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Search clinical trials for: autosomal dominant osteopetrosis type I
Total 494977 results
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Kadmon, a Sanofi CompanyCompletedPolycystic Kidney, Autosomal DominantUnited States
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Mario Negri Institute for Pharmacological ResearchOtsuka Pharmaceutical Italy S.r.l.CompletedAutosomal Dominant Polycystic Kidney DiseaseItaly
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AceLink Therapeutics, Inc.Novotech (Australia) Pty LimitedCompletedAutosomal Dominant Polycystic KidneyAustralia
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Regulus Therapeutics Inc.Completed
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SanofiTerminatedCongenital Cystic Kidney DiseaseGermany, Spain, United States, Australia, Belgium, Japan, Korea, Republic of, Netherlands
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University of CologneCompleted
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Southwest Oncology GroupNational Cancer Institute (NCI)CompletedLymphoma | Nonneoplastic ConditionUnited States
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Kyongtae Ty Bae, M.D., Ph.D.University of Maryland, Baltimore; United States Department of Defense; University... and other collaboratorsCompletedPolycystic Kidney, Autosomal DominantUnited States
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Azienda Ospedaliero-Universitaria Consorziale Policlinico...Institute of Biomembranes, Bioenergetics and Molecular Biotechnologies; Istituti... and other collaboratorsCompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD) | IgA Nephropathy (IgAN) | Diabetic Kidney Disease (DKD) | Advanced-Chronic Kidney Disease (CKD)Italy
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Rocket Pharmaceuticals Inc.California Institute for Regenerative Medicine (CIRM)TerminatedInfantile Malignant OsteopetrosisUnited States
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Bellicum PharmaceuticalsActive, not recruitingStudy of Gene Modified Donor T-cells Following TCR Alpha Beta Positive Depleted Stem Cell TransplantLymphoma, Non-Hodgkin | Myelodysplastic Syndromes | Acute Lymphoblastic Leukemia | Anemia, Aplastic | Primary Immune Deficiency Disorder | Cytopenia | Osteopetrosis | Leukemia, Acute Myeloid (AML), Child | Hemoglobinopathy in ChildrenUnited States
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Korea Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)Korea, Republic of
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Kadmon Corporation, LLCTerminatedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States
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ProQR TherapeuticsActive, not recruitingEye Diseases | Retinitis | Eye Diseases, Hereditary | Retinal Dystrophies | Vision Disorders | Retinal Disease | Autosomal Dominant Retinitis Pigmentosa | Vision TunnelUnited States
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Genzyme, a Sanofi CompanyCompletedHealthy Volunteers | Polycystic Kidney, Autosomal DominantUnited States
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Wake Forest University Health SciencesTerminatedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Chronic Myeloid Leukemia | Myelodysplastic Syndrome | Immune Deficiency | Lymphomas | Bone Marrow Failure | Osteopetrosis | HemoglobinopathyUnited States
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University of Colorado, DenverCompletedPolycystic Kidney, Autosomal DominantUnited States
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedPolycystic Kidney, Autosomal DominantUnited States
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Regulus Therapeutics Inc.CompletedPolycystic Kidney Disease, Autosomal DominantUnited States
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Alliance for Clinical Trials in OncologyNational Cancer Institute (NCI)Completed
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States, Australia, Belgium, Germany, Italy, Poland, Romania, United Kingdom, Argentina, Canada, France, Netherlands, Russian Federation
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Radboud University Medical CenterAcademisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA)CompletedPolycystic Kidney, Autosomal Dominant | Polycystic Liver DiseaseNetherlands, Spain
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
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Institut National de la Santé Et de la Recherche...Completed
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Institut National de la Santé Et de la Recherche...Assistance Publique - Hôpitaux de ParisCompletedSpinocerebellar Ataxias | Spastic ParaplegiasFrance
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ShireNational Institutes of Health (NIH)CompletedAutosomal Dominant Hypocalcemia (ADH)United States
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Assistance Publique - Hôpitaux de ParisMinistry of Health, FranceCompletedAutosomal Dominant Hypocalcemia OR Primary Hypoparathyroidism Related to Other Cause But Complicated by Hypercalciuria Under TreatmentFrance
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Christopher DvorakNo longer availableAcute Myeloid Leukemia | Leukocyte Disorders | Acute Lymphoblastic Leukemia | Chronic Myeloid Leukemia | Myelodysplastic Syndrome | Cytopenias | Immune Deficiency | Lymphomas | Bone Marrow Failure | Osteopetrosis | Hemoglobinopathy | Anemia Due to Intrinsic Red Cell AbnormalityUnited States
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Cadent TherapeuticsWithdrawnSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxias | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6 | Spinocerebellar Ataxia Type 10 | Spinocerebellar Ataxia Type 7 | Spinocerebellar Ataxia Type 8 | Spinocerebellar Ataxia Type 17 | ARCA1 - Autosomal Recessive...United States
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Inozyme PharmaEngage Health Inc.; GACI GlobalCompletedGeneralized Arterial Calcification in Infancy | Autosomal Recessive Hypophosphatemic Rickets Type 2United States
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University Hospital, BrestCompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)France
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ShireTerminatedRetinitis PigmentosaUnited States
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Indiana UniversityCompletedPolycystic Kidney DiseaseUnited States
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Esther MeijerUnknownPolycystic Kidney, Autosomal Dominant | Autosomal Dominant Polycystic Kidney | ADPKDNetherlands
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Wake Forest University Health SciencesCompleted
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory Syndrome | Muckle-Wells Syndrome | Neonatal Onset Multisystem Inflammatory Disease | Cryopyrin-associated Periodic SyndromesJapan
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Stanford UniversityNational Cancer Institute (NCI)CompletedLymphomaUnited States
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National Institute of Allergy and Infectious Diseases...TerminatedAutosomal-dominant Hyper-IgE SyndromeUnited States
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Kyorin UniversityUnknown
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Mayo ClinicCompletedAutosomal Dominant Polycystic Kidney Disease | Polycystic Liver Disease | Autosomal Dominant Polycystic Liver Disease | Somatostatin AnalogsUnited States
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Regional Hospital HolstebroCompletedChronic Kidney Diseases | Polycystic Kidney, Autosomal DominantDenmark
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NCIC Clinical Trials GroupEastern Cooperative Oncology GroupCompletedHodgkin LymphomaCanada, United Kingdom, Italy
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University of North Carolina, Chapel HillNational Institute of General Medical Sciences (NIGMS)CompletedRenal Disease | Autosomal Dominant Polycystic Kidney Disease | ADPKDUnited States
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National Human Genome Research Institute (NHGRI)CompletedPolydactyly | Malformations | Multiple AbnormaliesUnited States, Turkey
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Otsuka Pharmaceutical Development & Commercialization...CompletedPolycystic Kidney, Autosomal DominantBelgium, Germany, Italy, Spain, Sweden, United States, Canada, Australia, Netherlands, Czechia, Poland, Denmark, Israel, Hungary, Russian Federation, South Africa, United Kingdom, Romania, Argentina, Norway
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Assistance Publique - Hôpitaux de ParisIPSEN pharmaceutical company, Boulogne-Billancourt, FranceCompletedAutosomal Dominant Polycystic Kidney Disease (ADPKDFrance
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Indiana UniversityCompletedAutosomal Dominant Hypophosphatemic RicketsUnited States
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University Hospital, RouenCompletedAutosomal Dominant Cases of Alzheimer 's DiseaseFrance
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
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University of RochesterCompletedNon-Small Cell Lung CancerUnited States