Search clinical trials for: VX15-984-001

Total 11059 results

Aevi Genomic Medicine, LLC, a Cerecor company

Completed

PART A: Efficacy and Safety of AEVI-001 in Children and Adolescents With ADHD and With mGluR Mutations

Attention Deficit Hyperactivity Disorder

United States
MediciNova

Recruiting

MN-001 in Non-alcoholic Fatty Liver Disease, Type 2 Diabetes Mellitus, and Hypertriglyceridemia

Diabetes Mellitus, Type 2 | Hypertriglyceridemia | Non-Alcoholic Fatty Liver Disease

United States
Ascentawits Pharmaceuticals, Ltd

Recruiting

A Phase I/II Study of AST-001 in Subjects With Advanced Solid Tumors

Pancreatic Cancer | Solid Tumor

China
Innovo Therapeutics, Inc.

Recruiting

Ointment to Prevent Scar After Thyroidectomy

Scar

Korea, Republic of
Stoke Therapeutics, Inc

Enrolling by invitation

An Open-Label Extension Study of STK-001 for Patients With Dravet Syndrome

Dravet Syndrome

United States
MedRhythms, Inc.

Active, not recruiting

Facilitators and Barriers to the Clinical Implementation of MR-001 (RhaPSody)

Chronic Stroke

United States
Ossium Health, Inc.

Withdrawn

Mesenchymal Stem Cells (MSCs) for Steroid Refractory Acute GVHD (SR-aGVHD)

GVHD,Acute
Adicet Bio, Inc

Enrolling by invitation

Long-term Follow-up Study of Allogeneic Gamma Delta (γδ) CAR T Cells

Lymphoma, Follicular | Lymphoma, Non-Hodgkin | Lymphoma, Mantle-Cell | Marginal Zone Lymphoma | Diffuse Large B Cell Lymphoma | Primary Mediastinal B-cell Lymphoma

United States
Stargazer Pharmaceuticals, Inc.

Completed

Study of STG-001 in Subjects With Stargardt Disease

Stargardt Disease-1

United States
Cerenis Therapeutics, SA

Completed

Exploratory Study of Plaque Regression (EXPRESS)

Heterozygous Familial Hypercholesterolemia

Canada
Danube Pharmaceuticals, Inc.

Completed

Safety, Efficacy, and Pharmacokinetic Profile of DNB-001 in Subjects With Elevated Intraocular Pressure (DNB-001)

Ocular Hypertension | Glaucoma | Elevated IOP

United Kingdom
Cephalon

Completed

A Study to Assess the Abuse Potential of Hydrocodone Extended-Release Tablet in Recreational Opioid Users

Drug Abuse

United States, Canada
NantBioScience, Inc.

Active, not recruiting

QUILT-2.025 NANT Neoepitope Yeast Vaccine (YE-NEO-001): Adjuvant Immunotherapy Using a Personalized Neoepitope Yeast-Based Vaccine To Induce T-Cell Responses In Subjects W/ Previously Treated Cancers.

Melanoma | Breast Cancer | Colorectal Cancer | Pancreatic Cancer | Non Small Cell Lung Cancer | Head and Neck Squamous Cell Carcinoma | Liver Cancer

United States
PYC Therapeutics

Not yet recruiting

SAD of IVT PYC-001 in OPA1 Mutation-Associated Autosomal Dominant Optic Atrophy (Sundew)

Autosomal Dominant Optic Atrophy | Kjer Optic Atrophy | OPA1 Gene Mutation | Hereditary Optic Atrophies
ImmunoGenesis

Recruiting

Study to Evaluate IMGS-001 Treatment in Patients With Relapsed or Refractory Advanced Solid Tumors

Solid Tumor

United States
Fog Pharmaceuticals, Inc.

Recruiting

FOG-001 in Locally Advanced or Metastatic Solid Tumors

Cancer | Gastric Cancer | Colorectal Cancer | Solid Tumor | Metastatic Cancer | Adenomatous Polyposis Coli | Non-small Cell Lung Cancer | Non-small Cell Lung Cancer Metastatic | Non-small Cell Carcinoma | Locally Advanced Solid Tumor | Non-small Cell Lung Cancer Stage IIIB | Gastroesophageal-junction Cancer | Non-Small... and other conditions

United States
PYC Therapeutics

Recruiting

SAD of IVT VP-001 in PRPF31 Mutation-Associated Retinal Dystrophy Subjects (Platypus)

Retinal Dystrophy | PRPF31 Mutationassociated Retinal Dystrophy | RP11

United States
Medibio Limited

Recruiting

Sleep Signal Analysis for Current Major Depressive Episode (SAMDE) (SAMDE)

Depressive Disorder | Depression | Depressive Disorder, Major | Depressive Episode | Depression Mild

United States
PharmaMatrix Holdings Ltd
University of Alberta

Recruiting

A Study of CCI-001 in Patients With Recurrent and/or Metastatic Solid Tumours

Cancer: Recurrent and/or Metastatic Solid Tumours

Canada
Videregen Limited
Royal Free Hospital NHS Foundation Trust; Papworth Hospital NHS Foundation... and other collaborators

Not yet recruiting

ENgineered Tissue Repair of BronchopleUral fiSTula (ENTRUST)

Bronchopleural Fistula
Alumis Inc

Active, not recruiting

Open-Label Extension Study to Evaluate the Long Term Safety and Efficacy of ESK-001 in Plaque Psoriasis

Plaque Psoriasis

United States, Canada
Alumis Inc

Active, not recruiting

POC Study to Evaluate the Efficacy and Safety of ESK-001 in Patients With Active Intermediate, Posterior, or Pan NIU (OPTYK-1)

Uveitis, Intermediate | Noninfectious Panuveitis | Uveitis Posterior Non-Infectious

United States
LogicBio Therapeutics, Inc
Alexion Pharmaceuticals, Inc.

Active, not recruiting

Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy

Methylmalonic Acidemia

United States
Rohto Pharmaceutical Co., Ltd.

Active, not recruiting

A Study to Investigate the Safety and Efficacy of UC-MSCs in Pediatric Patients With Cerebral Palsy

Cerebral Palsy | Periventricular Leukomalacia

Japan
Celularity Incorporated
Lung Biotechnology PBC; California Institute for Regenerative Medicine (CIRM); ID...

Active, not recruiting

Natural Killer Cell (CYNK-001) Infusions in Adults With COVID-19 (CYNKCOVID)

Coronaviridae Infections | Nidovirales Infections | RNA Virus Infections | Respiratory Tract Infections | Coronavirus Infection | Pneumonia, Viral | Pneumonia | Lung Diseases | ARDS | Coronavirus | Severe Acute Respiratory Syndrome Coronavirus 2 | Respiratory Tract Disease | Virus Disease | Physiological Effects of... and other conditions

United States
Shanton Pharma Co., Ltd.

Completed

Placebo Controlled, Dose Escalation Study to Evaluate Safety, Pharmacokinetics & Efficacy of SAP-001 in Gout Patients

Gout, Hyperuricemia

United States
Teijin America, Inc.

Completed

A Study to Evaluate Safety and Exploratory Efficacy of KTP-001 in Subjects With Lumbar Disc Herniation

Lumbar Disc Herniation

United States
ADMA Biologics, Inc.

Completed

RI-001 in Immunosuppressed Respiratory Syncytial Virus (RSV) Infected Patients at Risk of Lower Tract RSV Illness

Lower Respiratory Tract Infection | Upper Respiratory Tract Infection

United States, Canada
Stoke Therapeutics, Inc

Completed

An Open-Label Study to Investigate the Safety of Single and Multiple Ascending Doses in Children and Adolescents With Dravet Syndrome

Dravet Syndrome

United States
The Medicines Company

Completed

Trial to Evaluate the Effect of Inclisiran Treatment on Low Density Lipoprotein Cholesterol (LDL-C) in Subjects With Heterozygous Familial Hypercholesterolemia (HeFH) (ORION-9)

Elevated Cholesterol | Heterozygous Familial Hypercholesterolemia

United States, Canada, Czechia, Denmark, Netherlands, South Africa, Spain, Sweden
Celgene

Completed

Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of CC-99677 in Healthy Adult Japanese Participants.

Healthy Volunteers

United States
Sanofi

Completed

Dermacyd in Odor Reducing.

Hygiene

Brazil
NanoBio Corporation

Unknown

NB-001 Treatment of Recurrent Herpes Labialis

Herpes Labialis

United States
n-Lorem Foundation
Mayo Clinic

Active, not recruiting

Personalized Antisense Oligonucleotide Therapy for A Single Participant With CHCHD10 ALS

Amyotrophic Lateral Sclerosis

United States
Balance Therapeutics

Completed

A Study to Investigate the Mass Balance of BTD-001 (HV103)

Molecular Mechanisms of Pharmacological Action

United Kingdom
Spyre Therapeutics, Inc.
Altasciences Company Inc.

Recruiting

A Study of SPY001-001 in Healthy Volunteers

Healthy

United States, Canada
Regend Therapeutics
Peking Union Medical College Hospital; RenJi Hospital; Ruijin Hospital

Recruiting

A Clinical Study to Evaluate the Efficacy and Safety of REGEND001 Cell Therapy on Idiopathic Pulmonary Fibrosis (IPF)

Idiopathic Pulmonary Fibrosis

China
Alumis Inc

Recruiting

Phase 2 Placebo-Controlled Study to Assess the Safety and Efficacy of ESK-001 in Active Systemic Lupus Erythematosus (LUMUS)

SLE

United States, Argentina, Bulgaria, Colombia, Georgia, India, Mexico, Peru, Philippines, Poland, Spain, United Kingdom, Croatia, Denmark, Germany, Hungary, Korea, Republic of, Romania, Taiwan, Chile
OXOLIFE

Completed

Phase II Clinical Trial to Evaluate the Ongoing Pregnancy Rate With OXO-001 in IVF/ICSI With Donor Oocytes. (OXOART2)

Infertility | Infertility, Female

Czechia, Spain, Poland
Red Queen Therapeutics, Inc.
PPD

Completed

Clinical Trial to Evaluate the Safety of RQ-01 in SARS-CoV-2 Positive Subjects

COVID-19 | Infectious Disease | SARS CoV 2 Infection | Symptomatic COVID-19 Infection Laboratory-Confirmed

United States
Better Therapeutics
University of Colorado, Denver; CPC Clinical Research; Ascension Health; Department... and other collaborators

Active, not recruiting

Digital Therapeutic Based Investigation to Improve Glycemic Control in Patients With Type 2 Diabetes and Residual Hyperglycemia on Stable Medical Therapy (BRIGHT)

Diabetes Mellitus, Type 2

United States
Regeneron Pharmaceuticals

Available

Compassionate Use of Vidutolimod
Staidson (Beijing) Biopharmaceuticals Co., Ltd

Completed

Efficacy and Safety Study of BDB-001 Injection in Patients With Moderate to Severe Hidradenitis Suppurativa (HS)

Hidradenitis Suppurativa

China
Equilibre Biopharmaceuticals B.V.

Active, not recruiting

Safety, Tolerability, and Exploratory Efficacy of Adjunctive EQU-001 for Seizures in Adults With Epilepsy

Epilepsy

United States, Israel
Sarkana Pharma Inc

Terminated

A Multiple Dose Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of SRK-001 in Healthy Participants

Healthy Participants

Netherlands
Yaqrit Ltd
Assistance Publique - Hôpitaux de Paris; IRCCS Azienda Ospedaliero-Universitaria... and other collaborators

Withdrawn

Safety and Tolerability of Yaq-001 in Patients With Non-Alcoholic Steatohepatitis

Non-Alcoholic Steatohepatitis

France, Italy, Portugal, Spain, Switzerland, United Kingdom
Vasomune Therapeutics, Inc.

Completed

A First-in-Human Study of AV-001 in Healthy Subjects

Covid19 | ARDS | Covid19-associated ARDS

United States
Balance Therapeutics

Completed

A Study of Safety and Efficacy of BTD-001 in Treatment of Patients With Idiopathic Hypersomnia (IH) or Narcolepsy Type 2

Idiopathic Hypersomnia | Narcolepsy Without Cataplexy

United States
Alliance for Clinical Trials in Oncology
National Cancer Institute (NCI)

Terminated

Seneca Valley Virus-001 After Chemotherapy in Treating Patients With Extensive-Stage Small Cell Lung Cancer

Lung Cancer

United States
Xenon Pharmaceuticals Inc.

Completed

Safety and Efficacy Study of XPF-001 to Treat Pain Following Wisdom Tooth Extraction

Dental Pain

United States

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