- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Heredodegenerative Disorders of the Nervous System
Total 474719 results
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NYU Langone HealthNational Institutes of Health (NIH)CompletedObsessive-Compulsive Disorder | Tourette Syndrome | Tic DisordersUnited States
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Sangamo TherapeuticsActive, not recruitingHemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIUnited States
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Teachers College, Columbia UniversityActive, not recruitingSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6 | Spinocerebellar Ataxia Type 7United States
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Bowdoin CollegeMassachusetts General HospitalCompletedTourette Syndrome | Persistent Tic DisorderUnited States
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Denali Therapeutics Inc.Active, not recruitingMucopolysaccharidosis IIUnited States, Netherlands, Canada, United Kingdom
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Beyond Batten Disease FoundationTheranexusActive, not recruitingBatten DiseaseUnited States
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Rare Thyroid Therapeutics International ABVitaccess LtdCompletedAllan-Herndon-Dudley Syndrome | Monocarboxylate Transporter 8 (MCT8) DeficiencyUnited Kingdom
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Neurophth Therapeutics IncActive, not recruitingLeber Hereditary Optic Neuropathy (LHON)United States
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Seelos Therapeutics, Inc.TerminatedSpinocerebellar Ataxia Type 3United States, Spain, Korea, Republic of, Australia, United Kingdom, Brazil, Germany, Portugal
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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Sanguine BiosciencesCompletedDepression | Melanoma | Epilepsy | Lymphoma | Multiple Sclerosis | Kidney Cancer | Cervical Cancer | Diabetes Mellitus | Leukemia | Breast Cancer | Chronic Kidney Diseases | Chronic Obstructive Pulmonary Disease | Parkinson's Disease | Systemic Lupus Erythematosus | Multiple Myeloma | Hepatitis B | Insomnia | Colorectal Cancer | HIV/AID... and other conditionsUnited States
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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Johns Hopkins UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Virginia Polytechnic...CompletedCerebellar Ataxia | Spinocerebellar Ataxias | Cerebellar DegenerationUnited States
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The Cleveland ClinicActive, not recruitingAL Amyloidosis | Amyloidosis | Amyloid Neuropathies, Familial | Amyloid | Transthyretin Amyloidosis | Amyloid Cardiomyopathy | Amyloid - PrimaryUnited States
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TakedaAvailableHunter SyndromeUnited States, Australia, Mexico, Spain, United Kingdom
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Cellatoz Therapeutics, IncActive, not recruitingCharcot Marie Tooth Disease, Type 1Korea, Republic of
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Pharnext S.C.A.Worldwide Clinical TrialsActive, not recruitingCharcot-Marie-Tooth DiseaseUnited States, Spain, Belgium, Italy, Israel, Canada, Denmark, France, Germany
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Istanbul University - Cerrahpasa (IUC)CompletedLow Back Pain | Nerve Entrapment Syndrome | Radiating PainTurkey
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Max Planck Institute for Human Cognitive and Brain...Hannover Medical School; Leipzig University Medical CenterCompletedTourette Syndrome | Gilles de la Tourette SyndromeGermany
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Max Planck Institute for Human Cognitive and Brain...Hannover Medical School; Leipzig University Medical CenterCompletedTourette Syndrome | Gilles de la Tourette SyndromeGermany
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SpringWorks Therapeutics, Inc.Active, not recruitingPlexiform Neurofibroma | Neurofibromatosis Type 1 (NF1)United States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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OrphalanCompletedWilson DiseaseUnited States, United Kingdom, Belgium, Brazil, Denmark, France, Germany, Italy, Poland
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.TerminatedNeurofibromatosis and Malignant Peripheral Nerve Sheath TumorsChina
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); St. Jude Children... and other collaboratorsEnrolling by invitationAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Progressive Muscular Atrophy | Hereditary Spastic Paraplegia | Multisystem ProteinopathyUnited States, South Africa, Germany
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Children's Hospital Medical Center, CincinnatiActive, not recruitingNeurofibromatosis 1United States
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SpringWorks Therapeutics, Inc.AvailableNeurofibromatosis Type 1-Associated Plexiform Neurofibromas | Histiocytic Neoplasm | Other MAP-K Pathway Driven Diseases
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IRCCS Eugenio MedeaCompletedCerebral Palsy | Acquired Brain Injury | Hereditary Spastic ParaplegiaItaly
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State University of New York at BuffaloThe Callum McKeefery and Nikki Albano McKeefery Pediatric Division of Genetics...CompletedMitochondrial Diseases | Optic Atrophy | Neurodegenerative Disease, HereditaryUnited States
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Hoffmann-La RocheCompletedHuntingtons DiseaseUnited States, United Kingdom, Australia, Canada, Japan, Poland, Netherlands, Germany, Russian Federation, France, Spain, Argentina, New Zealand, Austria, Denmark, Italy, Switzerland, Chile
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Design Therapeutics, Inc.CompletedFriedreich AtaxiaUnited States
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Novartis Gene TherapiesActive, not recruitingSpinal Muscular Atrophy 1United States
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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Pharnext S.C.A.Premier Research Group plc; Eurofins Optimed; Synteract HCR (Syneos Health); Gr... and other collaboratorsActive, not recruitingCharcot-Marie-Tooth Disease, Type IAUnited States, Belgium, Canada, France, Netherlands, Spain, United Kingdom
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University Hospital, BordeauxCentre National de la Recherche Scientifique, FranceCompleted
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Istituto Auxologico ItalianoFondazione Serena Onlus - Centro Clinico NeMO MilanoCompletedMyotonic Dystrophy 1Italy
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Larimar Therapeutics, Inc.CompletedFriedreich AtaxiaUnited States
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University Hospitals Bristol and Weston NHS Foundation...University College, London; The Tuberous Sclerosis AssociationActive, not recruitingTuberous Sclerosis ComplexUnited Kingdom
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Poland, Argentina, Australia, Belgium, France, Germany, Japan, Netherlands, Portugal, Spain, Sweden, United Kingdom, Canada, Czechia, Denmark, Hungary, Ireland, Norway, Korea, Republic of, Austria, Croatia, Israel, Latvia, Lithuan... and more
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PfizerCompletedTransthyretin Amyloidosis Cardiomyopathy (ATTR-CM)Italy, Romania, France, Australia, Austria, Portugal, Slovakia, Slovenia, Spain, United Kingdom
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University of RochesterCompletedHuntington Disease | ChoreaUnited States
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Spaulding Rehabilitation HospitalMassachusetts General HospitalWithdrawnHereditary Spastic Paraplegia
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Roger PackerWithdrawnNeurofibromatosis Type 1 | Tumors of the Central Nervous SystemUnited States
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University of MinnesotaCompletedTourette Syndrome | Tic Disorders | Tics | Tourette Syndrome in Children | Tourette Syndrome in Adolescence | Tic Disorder, Childhood | Tic, MotorUnited States
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Novartis PharmaceuticalsCompletedEarly Manifest Huntington DiseaseCanada, Germany, France, Spain, Hungary
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada