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Search clinical trials for: severe aplastic anemia
Total 13022 results
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University of EdinburghUniversity of OxfordRecruitingQuality of Life | Fatigue | Physical Disability | Anemia AcuteUnited Kingdom
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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Foresee Pharmaceuticals Co., Ltd.Recruiting
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University of ChicagoRecruitingSickle Cell DiseaseUnited States
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National Taiwan University HospitalRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Aplastic Anemia | Myeloproliferative NeoplasmTaiwan
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Academic and Community Cancer Research UnitedNational Cancer Institute (NCI)RecruitingBile Duct Adenocarcinoma | Fanconi Anemia Complementation Group Gene Mutation | Metastatic Bile Duct Carcinoma | PTEN Gene DeletionUnited States
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Paul SzabolcsRecruitingSickle Cell Anemia | Diamond-blackfan Anemia | Beta-thalassemia MajorUnited States
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M.D. Anderson Cancer CenterRecruitingFollicular Lymphoma | Acute Myeloid Leukemia | Hodgkin Lymphoma | Acute Lymphoblastic Leukemia | Mantle Cell Lymphoma | Chronic Lymphocytic Leukemia | Non-Hodgkin Lymphoma | Myelodysplastic Syndrome | Plasma Cell Myeloma | Aplastic Anemia | Myeloproliferative Neoplasm | Bone Marrow Failure | Chronic Myelogenous...United States
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Washington University School of MedicineRecruitingHemoglobinopathies | Bone Marrow Failure Syndromes | Metabolic Disorders | Non-malignant Disorders | Severe Sickle Cell Disease | Immunologic DisordersUnited States
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St. Jude Children's Research HospitalRecruitingPancreatic Cancer | Hodgkin Lymphoma | Lynch Syndrome | Tuberous Sclerosis | Fanconi Anemia | AML | Non Hodgkin Lymphoma | Familial Adenomatous Polyposis | Acute Leukemia | Nevoid Basal Cell Carcinoma Syndrome | Neurofibromatosis Type 1 | Neuroblastoma | Retinoblastoma | MDS | Rhabdomyosarcoma | Von Hippel-Lindau Disease | Adrenocortical Carcinoma and other conditionsUnited States
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Children's Hospital of PhiladelphiaRecruitingParoxysmal Nocturnal Hemoglobinuria | Acquired Aplastic Anemia | Inherited Bone Marrow Failure SyndromesUnited States
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University of RochesterRecruitingLymphoma | Myelodysplastic Syndromes | Multiple Myeloma | Solid Tumor | Acute Leukemia | Aplastic Anemia | Chronic Leukemia | Immune Deficiency Disorder | Congenital Hematological Disorder | Metabolism DisorderUnited States
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Mayo ClinicRecruitingHematologic Neoplasms | Myeloid Malignancy | Cytopenia | Bone Marrow Failure Syndrome | Clonal Cytopenia of Undetermined Significance | Clonal Hematopoiesis of Indeterminate Potential | Low Risk Myelodysplastic Syndrome | Inherited Bone Marrow Failure Syndrome | Clonal Expansion | Hereditary Neoplastic... and other conditionsUnited States
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Children's Hospital of PhiladelphiaRecruiting
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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National Heart, Lung, and Blood Institute (NHLBI)National Cancer Institute (NCI); National Institute of Allergy and Infectious... and other collaboratorsRecruitingLymphoma | Leukemia | Aplastic Anemia | Myelodysplastic Syndrome (MDS)United States
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Massachusetts General HospitalRecruitingBone Marrow and Kidney Transplant for Patients With Chronic Kidney Disease and Blood Disorders (BMT)Autoimmune Diseases | Multiple Myeloma | Hodgkin Disease | AL Amyloidosis | Myelofibrosis | Chronic Kidney Disease | Sickle Cell Anemia | Thalassemia | Aplastic Anemia | Chronic Lymphocytic Leukemia (CLL) | Acute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS) | Non-Hodgkin... and other conditionsUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)RecruitingPreviously Treated Myelodysplastic Syndrome | Myelodysplastic Syndrome | Aplastic Anemia | de Novo Myelodysplastic SyndromeUnited States
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UNC Lineberger Comprehensive Cancer CenterNational Cancer Institute (NCI)RecruitingLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Multiple Myeloma and Plasma Cell Neoplasm | Nonmalignant Neoplasm | Lymphoproliferative Disorder | Myelodysplastic/Myeloproliferative NeoplasmsUnited States
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Feinstein Institute for Medical ResearchDiamond Blackfan Anemia Foundation, Inc.Recruiting
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Hematological DiseasesUnited States, Belgium, Canada, France, Germany, Italy, United Kingdom
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Janssen Research & Development, LLCActive, not recruitingHemolytic Disease of the Fetus and NewbornUnited States, Canada, Netherlands, Belgium, Germany, Spain, Sweden, United Kingdom, Australia
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group ASpain, United Kingdom
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Fred Hutchinson Cancer CenterNational Heart, Lung, and Blood Institute (NHLBI); Rocket Pharma LimitedTerminated
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Kyowa Kirin Korea Co., Ltd.CompletedAplastic AnemiaKorea, Republic of
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Sanguine BiosciencesTerminated
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Seoul National University HospitalMerck Sharp & Dohme LLCCompletedMyelodysplastic Syndromes | Fungal Infection | Aplastic AnemiaKorea, Republic of
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Medical College of WisconsinNational Heart, Lung, and Blood Institute (NHLBI); Dana-Farber Cancer Institute and other collaboratorsCompletedSickle Cell DiseaseUnited States
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group AUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI)Active, not recruitingLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative Diseases | Graft Versus Host Disease | Precancerous/Nonmalignant Condition
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingTobacco Use Disorder | Fanconi Anemia | Lichen Planus | Oral Neoplasm | Erythroplakia | Premalignant Lesion | Oral Cavity and Lip Precancerous Condition | Oral Cavity LeukoplakiaUnited States
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Vanderbilt University Medical CenterAminu Kano Teaching Hospital; Murtala Muhammad Specialist HospitalCompletedSickle Cell Anemia | Severe Acute MalnutritionNigeria, United States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Bellicum PharmaceuticalsTerminatedHemoglobinopathies | Hemophagocytic Lymphohistiocytosis | Metabolic Disorders | Primary Immune Deficiency Disorders | Inherited Bone Marrow Failure SyndromeUnited States
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria de... and other collaboratorsCompletedFanconi AnemiaSpain
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Jonathan H. WatersHbO2 Therapeutics LLCAvailableAnemia SevereUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Congenital Hemolytic AnemiaUnited States
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bluebird bioCompletedSickle Cell DiseaseUnited States
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Boston Children's HospitalMassachusetts General Hospital; Mayo Clinic; Karolinska University Hospital; Baylor... and other collaboratorsActive, not recruitingAplastic Anemia | Dyskeratosis Congenita | Hoyeraal Hreidarsson Syndrome | Revesz SyndromeUnited States, Norway, Sweden
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Children's Hospital Medical Center, CincinnatiFood and Drug Administration (FDA)Completed
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London School of Hygiene and Tropical MedicineBill and Melinda Gates Foundation; Wellcome TrustCompletedIntrapartum - Moderate and Severe AnaemiaNigeria, Pakistan, Tanzania, Zambia
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Jennifer WoyachJanssen Scientific Affairs, LLCCompletedHematopoietic and Lymphoid Cell Neoplasm | Malignant Solid Neoplasm | Monoclonal Gammopathy of Undetermined Significance | Myelodysplastic Syndrome | Aplastic Anemia | Symptomatic COVID-19 Infection Laboratory-Confirmed | Monoclonal B-Cell LymphocytosisUnited States
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Center for International Blood and Marrow Transplant...National Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Hodgkin Lymphoma | Acute Lymphoblastic Leukemia | Sickle Cell Disease | Non-hodgkin Lymphoma | Acquired Aplastic AnemiaUnited States
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Jiangsu HengRui Medicine Co., Ltd.Completed
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Memorial Sloan Kettering Cancer CenterActive, not recruiting