands, Sweden, Korea, Republic of, Spain, Switzerland, Serbia, Turkey, Bulgaria, Italy, Japan, Poland, South Africa, Croatia, Algeria, Australia, Bosnia and Herzegovina, ... and more