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Search clinical trials for: Inborn Brain Diseases
Total 379764 results
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Capital Medical UniversityWangjing Hospital, China Academy of Chinese Medical Sciences; Bejing Fengtai...RecruitingCerebral Amyloid Angiopathy | Intracerebral Hemorrhage LobarChina
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M.A.G.I.C. Clinic LTDHanalytics Solutions Inc.RecruitingMitochondrial Diseases | Fabry Disease | Metabolic Disease | Gaucher Disease | Pompe DiseaseCanada
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Rambam Health Care CampusRecruitingPompe Disease Infantile-OnsetIsrael
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Mayo ClinicRecruitingCerebral Small Vessel Diseases | Cerebral Autosomal Dominant Arteriopathy With Subcortical Infarcts and Leukoencephalopathy | Cerebral Microbleeding | Sporadic White Matter DiseaseUnited States
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M.D. Anderson Cancer CenterRecruitingDepression | Hematopoietic and Lymphoid Cell Neoplasm | Malignant Solid Neoplasm | Anxiety Disorder | Genetic DisorderUnited States
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Hospital de Clinicas de Porto AlegreRecruitingSpinocerebellar Ataxia Type 3 | Machado-Joseph Disease | SCA3 | MJDBrazil
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Vanderbilt University Medical CenterTeva Branded Pharmaceutical Products R&D, Inc.RecruitingHuntington DiseaseUnited States
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Rigshospitalet, DenmarkRecruitingCerebral Palsy | Muscular DystrophiesDenmark
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Leipzig University Medical CenterRecruitingX-linked AdrenoleukodystrophyGermany
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Spain, United Kingdom, Netherlands
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Shenzhen Second People's HospitalNot yet recruitingCerebral Amyloid Angiopathy
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Hospital General Universitario Gregorio MarañonHospital Clinic of Barcelona; University of SalamancaRecruitingStroke | Dilated Cardiomyopathy | Hypertrophic Cardiomyopathy | Thrombosis CardiacSpain
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Yonsei UniversityRecruitingFabry DiseaseKorea, Republic of
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Duke UniversitySanofiRecruiting
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SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt)RecruitingGangliosidoses | Galactosialidosis | Sialidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Morquio B Disease | Gm2-Gangliosidosis, Variant B1 | GM2 Activator DeficiencyGermany
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Baylor College of MedicineChildren's Hospital of Philadelphia; Children's Hospital Colorado; Seattle Children... and other collaboratorsRecruitingOrnithine Transcarbamylase Deficiency | Urea Cycle Disorder | Argininosuccinic Aciduria | Hyperargininemia | Citrullinemia 1 | ARGI Deficiency | ASL Deficiency | ASS DeficiencyUnited States
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National Taiwan University HospitalRecruitingCerebral Amyloid Angiopathy | Intracerebral HemorrhageTaiwan
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Children's National Research InstituteNational Center for Advancing Translational Sciences (NCATS)RecruitingHypoxic-Ischemic Encephalopathy | Urea Cycle Disorder | Organic Acidemia | Fatty Acid Oxidation Disorder | Maple Syrup Urine Disease | Glutaric Acidemia IUnited States
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Christian BaumannETH ZurichRecruitingParkinson Disease | Mild Cognitive Impairment | Huntington DiseaseSwitzerland
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Netherlands, Spain, United Kingdom
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Nemours Children's ClinicPotentials Foundation; Walking with Giants FoundationRecruitingMOPDII | RNU4atac-opathy (e.g. MOPDI/III, Lowry-Wood Syndrome, Roifman Syndrome) | Meier-Gorlin Syndrome | Saul-Wilson Syndrome | Ligase 4 Syndrome | Microcephalic Primordial DwarfismUnited States
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Vivet Therapeutics SASRecruitingWilson's DiseaseUnited States, Denmark, Germany, United Kingdom
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University of California, San FranciscoDuke UniversityRecruitingWolman Disease | MPS IVA | Pompe Disease Infantile-Onset | Gaucher Disease, Type 2 | MPS VI | MPS I | Gaucher Disease, Type 3 | MPS II | Mps VIIUnited States
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Mayo ClinicRecruitingCerebellar Ataxia | Spinocerebellar Ataxias | Nucleotide Repeat DiseaseUnited States
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The Methodist Hospital Research InstituteHospital de Clinicas de Porto AlegreRecruitingSpinocerebellar Ataxia Type 10United States, Brazil
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Jazz PharmaceuticalsRecruitingSeizure in Participants With Tuberous Sclerosis Complex | Seizure in Participants With Dravet Syndrome | Seizure in Participants With Lennox-Gastaut SyndromeUnited States
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Fundación Pública Andaluza para la gestión de la...Ciberned (Centro de Investigación Biomédica en Red)RecruitingHuntington DiseaseSpain
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Serhat Gumrukcu, MD PhDFrida Therapeutics LLCRecruiting
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Oregon Health and Science UniversityRecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Multiple System Atrophy | Parkinson's Disease and Parkinsonism | Brain Tumor Adult | Locked-in Syndrome | Brainstem StrokeUnited States
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dr. Laura C. G. de Graaff-HerderRecruitingDisorders of Sex Development | Congenital Adrenal Hyperplasia | Tuberous Sclerosis | Kallmann Syndrome | Prader-Willi Syndrome | Neurofibromatosis | Rett Syndrome | 22q11 Deletion Syndrome | Turner Syndrome | Noonan Syndrome | Allan-Herndon-Dudley Syndrome | Saethre-Chotzen Syndrome | Congenital Hypopituitarism | Cornelia... and other conditionsNetherlands
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University Hospital, Strasbourg, FranceRecruitingBardet-Biedl Syndrome | Alström SyndromeFrance
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Assistance Publique - Hôpitaux de ParisRecruitingTourette SyndromeFrance
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Institut National de la Santé Et de la Recherche...Not yet recruitingFabry Disease
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University Hospital, LilleNot yet recruiting
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Western University, CanadaNot yet recruitingHuntington Disease
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Washington University School of MedicineNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingBrain Diseases | Sickle Cell Disease | Anemia, Sickle Cell | Child, OnlyUnited States
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Emory UniversityBioMarin PharmaceuticalRecruitingPhenylketonuriasUnited States
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Yale UniversityRheumatology Research FoundationRecruitingRheumatic Diseases | Rheumatoid Arthritis | Systemic Lupus Erythematosus | Systemic Sclerosis | Dermatomyositis | Polymyositis | Giant Cell Arteritis | Polymyalgia Rheumatica | Psoriatic Arthritis | Sjogren's Syndrome | Antiphospholipid Syndrome | Sarcoidosis | Lyme Disease | Ankylosing Spondylitis | Scleroderma | Reactive... and other conditionsUnited States
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National University of MalaysiaRadboud University Medical CenterRecruiting
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Sun Yat-sen UniversityRecruitingBreast Cancer | Cognitive Impairment | Brain Metastases | Radiotherapy Side Effect | Gangliosidosis, GM1China
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University Hospital, LilleRecruiting
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Shaare Zedek Medical CenterRecruitingParkinson Disease | Gaucher Disease | GBA Gene MutationIsrael
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Nelly PitteloudRecruitingDown Syndrome | Cognitive Decline | Alzheimer Disease, Early Onset | Olfaction DisordersSwitzerland
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Fundacion Huntington Puerto RicoNot yet recruiting
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Dr. Rebecca SchuleGerman Research Foundation; German Center for Neurodegenerative Diseases (DZNE)RecruitingSpastic AtaxiaCanada, France, Germany, Italy, Netherlands, Turkey, United Kingdom
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Nutricia UK LtdNot yet recruitingPhenylketonurias | Hyperphenylalaninaemia
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Fondazione I.R.C.C.S. Istituto Neurologico Carlo...Istituto Di Ricerche Farmacologiche Mario NegriRecruitingHuntington DiseaseItaly
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Amicus TherapeuticsRecruiting
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Beijing Municipal Administration of HospitalsMedtronicRecruitingHuntington Disease | Deep Brain StimulationChina