Search clinical trials for: Rare Neurogenetic Conditions

Total 438665 results

Juventas Cell Therapy Ltd.

Not yet recruiting

Inaticabtagene Autoleucel Injection Treatment for Adult Relapsed or Refractory Acute Lymphocytic Leukemia

B-cell Acute Lymphoblastic Leukemia
Assistance Publique - Hôpitaux de Paris

Not yet recruiting

Modeling Amyotrophic Lateral Sclerosis With Fibroblasts (FIBRALS)

Amyotrophic Lateral Sclerosis

France
Institute of Hematology & Blood Diseases Hospital...

Recruiting

Selinexor、Venetoclax and Azactidine in the Treatment of ND AML Patients Who Are Not Eligible for Intense Chemotherapy

Acute Myeloid Leukemia, Adult

China
Central Hospital, Nancy, France

Not yet recruiting

Janus Kinase Inhibitors for the Treatment of Acute Severe Ulcerative Colitis (ATTRACT)

Inflammatory Bowel Diseases | Ulcerative Colitis

France
Hoffmann-La Roche

Not yet recruiting

An Open-label Study to Assess the Efficacy and Safety of Satralizumab in Duchenne Muscular Dystrophy (SHIELD DMD)

Duchenne Muscular Dystrophy

United States
Fudan University

Recruiting

A Cohort Study in Newly Diagnosed MZL

Marginal Zone Lymphoma

China
Zhujiang Hospital

Recruiting

Effect of Henagliflozein on Hepatic Fat Content in Patients With T2DM and NAFLD (HHTN)

Nonalcoholic Fatty Liver Disease | Type2 Diabetes Mellitus

China
TBF Genie Tissulaire

Not yet recruiting

Use of a Freeze-dried Amniotic Membrane Post Crosslinking in Subjects With Progressive Keratoconus

Progressive Keratoconus
Hacettepe University

Recruiting

Exercise Capacity, Physical Fitness, and Physical Activity Levels in Children With CAH

Quality of Life | Congenital Adrenal Hyperplasia | Physical Activity | Exercise Capacity

Turkey
Chinese University of Hong Kong
University of Palermo; University of Malaya; Singapore General Hospital; University... and other collaborators

Not yet recruiting

Non-selective Beta-blocker in Compensated Advanced Chronic Liver Disease (BB_cACLD)

Portal Hypertension | Advanced Chronic Liver Disease | Hepatic Decompensation
NEXBIOME THERAPEUTICS

Not yet recruiting

Efficacy, Safety, and Dose-response of a Live Biotherapeutic Product in Women With Acute Vaginal Infection (ELINA)

Bacterial Vaginosis | Vulvovaginal Candidiasis
American University of Beirut Medical Center

Not yet recruiting

An Endotracheal Tube Inserted to the Level of the Hypopharynx

Pediatric ALL | Intubation; Difficult or Failed | Ventilator Lung
Nantes University Hospital

Recruiting

Parathyroid Assessment of Symptoms French Version (PAS_fr)

Quality of Life in Primary Hyperparathyroidism

France
Janssen Research & Development, LLC

Recruiting

A Study of Nipocalimab in Reducing the Risk of Fetal and Neonatal Alloimmune Thrombocytopenia (FNAIT) (FREESIA-1)

Thrombocytopenia, Neonatal Alloimmune

Spain, Belgium, Norway, Slovakia, Italy, Sweden
Pfizer

Recruiting

A Study in Advanced/Metastatic Solid Tumors With the Study Medicine (PF-07329640) When Given Alone or In Combination (LTbR)

Melanoma | Colorectal Cancer | Non-Small Cell Lung Cancer | Urothelial Cancer | Advanced or Metastatic Solid Tumors

United States, Puerto Rico
Sohag University

Recruiting

Clinical Spectrum and Outcome of Poisoning in Children Admitted to the Pediatric Emergency and Intensive Care Units at Sohag University Hospital

Acute Poisoning

Egypt
Alexion Pharmaceuticals, Inc.

Not yet recruiting

Study of Danicopan as Add-on Treatment to Ravulizumab or Eculizumab in Pediatric Participants With PNH Who Have Clinically Significant Extravascular Hemolysis

Paroxysmal Nocturnal Hemoglobinuria | PNH | Extravascular Hemolysis
Case Comprehensive Cancer Center
AbbVie; Genmab; Recordati Rare Diseases

Not yet recruiting

Study of Cytokine Release Syndrome Prophylaxis and Treatment With Siltuximab Prior to Epcoritamab

Non-Hodgkin Lymphoma | Cytokine Release Syndrome

United States
Jonsson Comprehensive Cancer Center

Not yet recruiting

PH Weighted Chemical Exchange Saturation Transfer MRI-Based Surgical Resection to Improve Survival in Patients With Glioblastoma

Glioblastoma

United States
Assiut University

Not yet recruiting

Minerals Status in Relation to Overweight and Obese Adolescent

Mineral Deficiency

Egypt
Harbin Medical University
Shanghai Shenqi Medical Technology Co., Ltd

Not yet recruiting

RESTORE Imaging: an OCT-IVUS Imaging Substudy of RESTORE Trial

Acute Coronary Syndrome (ACS)

China
Fudan University

Not yet recruiting

Perioperative Surufatinib Plus Sintilimab Combined With Chemotherapy in Gastric/Gastroesophageal Junction Adenocarcinoma

Gastric Cancer | Gastro Esophageal Junction Cancer

China
Pfizer

Not yet recruiting

A Study to Learn About the Study Medicine PF-07934040 When Given Alone or With Other Anti-cancer Therapies in People With Advanced Solid Tumors That Have a Genetic Mutation.

Carcinoma, Non-Small-Cell Lung | Colorectal Neoplasms | Carcinoma, Pancreatic Ductal
Affiliated Hospital of Jiangnan University

Not yet recruiting

An Exploratory Study of Deep Cervical Lymphovenous Bypass (LVB) in Alzheimer's Disease

Alzheimer Disease
Norwegian University of Science and Technology

Not yet recruiting

Multimodal Assesment of Alzheimer Patients (MultiAD)

Cognitive Impairment | Dementia | Mild Cognitive Impairment | Alzheimer Disease, Late Onset
City of Hope Medical Center
National Cancer Institute (NCI)

Recruiting

Humanized CD19-Specific CAR T Cells for the Treatment of Patients With Positive Relapsed or Refractory CD19 Positive B-Cell Acute Lymphoblastic Leukemia

Recurrent Acute Lymphoblastic Leukemia | Refractory Acute Lymphoblastic Leukemia

United States
Shanghai Zhongshan Hospital

Not yet recruiting

Combining Chemoradiotherapy With Sintilimab in First-Line ICC

ICC

China
Cairo University

Not yet recruiting

Assessment of Green Dentistry Knowledge, Attitude and Implementation and Its Association With Sociodemographic Factors Among Dental Professionals in Cairo University.

Green Dentistry
BioNTech SE

Not yet recruiting

Safety, Preliminary Effectiveness of BNT327, an Investigational Therapy for Patients With Small-cell Lung Cancer in Combination With Chemotherapy

Small-cell Lung Cancer | Extensive-stage Small-cell Lung Cancer
Laval University
Institut universitaire de cardiologie et de pneumologie de Québec, University... and other collaborators

Recruiting

Assessing Functional Capacity in Directly and Remotely Monitored Home-based Settings: A Protocol for a Multinational Validation Study in Individuals With Chronic Respiratory Diseases (6MST)

Interstitial Lung Disease | COPD Chronic Obstructive Pulmonary Disease

Canada, France
Memorial Sloan Kettering Cancer Center
NeuroEndocrine Tumor Research Foundation (NETRF)

Recruiting

Defining Response Criteria for PET Scans for People With Neuroendocrine Tumors

Neuroendocrine Tumors

United States
Shanghai Jiaolian Drug Research and Development...
Shanghai Pharmaceuticals Holding Co., Ltd

Not yet recruiting

A Clinical Study to Evaluate Safety, Tolerability and Pharmacokinetics of SV001 in Chinese Healthy Adult Volunteers.

Generalized Myasthenia Gravis

China
Second Affiliated Hospital, School of Medicine,...

Not yet recruiting

A Pilot Study of Deep Cervical Lymphatic-venous Anastomosis in the Treatment of Alzheimer's Disease

Feasibility | Safety Issues | Therapeutic Value
M.D. Anderson Cancer Center
Kura Oncology, Inc.

Not yet recruiting

A Phase I Study Investigating the Combination of the Menin Inhibitor Ziftomenib With Venetoclax and Gemtuzumab in Pediatric Patients With Acute Myeloid Leukemia

Acute Myeloid Leukemia

United States
Post Graduate Institute of Medical Education and...

Recruiting

A Trial to Compare Nebulized Amphotericin B and Nebulized Normal Saline as Maintenance in Patients With Chronic Pulmonary Aspergillosis (NAB-CPA)

Chronic Pulmonary Aspergillosis | Aspergilloma | CPA

India
University of Central Florida
University of South Florida

Not yet recruiting

Gut Microbiomes in HD

Huntington Disease

United States
Centre Integre Universitaire de Sante et Services...

Not yet recruiting

Cannabidiol After Multi-Trauma for Pain and Opioid Therapy (CAM-POT)

Fracture
Assistance Publique - Hôpitaux de Paris

Not yet recruiting

Preventing Iatrogenic Dependence Linked to Hospitalisation in Elderly Patients Hospitalised in Acute Geriatrics (TAKE CARE)

an Acute Pathology
D. Bradley Welling, MD, PhD
Nobelpharma

Not yet recruiting

In-office Repair of Chronic Tympanic Membrane Perforations

Chronic Tympanic Membrane Perforation

United States
Shanghai Zhongshan Hospital

Recruiting

Effects of Growth Hormone Therapy on Metabolic Function in Fatty Liver Post-Pituitary Adenoma Surgery

Growth Hormone Treatment

China
Fujian Shengdi Pharmaceutical Co., Ltd.

Not yet recruiting

Safety, Tolerability, and Preliminary Efficacy of HRS-7450 Injection in the Treatment of Acute Ischemic Stroke: a Multi-center, Randomized, Double-blind, Double-dummy, Placebo-controlled Clinical Trial

Acute Ischemic Stroke

China
University of Milan
Kolfarma s.r.l. - Italy; Fondazione Telethon

Recruiting

Targeting the Gut to Improve Seizure Control in CDKL5 Deficiency Disorder (CDD) (NUTRIENT)

CDKL5

Italy
Fondazione Policlinico Universitario Agostino Gemelli...

Not yet recruiting

Evaluation of Respiratory Mechanics in Supine and PARK-bench Positions (SPARK) (SPARK)

Ventilator-Induced Lung Injury | Ventilation Therapy; Complications

Italy
Xuanwu Hospital, Beijing

Not yet recruiting

Efficacy and Safety Evaluation of Hyperthermic Baths in the Treatment of Seizures in Children With CDKL5 Deficiency

CDKL5 Deficiency Disorder

China
Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...

Recruiting

Ultrasound to Assess Sarcopenia in Prader Willi Syndrome (PWS)

Metabolic Syndrome | Sarcopenia | Prader-Willi Syndrome

Taiwan
Karolinska Institutet

Not yet recruiting

Early Double Sequential Defibrillation in Out-of-hospital Cardiac Arrest (DOUBLE-D)

Cardiac Arrest | Sudden Cardiac Death | Sudden Cardiac Arrest | Fibrillation, Ventricular
University Hospital, Montpellier

Not yet recruiting

Identification and Characterization of Circulating Tumor Cells Before and After Treatment (Surgery and Radiotherapy) in a Cohort of Patients Treated for Resectable Stage I-III Merkel Cell Carcinoma (MERCCALIBI)

Merkel Cell Carcinoma
Sohag University

Recruiting

Short Term Outcome of Acute Heart Failure in Diabetic and Non Diabetic Patients

Diabetes Mellitus | Acute Heart Failure

Egypt
Shanghai Zhongshan Hospital

Not yet recruiting

Efficacy and Safety of Oxycodone Hydrochloride for Long-term Analgesia in ICU Patients

Analgesia | Mechanical Ventilation | Remifentanil | Postoperative | Oxycodone

China
Postgraduate Institute of Dental Sciences Rohtak

Recruiting

Effects of RCT on Periapical Healing, Inflammatory Markers, and Kidney Function Indicators in CKD Patients With AP

Chronic Kidney Diseases | Apical Periodontitis

India

Search clinical trials for: Rare Neurogenetic Conditions

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