- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Genetic Therapy
Total 68693 results
-
Bacchetta, Rosa, MDFood and Drug Administration (FDA); California Institute for Regenerative Medicine...Recruiting
-
I.M. Sechenov First Moscow State Medical UniversityRecruitingHeart Failure | Cardiomyopathies | Dilated Cardiomyopathy | Sudden Cardiac Death | Lymphocytic Myocarditis (Disorder)Russian Federation
-
Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RecruitingHaploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion (HAPLOTAB)Myelodysplastic Syndromes | Primary Immunodeficiency Diseases | Hemoglobinopathies | Chronic Myeloid Leukemia | Cytopenia | Severe Aplastic Anemia | Bone Marrow Failure Syndrome | Acute Myeloid Leukemia in Remission | Hemophagocytic Lymphohistiocytoses | Acute Lymphoblastic Leukemia in Remission | Severe...United States
-
Cairo UniversityRecruitingEntrapment NeuropathiesEgypt
-
General University Hospital, PragueNot yet recruiting
-
Asklepios Biopharmaceutical, Inc.RecruitingMuscular Dystrophy | Limb Girdle Muscular Dystrophy | LGMD2I | LGMD | Limb-Girdle Muscular Dystrophy Type 2 | LGMD2 | FKRP | FKRP Mutation | Fukutin Related ProteinUnited States
-
Neurogene Inc.RecruitingNeuronal Ceroid Lipofuscinosis CLN5United States, United Kingdom
-
Delta University for Science and TechnologyRecruitingAtaxic Cerebral PalsyEgypt
-
Atamyo TherapeuticsRecruiting
-
Medical University of SilesiaRecruiting
-
University of British ColumbiaRecruiting
-
University of FloridaRecruiting
-
Xuanwu Hospital, BeijingRecruitingGait | Motor FunctionChina
-
University Hospital, MontpellierRecruitingHemophilia A | Hemophilia B | ArthropathyFrance
-
Ohio State UniversityNationwide Children's HospitalRecruiting
-
2seventy bioRecruitingDiffuse Large B Cell Lymphoma (DLBCL)United States
-
Ottawa Hospital Research InstituteRecruitingProstate CancerCanada
-
TakedaRecruitingLennox Gastaut Syndrome (LGS) | Dravet Syndrome (DS)United States, China, Spain, France, Belgium, Australia, Brazil, Canada, Germany, Greece, Hungary, Italy, Japan, Latvia, Netherlands, Poland, Serbia, Mexico, Russian Federation, Ukraine
-
Vanderbilt University Medical CenterJohns Hopkins University; Emory University; Children's National Research InstituteRecruitingHeart Disease | Sickle Cell Disease | Pulmonary Disease | Renal DiseaseUnited States
-
Institute of Hematology & Blood Diseases HospitalRecruiting
-
National Cancer Institute (NCI)Childrens Oncology Group (COG); LLS PedAL LLCRecruitingDown Syndrome | Recurrent Acute Myeloid Leukemia | Recurrent Myelodysplastic Syndrome | Refractory Acute Myeloid Leukemia | Refractory Myelodysplastic Syndrome | Recurrent Mixed Phenotype Acute Leukemia | Refractory Mixed Phenotype Acute Leukemia | Acute Myeloid Leukemia Post Cytotoxic Therapy | Myelodysplastic...United States
-
The Foundation for Orthopaedics and Regenerative...RecruitingGlaucoma | Eye Diseases | Macular Degeneration | Diabetic Retinopathy | Retinitis Pigmentosa | Optic Atrophy | Traumatic Optic NeuropathyAntigua and Barbuda, Argentina, Mexico
-
Capricor Inc.RecruitingNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States
-
Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RecruitingSolid Tumor | Liposarcoma | Rhabdomyosarcoma | Wilms Tumor | Malignant Rhabdoid Tumor | Yolk Sac Tumor | Liver Cell Carcinoma | Embryonal Sarcoma of the LiverUnited States
-
Adrenas Therapeutics IncRecruitingCongenital Adrenal HyperplasiaUnited States
-
University Hospital, MontpellierHôpital Cochin; Hôpital Necker-Enfants Malades; Foch Hospital, Suresnes, FRANCERecruitingCystic Fibrosis | CFTR Gene MutationFrance
-
Charite University, Berlin, GermanyRecruiting
-
Universitat Pompeu FabraHospital Clinic of BarcelonaRecruiting
-
AbbVieRecruitingAtopic DermatitisAustralia, Austria, Canada, Spain, Switzerland, Taiwan, United Arab Emirates, Poland, Czechia, Greece, Russian Federation, Italy, Israel, Argentina, Hungary, Mexico
-
Assistance Publique - Hôpitaux de ParisRecruitingArtemis (DCLRE1C ) Deficient Severe Combined ImmunodeficiencyFrance
-
EpygenixNot yet recruiting
-
Genprex, Inc.RecruitingNon Small Cell Lung CancerUnited States
-
Marquette UniversityUniversity of UtahRecruitingTourette Disorder | Persistent Tic DisordersUnited States
-
St. Jude Children's Research HospitalRecruitingHemophilia B | Gene TherapyUnited States
-
Mark TuszynskiOhio State UniversityRecruitingMild Cognitive Impairment | Alzheimer's DiseaseUnited States
-
National Cancer Institute (NCI)RecruitingKita-kyushu Lung Cancer Antigen 1, HumanUnited States
-
LMU KlinikumDepartment of Internal Medicine V, Thoracic Oncology Centre Munich, LMU Munich... and other collaboratorsRecruitingOncology | NSCLC, Stage III | Chemoradiotherapy | Biomarker | DurvalumabGermany
-
First Affiliated Hospital Xi'an Jiaotong UniversitySimcere CompanyRecruitingCerebral Infarction | G6PD DeficiencyChina
-
National Cancer Institute (NCI)RecruitingHepatocellular Carcinoma | Hepatocellular Cancer | Metastatic Hepatocellular CarcinomaUnited States
-
Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
-
National Medical Research Center for Children's...RecruitingCongenital IchthyosisRussian Federation
-
Help TherapeuticsXijing HospitalRecruitingCardiovascular Diseases | Dilated Cardiomyopathy | Congestive Heart FailureChina
-
University Medical Centre LjubljanaNot yet recruitingPhenylketonurias | Nutritional and Metabolic Diseases
-
Rabin Medical CenterRecruiting
-
Central Hospital, Nancy, FranceRecruitingPompe's Disease Juvenile OnsetFrance
-
The University of QueenslandRecruitingAutosomal Dominant Polycystic Kidney DiseaseAustralia
-
Wuhan Neurophth Biotechnology Limited CompanyRecruitingLeber's Hereditary Optic Neuropathy (LHON)China
-
The Methodist Hospital Research InstituteGenentech, Inc.Recruiting
-
Monaldi HospitalRecruitingHeart Failure | Lamin A/C Gene Mutation | LaminopathyItaly
-
St. Jude Children's Research HospitalRecruitingMelanoma | Soft Tissue Sarcoma | Carcinoma | Osteosarcoma | Ewing Sarcoma | Rhabdoid Tumor | Neuroblastoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Desmoplastic Small Round Cell Tumor | Pediatric Solid Tumor | Clear Cell Sarcoma | Malignant Peripheral Nerve Sheath Tumors | Adrenocortical Cancer | Germ Cell CancerUnited States