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Search clinical trials for: Inherited Bone Marrow Failure Syndromes
Total 57475 results
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Indiana University School of MedicineCompletedMyelodysplastic Syndromes | Leukemia | Myeloproliferative Disorders | Multiple Myeloma | Non-Hodgkin's Lymphoma | Chronic Lymphocytic Leukemia | Chronic Myelogenous Leukemia | Aplastic Anemia | Hodgkin's DiseaseUnited States
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University of Erlangen-Nürnberg Medical SchoolGerman Research Foundation; University Hospital, Essen; Wuerzburg University... and other collaboratorsUnknownAcute Myeloid Leukemia | Multiple Myeloma | Acute Lymphoblastic Leukemia | Chronic Myeloid Leukemia | Myelodysplastic Syndrome | Aplastic Anemia | Non Hodgkin's Lymphoma | Hodgkin's DiseaseGermany
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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Cystinosis Research FoundationUnknownCystinosis | Nephropathic Cystinosis | Renal Fanconi SyndromeUnited States
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of Medicine; University of...TerminatedFANCONI ANEMIAUnited States
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Milton S. Hershey Medical CenterUnknownSarcoma | Lymphoma | Unspecified Childhood Solid Tumor, Protocol Specific | Myelodysplastic Syndromes | Leukemia | Fanconi Anemia | Neuroblastoma | Childhood Langerhans Cell HistiocytosisUnited States
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University of California, San FranciscoNational Cancer Institute (NCI)UnknownLymphoma | Kidney Cancer | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative NeoplasmsUnited States
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Xiaofan ZhuAvailableFanconi Anemia | Autosomal or Sex Linked Recessive Genetic Disease | Bone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases. | Hematopoiesis Maintainance.China
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Texas Oncology Cancer CenterTerminatedMultiple Myeloma | Chronic Lymphocytic Leukemia | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Aplastic Anemia | Non-Hodgkins Lymphoma | Hodgkins DiseaseUnited States
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Asan Medical CenterCompleted
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M.D. Anderson Cancer CenterGenzyme, a Sanofi CompanyCompletedMyelodysplastic Syndrome | Aplastic AnemiaUnited States
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Institute of Hematology & Blood Diseases HospitalUnknownUrination Disorders | Thrombosis | Proteinuria | Anemia, Hemolytic | Hemoglobinuria, Paroxysmal | Hemoglobinuria | Paroxysmal Nocturnal Hemoglobinuria | Bone Marrow Failure | Aplastic Anemia,China
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Institute of Hematology & Blood Diseases HospitalUnknownUrination Disorders | Thrombosis | Proteinuria | Anemia, Hemolytic | Hemoglobinuria, Paroxysmal | Hemoglobinuria | Paroxysmal Nocturnal Hemoglobinuria | Bone Marrow Failure | Aplastic Anemia,China
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedLeukemia | Thrombocytopenia | Fanconi Anemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital Neutropenia | Diamond-blackfan AnemiaUnited States
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital NeutropeniaUnited States
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M.D. Anderson Cancer CenterEisai Inc.TerminatedChronic Myelomonocytic Leukemia | Myelodysplastic SyndromeUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedFanconi AnemiaUnited States, Brazil
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Columbia UniversityUnknownSevere Combined Immunodeficiency | Fanconi Anemia | Bone Marrow Failure | OsteopetrosisUnited States
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Children's Hospital Medical Center, CincinnatiFDA Office of Orphan Products DevelopmentCompleted
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Novartis PharmaceuticalsCompletedMyelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan AnemiaUnited States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
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Cooperative Study Group A for HematologyCompletedBone Marrow Failure SyndromesKorea, Republic of
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Myelodysplastic/Myeloproliferative DiseasesUnited States
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King's College LondonKing's College Hospital NHS TrustUnknownAcute Myeloid Leukemia | Chronic Myelomonocytic Leukemia | Myelodysplastic SyndromeUnited Kingdom
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AlexionCompleted
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic Syndromes | Purpura, Thrombocytopenic | Anemia, Aplastic | Red-Cell Aplasia, Pure | Bone Marrow Failure Syndromes | Hemoglobinuria, Paroxysmal | Leukemia, LymphocyticUnited States
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States
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PETHEMA FoundationCompletedMyelodysplastic SyndromeSpain
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National Heart, Lung, and Blood Institute (NHLBI)CompletedDiamond Blackfan AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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University of MinnesotaUnknown
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National Center for Research Resources (NCRR)University of California, Los AngelesCompletedThrombocytopenia | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Fanconi's Anemia | Thalassemia Major | Pure Red-Cell AplasiaUnited States
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National Center for Research Resources (NCRR)University of California, San DiegoCompletedFanconi Syndrome | Cystinosis
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Fairview University Medical CenterCompleted
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Dana-Farber Cancer InstituteUnknownFanconi's AnemiaUnited States
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Fairview University Medical CenterCompletedMyelodysplastic Syndromes | Leukemia, Lymphocytic, Acute | Fanconi's Anemia | Leukemia, Nonlymphocytic, AcuteUnited States
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University of MinnesotaCompleted
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St. Petersburg State Pavlov Medical UniversityRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Acute Lymphoblastic Leukemia | Lymphoblastic Lymphoma | Myeloproliferative Neoplasm | Biphenotypic Acute LeukemiaRussian Federation
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Federal Research Institute of Pediatric Hematology...RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Acute Lymphoblastic Leukemia | Malignant Lymphoma | Biphenotypic Acute LeukemiaRussian Federation
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Navy General Hospital, BeijingNot yet recruitingHigher-risk Myelodysplastic SyndromesChina
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Institut de Recherches Internationales ServierServier Bio-Innovation LLCNot yet recruitingMyelodysplastic Syndromes (MDS) | Hypomethylating Agent (HMA) Naive Myelodysplastic Syndromes (MDS)
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Minovia Therapeutics Ltd.Recruiting
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Tr1X, Inc.RecruitingMyelodysplastic Syndromes | Hematologic Malignancy | Hematopoietic Stem Cell Transplant | Acute Myeloid Leukemia in Remission | GVHD, Chronic | GVHD,Acute | GvHD | Acute Lymphoblastic Leukemia, Adult B-Cell | Cancer Remission | Acute Lymphoblastic Leukemia, Adult T-Cell | Chronic Myelomonocytic Leukemia,...United States
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TC BiopharmNot yet recruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes
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City of Hope Medical CenterNational Cancer Institute (NCI)Not yet recruitingRecurrent Acute Myeloid Leukemia | Recurrent Myelodysplastic Syndrome | Refractory Acute Myeloid Leukemia | Refractory Myelodysplastic Syndrome | Myelodysplastic Syndrome/Acute Myeloid LeukemiaUnited States
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Alexion Pharmaceuticals, Inc.Not yet recruitingParoxysmal Nocturnal Hemoglobinuria | PNH | Extravascular Hemolysis
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Nantes University HospitalInstitut National de la Santé Et de la Recherche Médicale, FranceNot yet recruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Chronic Myelomonocytic LeukemiaFrance
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Memorial Sloan Kettering Cancer CenterRecruitingAplastic Anemia | Cytopenia | Hypocellular MarrowUnited States
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Peking Union Medical College HospitalNot yet recruiting
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Peking Union Medical College HospitalNot yet recruiting
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Bristol-Myers SquibbRecruitingAcute Myeloid Leukemia | Myelodysplastic SyndromeCanada, United States