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Search clinical trials for: X-linked myotubular myopathy
Total 445 results
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaKorea, Republic of, Canada, United States, Australia, Japan, United Kingdom, Sweden
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Kyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia (XLH)China
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Kyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia (XLH)China
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Kyowa Kirin Pharmaceutical Development LtdActive, not recruitingX-Linked HypophosphatemiaSpain, Italy, United Kingdom, France, Belgium, Denmark, Germany, Hungary, Portugal, Norway, Switzerland, Israel, Netherlands, Czechia, Bulgaria, Sweden, Slovenia, Ireland, Latvia, Slovakia
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
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Damascus UniversityCompleted
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Rigshospitalet, DenmarkCompletedMitochondrial Myopathies | Healthy ControlsDenmark
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Ondokuz Mayıs UniversityCompletedSarcopenia | Critical Illness Myopathy | SARS-CoV-2 Acute Respiratory Disease | ICU Acquired WeaknessTurkey
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Scripps HealthWithdrawn
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Ultragenyx Pharmaceutical IncTerminatedCreatine Deficiency, X-linkedUnited States, Canada
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Holland Bloorview Kids Rehabilitation HospitalChildren's Hospital of Eastern OntarioCompletedMuscular Dystrophies | Congenital MyopathyCanada
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University of WashingtonGrifols Biologicals, LLCWithdrawnImmune-Mediated Necrotizing MyopathyUnited States
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Barts & The London NHS TrustQueen Mary University of LondonCompletedSurgery | Critical Illness Myopathy | Aortic Diseases | Intensive Care Unit Syndrome | Intensive Care (ICU) Myopathy | Intensive Care NeuropathyUnited Kingdom
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University Hospital, GenevaLigue Pulmonaire GenevoiseActive, not recruitingChronic Thromboembolic Pulmonary Hypertension | Myopathy | Restrictive Lung Disease | Covid19 PneumoniaSwitzerland
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University of Southern CaliforniaCompletedSleep Disorder | Insomnia | Sleep Disturbance | Critical Illness MyopathyUnited States
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Kyowa Kirin Co., Ltd.CompletedX-linked Hypophosphatemic Rickets/OsteomalaciaJapan
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Kyowa Kirin Co., Ltd.CompletedA Study of KRN23 in Adult and Pediatric Patients With X-linked Hypophosphatemic Rickets/OsteomalaciaXLHJapan, Korea, Republic of
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Khondrion BVJulius ClinicalCompletedMitochondrial Diseases | Mitochondrial Myopathies | MELAS Syndrome | Mitochondrial Encephalomyopathies | MIDDNetherlands, Denmark, Germany, United Kingdom
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Wake Forest University Health SciencesCompletedHypophosphatemia | X-linked Hypophosphatemia | Left Ventricular Hypertrophy | Renin-angiotensin SystemUnited States
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Azienda Socio Sanitaria Territoriale degli Spedali...Active, not recruitingCritical Illness Myopathy | Neuromuscular Blockade | Critical Illness Polyneuropathy | Weakness Due to DiseaseItaly
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Human Stem Cell Institute, RussiaGenotargetEnrolling by invitationDysferlinopathy | Miyoshi Myopathy | LGMDR2 | DMATRussian Federation
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Ra PharmaceuticalsTerminatedImmune Mediated Necrotizing MyopathyUnited States, Netherlands, France, United Kingdom
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Newcastle-upon-Tyne Hospitals NHS TrustJain FoundationActive, not recruitingDysferlinopathy | LGMD2B Now Classified as LGMDR2 | Miyoshi MyopathyKorea, Republic of, Chile, Spain, United States, Denmark, France, Italy, Japan, United Kingdom
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DynacureWithdrawnCentronuclear MyopathyGermany, France
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DynacureWithdrawnCentronuclear Myopathy
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser... and other collaboratorsCompletedX-linked AdrenoleukodystrophyUnited States
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University of Massachusetts, WorcesterEnrolling by invitationMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophy | Frontotemporal Dementia | Miyoshi Myopathy | Amyotrophic Lateral Sclerosis, Sporadic | PLS | Lou Gehrigs Disease | Familial Disease | Amyotrophic Lateral Sclerosis With DementiaUnited States
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-linked HypophosphatemiaUnited Kingdom, France, Ireland, Italy
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NobelpharmaCompletedGNE Myopathy | Nonaka Disease | Distal Myopathy With Rimmed Vacuoles (DMRV) | Hereditary Inclusion Body Myopathy (hIBM)Japan
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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University of CalgaryMuscular Dystrophy CanadaEnrolling by invitationMuscular Dystrophies | Oculopharyngeal Muscular Dystrophy | Myopathy; HereditaryCanada
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Northern Care Alliance NHS Foundation TrustCompletedIdiopathic Inflammatory MyopathyUnited Kingdom
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Nantes University HospitalMinistry of Health, France; University Hospital, ToursCompletedShock | Critical Illness | Critical Illness Myopathy | Mechanical Ventilation | Nosocomial InfectionFrance, Guadeloupe
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Saglik Bilimleri UniversitesiMedical Park Hospital IstanbulCompletedIntensive Care Unit Acquired Weakness | Intensive Care (ICU) MyopathyTurkey
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Beth Israel Deaconess Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)CompletedAmyotrophic Lateral Sclerosis | Muscular Dystrophy | Radiculopathy | Trauma Injury | Orthopedic Disorder | Myopathy | Polyneuropathy and MononeuropathiesUnited States
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSpinal Muscular Atrophy Type 3 | Mitochondrial MyopathyUnited States
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National Institute of Allergy and Infectious Diseases...Completed
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General Hospital of Shenyang Military RegionCompleted
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Stealth BioTherapeutics Inc.TerminatedPrimary Mitochondrial MyopathyUnited States, Germany, Canada, Italy, United Kingdom, Denmark, Hungary
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OctapharmaCompletedDermatomyositisUnited States, Poland, Canada, Czechia, Germany, Hungary, Netherlands, Romania, Russian Federation, Ukraine
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Stealth BioTherapeutics Inc.TerminatedPrimary Mitochondrial DiseaseUnited States
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University Hospital, Basel, SwitzerlandUniversity of MinnesotaCompletedSepsis | Primary MyopathiesSwitzerland
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Abliva ABCompletedMitochondrial Diseases | Mitochondrial Myopathies | MELAS Syndrome | Mitochondrial Respiratory Chain DeficienciesUnited Kingdom
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Patagonia Pharmaceuticals, LLCCompletedCongenital IchthyosisUnited States
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University of California, San DiegoAmerican Heart AssociationCompletedStatin IntoleranceUnited States
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Assistance Publique - Hôpitaux de ParisCompletedX-linked Severe Combined ImmunodeficiencyFrance
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BiogenCompleted
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Yale UniversityCompletedIdiopathic Inflammatory MyopathiesUnited States