- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Inherited Retinal Disorders
Total 149442 results
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University of SydneyNational Health and Medical Research Council, Australia; Mylan Pharmaceuticals... and other collaboratorsRecruitingDiabetic Retinopathy | Diabetic Nephropathies | Type 1 Diabetes MellitusAustralia, Hong Kong, New Zealand, United Kingdom
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Charite University, Berlin, GermanyRecruiting
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National Human Genome Research Institute (NHGRI)RecruitingCongenital Anomaly | Rare Disorders | Intellectual DisabilitiesUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingSoft Tissue Sarcoma | Lymphoma | Acute Myeloid Leukemia | Leukemia | Osteosarcoma | Acute Lymphoblastic Leukemia | Ewing Sarcoma | Rhabdoid Tumor | Neuroblastoma | Retinoblastoma | Rhabdomyosarcoma | Malignant Neoplasm | Germ Cell Tumor | Central Nervous System NeoplasmUnited States, Canada
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Washington University School of MedicineNational Institute on Aging (NIA)RecruitingAlzheimer's DiseaseUnited States, Argentina, Australia, Brazil, Canada, Colombia, Germany, Japan, Korea, Republic of, Mexico, United Kingdom, Spain
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); St. Jude Children's Research HospitalRecruitingRetinoblastomaUnited States
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University of California, San FranciscoUniversity of California, BerkeleyRecruiting
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Andrea GropmanEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingBrain Diseases, Metabolic, Inborn | Amino Acid Metabolism, Inborn Errors | Urea Cycle DisordersUnited States, Canada, Germany, Switzerland
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Rockefeller UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingGlanzmann ThrombastheniaUnited States
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The University of Texas Health Science Center,...RecruitingBlood Coagulation Disorders, Inherited | Thrombotic DisorderUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Severe Combined Immune Deficiency (XSCID) | Leukocyte Adhesion Deficiency 1 (LAD) | Graft Versus Host Disease (cGvHD)United States
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Feinstein Institute for Medical ResearchDiamond Blackfan Anemia Foundation, Inc.Recruiting
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National Human Genome Research Institute (NHGRI)RecruitingPulmonary Fibrosis | Healthy Volunteers | Hermansky-Pudlak Syndrome (HPS)United States
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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National Institute of Neurological Disorders and...Recruiting
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Muscular Dystrophy | Peripheral Nervous System Disease | Muscular DiseaseUnited States, Mali
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National Human Genome Research Institute (NHGRI)Merck Sharp & Dohme LLC; Duke University; University of Massachusetts, WorcesterRecruitingFever | Genetic Diseases | Familial Mediterranean Fever (FMF) | Autoinflammation | Periodic Fever | ROSAH | ALPK1United States
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National Cancer Institute (NCI)RecruitingKidney Cancer | Renal Cell Carcinoma | Urologic Malignant Disorders | Familial Renal Cancer (FRC) | Clear Cell Renal CancerUnited States
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National Human Genome Research Institute (NHGRI)RecruitingHermansky-Pudlak Syndrome (HPS)United States
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Regeneron PharmaceuticalsBayerActive, not recruitingType 2 Diabetes Mellitus | Diabetic Macular Edema | Type 1 Diabetes MellitusUnited States, Puerto Rico, Japan, United Kingdom, Canada, Czechia, Germany, Hungary
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David WilliamsActive, not recruitingWiskott-Aldrich SyndromeUnited States
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PfizerActive, not recruiting
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompletedHemophilia ACzechia, Switzerland, Denmark, Canada, Australia, Austria, France, United Kingdom, Italy, Sweden, Belgium, Brazil, China, Colombia, Greece, Hungary, Norway, Poland, Portugal, Russian Federation, Slovenia, Spain
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Hoffmann-La RocheActive, not recruitingSevere Hemophilia ACanada, United States, United Kingdom, Belgium, Australia, Austria, Brazil, France, Germany, Israel, Italy, South Africa, Spain, Turkey
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National Human Genome Research Institute (NHGRI)CompletedUndiagnosed Disease | Healthy Volunteer (Adult With Typically Developing Child) | Inherited Neurodegenerative Disorders | Inherited Metabolic Disorders (Inborn Errors of Metabolism) | Alzheimer's Disease and Related DementiasUnited States
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Mayo ClinicAstellas Pharma Inc; Casimir, LLCCompletedMitochondrial Diseases | Mitochondrial Myopathies | Kearns-Sayre Syndrome | Mitochondrial DNA Mutation | Chronic Progressive External Ophthalmoplegia With MyopathyUnited States
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BayerActive, not recruitingHemophilia ACanada, Japan, Spain, United States, Germany, Sweden, Belgium, Brazil, Greece, Italy, Netherlands, Taiwan, Denmark, Kuwait, Saudi Arabia, United Arab Emirates, Norway, Colombia, Switzerland, Slovenia
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BayerActive, not recruitingHemophilia A | Children | Prophylaxis of Bleeding | Treatment of BleedingCanada, United States, Brazil, Italy, Turkey, Argentina, Norway
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Bioverativ, a Sanofi companyActive, not recruitingHemophilia AUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, China, France, Germany, Greece, Hungary, Ireland, Italy, Japan, Korea, Republic of, Netherlands, Spain, Sweden, Switzerland, Taiwan, Turkey, United Kingdom
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Washington University School of MedicineHoffmann-La Roche; Genentech, Inc.; National Institute on Aging (NIA); Alzheimer...SuspendedDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, Canada, Italy, France, Spain, Ireland, Argentina, Australia, Colombia, Germany, Mexico, Netherlands, Puerto Rico, United Kingdom
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OctapharmaActive, not recruitingVon Willebrand DiseaseUnited States, Moldova, Republic of, Czechia, Germany, North Macedonia, Russian Federation, Ukraine
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Novo Nordisk A/SActive, not recruitingHaemophilia A Without Inhibitors | Haemophilia B Without InhibitorsSpain, United States, Korea, Republic of, United Kingdom, Australia, Lithuania, France, Turkey, India, Estonia, Russian Federation, Ukraine, Mexico, Japan, Serbia, Canada, Croatia, Algeria, Bosnia and Herzegovina, Bulgaria, Denmark and more
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Novo Nordisk A/SActive, not recruitingHaemophilia A With Inhibitors | Haemophilia ASpain, Korea, Republic of, Canada, United Kingdom, United States, Germany, South Africa, Italy, Austria, Belgium, France, Japan
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University of FloridaActive, not recruitingRenal Failure | Protein-Energy MalnutritionUnited States
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Assistance Publique - Hôpitaux de ParisDélégation de la Recherche Clinique et de l'innovation (DRCI); CRC (Centre... and other collaboratorsCompletedDiabetes | Diabetic Retinopathy | Microangiopathy | Angiography | Microvascular ComplicationsFrance
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Novo Nordisk A/SAvailableCongenital HaemophiliaUnited States, Bulgaria, Sweden
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Kodiak Sciences IncCompletedMacular Edema | Retinal Vein OcclusionSpain, United States, Latvia, Israel, France, Italy, Hungary, Germany, Poland, Slovakia, Puerto Rico, Czechia
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BayerUltragenix pharmaceuticalActive, not recruitingHemophilia ANetherlands, United States, Germany, United Kingdom, France, Bulgaria
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BBulgaria, United States, United Kingdom, Russian Federation, Switzerland
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Cyclo Therapeutics, Inc.Active, not recruitingNiemann-Pick Disease, Type C1United States, Taiwan, United Kingdom, Israel, Spain, Brazil, Italy, Australia, Turkey, Saudi Arabia, Argentina, Poland, Germany
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Hoffmann-La RocheActive, not recruitingHemophilia A | Mild Hereditary Factor VIII Deficiency Disease Without Inhibitor | Moderate Hereditary Factor VIII Deficiency Disease Without InhibitorUnited States, Netherlands, Belgium, France, Germany, South Africa, Spain, Canada, United Kingdom, Poland
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Asociación para Evitar la Ceguera en MéxicoWithdrawnDiabetic Macular Edema | Diabetes Mellitus Type 2Mexico
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Asociación para Evitar la Ceguera en MéxicoInstituto Nacional de Referencia Epidemiológica (INdRE)WithdrawnHLA and it Relation With the Development of Proliferative Diabetic Retinopathy in Mexican PopulationProliferative Diabetic Retinopathy | Diabetes Mellitus Type 2Mexico
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BayerActive, not recruiting
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Asociación para Evitar la Ceguera en MéxicoWithdrawn
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St. Jude Children's Research HospitalChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingHemophilia BUnited States, United Kingdom
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Universiteit AntwerpenUniversity Hospital, Antwerp; Cliniques universitaires Saint-Luc- Université...CompletedHemophilia A | Hemophilia BBelgium
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CSL BehringEnrolling by invitation
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Asociación para Evitar la Ceguera en MéxicoTerminatedRetinal DetachmentMexico