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Search clinical trials for: Leber Hereditary Optic Neuropathy (LHON)
Total 22197 results
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Hospital JP GarrahanHospital San Juan de Dios, SantiagoActive, not recruitingUnilateral RetinoblastomaArgentina
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IRCCS Eugenio MedeaCompletedCerebral Palsy | Acquired Brain Injury | Hereditary Spastic ParaplegiaItaly
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Washington University School of MedicineNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National...CompletedDiabetes Mellitus | Ataxia | Wolfram Syndrome | Optic Nerve AtrophyUnited States
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University of PennsylvaniaAstraZeneca; Ionis Pharmaceuticals, Inc.Active, not recruitingHereditary Amyloidosis, Transthyretin-RelatedUnited States
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State University of New York at BuffaloHadley Jo FoundationCompletedMitochondrial Diseases | Optic Atrophy | Neurodegenerative Disease, HereditaryUnited States
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State University of New York at BuffaloThe Callum McKeefery and Nikki Albano McKeefery Pediatric Division of Genetics...CompletedMitochondrial Diseases | Optic Atrophy | Neurodegenerative Disease, HereditaryUnited States
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Iran University of Medical SciencesTehran University of Medical Sciences; Mashhad University of Medical SciencesCompletedTraumatic Optic NeuropathyIran, Islamic Republic of
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Janssen Research & Development, LLCCompletedHepatitis BFrance, United States, Belgium, United Kingdom, Poland, New Zealand, Germany, Italy, Canada
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Atsena Therapeutics Inc.Active, not recruitingLeber Congenital Amaurosis | LCA | LCA1United States
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Pharnext S.C.A.Premier Research Group plc; Eurofins Optimed; Synteract HCR (Syneos Health); Gr... and other collaboratorsActive, not recruitingCharcot-Marie-Tooth Disease, Type IAUnited States, Belgium, Canada, France, Netherlands, Spain, United Kingdom
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University Hospital, Clermont-FerrandActive, not recruitingCharcot-Marie-Tooth Type 1A NeuropathyFrance
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Cellaion SAEnrolling by invitationUrea Cycle Disorder | Crigler-Najjar Syndrome | Acute on Chronic Liver FailureBelgium, Spain, France, Bulgaria, Poland
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The Christ HospitalGilead SciencesCompletedHepatitis C | Pregnancy Complications | Vertical Disease TransmissionUnited States
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Spaulding Rehabilitation HospitalMassachusetts General HospitalWithdrawnHereditary Spastic Paraplegia
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SanofiCompletedHepatic Function AbnormalUnited States, Germany
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Ankara City Hospital BilkentCompletedLow Back Pain | Radiofrequency Ablation | Nerve Entrapment SyndromeTurkey
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Recurrent Childhood Pilocytic Astrocytoma | Recurrent Childhood Visual Pathway GliomaUnited States, Canada, Australia, New Zealand
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NYU Langone HealthNational Eye Institute (NEI)Active, not recruitingFuch's Dystrophy | Corneal Disorders | Prior SurgeryUnited States
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Byondis B.V.CompletedMetastatic Breast CancerFrance, Belgium, Spain
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Johns Hopkins UniversityNovartisEnrolling by invitationMultiple Sclerosis | Retinal Degeneration | Visual Acuity | Tomography, Optical CoherenceUnited States
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Clene NanomedicineGeorge ClinicalCompletedRelapsing Multiple SclerosisAustralia
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Cutaneous Neurofibroma | Optic Nerve GliomaUnited States
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Rhythm Pharmaceuticals, Inc.CompletedBardet Biedl Syndrome (BBS) | Alström Syndrome (AS)United States, United Kingdom, France, Canada, Puerto Rico, Spain
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University of Campania "Luigi Vanvitelli"Retina Italia OnlusCompletedLeber Congenital Amaurosis 2 | Retinitis Pigmentosa 20Italy
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University College London HospitalsCompletedDistal Hereditary Motor Neuropathy, Type II | Distal Hereditary Motor Neuropathy, Type V | Distal Hereditary Motor Neuronopathy Type I | Distal Hereditary Motor Neuronopathy Type VIUnited Kingdom
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St. Justine's HospitalCHU de Quebec-Universite Laval; Montreal Children's Hospital of the MUHCActive, not recruitingLow-grade Glioma | Plexiform Neurofibroma | Central Nervous System GliomaCanada
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Taysha Gene Therapies, Inc.National Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGene Transfer | Giant Axonal NeuropathyUnited States
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Centre Hospitalier Universitaire de NiceDENSMORE pharmaceuticalsCompleted
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Oregon Health and Science UniversityActive, not recruitingAnterior Cutaneous Nerve Entrapment SyndromeUnited States
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Assistance Publique - Hôpitaux de ParisCompletedHereditary Spastic ParaplegiaFrance
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University Medical Center GroningenCompletedAdenomatous Polyposis ColiNetherlands
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National Institutes of Health Clinical Center (CC)Enrolling by invitationHepatocellular CarcinomaUnited States
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Spark TherapeuticsActive, not recruitingLeber Congenital AmaurosisUnited States
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Applied Therapeutics, Inc.Active, not recruitingHereditary Neuropathy Caused by SORD DeficiencyUnited States, United Kingdom, Czechia, Italy
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Omar SaidCompletedNon-arteritic Ischemic Optic NeuropathyEgypt
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AeRang KimTerminatedOsteosarcoma | Ewing Sarcoma | Neuroblastoma | Solid Tumors | Pediatric Cancer | Rhabdomyosarcoma | Wilms Tumor | Soft Tissue Sarcomas | Germ Cell Tumors | Hepatic TumorUnited States
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Sunnybrook Health Sciences CentreGlaucoma Research Society of CanadaCompleted
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University of BirminghamActive, not recruitingWolfram SyndromeFrance, United Kingdom, Poland, Spain
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University of NebraskaWithdrawnChronic Hepatitis CUnited States
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AeRang KimActive, not recruitingOsteosarcoma | Ewing Sarcoma | Neuroblastoma | Rhabdomyosarcoma | Wilms Tumor | Desmoid Tumor | Germ Cell Tumor | Relapsed Pediatric Solid Tumors | Refractory Pediatric Solid Tumors | Hepatic TumorUnited States
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MeiraGTx UK II LtdCompletedNatural History Study of Patients With Leber Congenital Amaurosis Associated With Mutations in RPE65Leber Congenital AmaurosisUnited Kingdom, United States
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Amira M elSonbatyCompletedOptic NeuropathyEgypt
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University Eye Hospital, FreiburgCompletedFuchs' Endothelial DystrophyGermany
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Eastern Cooperative Oncology GroupNational Cancer Institute (NCI)CompletedMetastatic Cancer | Liver CancerUnited States
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University of PennsylvaniaNational Eye Institute (NEI)Active, not recruitingRetinal Diseases | Amaurosis of LeberUnited States
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Batman Training and Research HospitalCompletedCorneal Dystrophy | Macular Dystrophy | Hyperemesis Gravidarum - SevereTurkey
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October 6 UniversityCompletedCubital Tunnel Syndrome | Ulnar Nerve Entrapment at Elbow | Ulnar Nerve Compression | Ulnar Nerve Entrapment SyndromeEgypt
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityCompletedOptic Radiation Neuropathy Following Radiotherapy ProcedureChina
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Nemours Children's ClinicTerminated
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Clene NanomedicineClene Australia Pty LtdTerminatedRelapsing Remitting Multiple Sclerosis | Optic Neuropathy | Optic; Neuritis, With DemyelinationUnited States, Canada, Australia