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Search clinical trials for: Natural history study
Total 122272 results
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Boston Children's HospitalAgios Pharmaceuticals, Inc.CompletedPyruvate Kinase Deficiency | Congenital Non-Spherocytic Hemolytic AnemiaUnited States, Germany, Canada, Czechia, Italy, Netherlands
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University of California, San FranciscoCompletedLupus Erythematosus, SystemicUnited States
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National Cancer Institute (NCI)WithdrawnHepatocellular Carcinoma | Hepatocellular CancerUnited States
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National Cancer Institute (NCI)Terminated
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Enzyvant Therapeutics GmBHCompletedFarber Disease | Farber's Disease | Farber Lipogranulomatosis | Acid Ceramidase Deficiency | Ceramidase Deficiency | N-Laurylsphingosine Deacylase Deficiency | ASAH1 MutationUnited States, Egypt, Canada, Italy, Turkey, Argentina, Germany, India, Sweden
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Janssen Research & Development, LLCTerminated
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National Cancer Institute (NCI)Multicenter Hemophilia Cohort StudyCompletedHepatocellular Carcinoma | Non-Hodgkin Lymphoma | Liver DecompensationUnited States, Germany, Italy, Brazil, Canada, France, Greece, Sweden
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National Cancer Institute (NCI)Completed
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National Institute of Neurological Disorders and...Terminated
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National Cancer Institute (NCI)CompletedAdrenocortical CarcinomaUnited States
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National Eye Institute (NEI)CompletedGraft-Versus-Host DiseaseUnited States
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NYU Langone HealthUniversitätsklinikum Hamburg-EppendorfCompleted
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Yonsei UniversityUnknown
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MED-LIFE DISCOVERIES LPUnknown
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Genzyme, a Sanofi CompanyCompletedAlport Syndrome Patients With eGFR Between 45-90 ml/Min/1.73 m2France, Germany, Australia, United States, United Kingdom, Canada
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Dermelix Biotherapeutics, LLC.Withdrawn
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Imperial College LondonUniversity of Oxford; Clinical Trial Service Unit and Epidemiological Studies...CompletedCardiovascular Diseases | Stroke | TIA | Heart AttackUnited Kingdom
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VA Office of Research and DevelopmentCompleted
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Taiwan, United Kingdom, Australia, Canada, Germany, Spain
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency | Isolated Sulfite Oxidase DeficiencySpain, Israel, United States, United Kingdom, Canada, Netherlands, Germany, Saudi Arabia, Tunisia, Japan, Italy, Malaysia, Poland, Turkey
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Korea University Guro HospitalCompleted
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Fondazione TelethonUnknownUsher Syndrome, Type 1BItaly, Netherlands, Spain
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BayerCompletedVenous ThromboembolismTaiwan
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X4 PharmaceuticalsWithdrawn
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Alexion PharmaceuticalsTerminatedMPS IIIB (Sanfilippo B Syndrome)Spain, United States, Brazil, United Kingdom, Portugal, Italy
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Institut de Myologie, FranceInstitut RocheCompletedType 2 Spinal Muscular Atrophy | Type 3 Spinal Muscular AtrophyBelgium, France, Germany
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Cooperative International Neuromuscular Research...UnknownBecker Muscular DystrophyUnited States, Canada, Italy, United Kingdom
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Valerion Therapeutics, LLCInstitut de Myologie, France; GenethonCompletedMyotubular MyopathyFrance, Belgium, United States, Canada, Germany, Italy, Spain
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Ultragenyx Pharmaceutical IncNewcastle UniversityCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Nonaka Disease | Quadriceps Sparing Myopathy (QSM) | Distal Myopathy With Rimmed Vacuoles (DMRV)United States, Bulgaria, Canada, France, United Kingdom
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Zymenex A/SCompletedInfantile Globoid Cell LeukodystrophyUnited States
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Cure CMDUniversity of Michigan; Congenital Muscle Disease International RegistrCompleted
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Institute of Liver and Biliary Sciences, IndiaTerminatedAcute on Chronic Liver FailureIndia
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European Organisation for Research and Treatment...CompletedCancerBelgium, Switzerland, Italy, France, Germany
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey
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BayerCompleted
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Chinese University of Hong KongCompleted
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National Cancer Institute (NCI)CompletedMelanocytic Nevi | Acquired Melanocytic Nevi | Primary Cutaneous MelanomaUnited States
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National Institute of Neurological Disorders and...National Institute of Neurological Disorders and Stroke@@@Shire Human Genetic...Completed
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GlaxoSmithKlineTerminated
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Liu ZhiyongXuanwu Hospital, BeijingUnknownIschemic Heart Disease | Intracranial Aneurysm | Ischemic Cerebrovascular Disease | Natural History
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University Hospital, BonnGenentech, Inc.CompletedEye Diseases | Age-related Macular Degeneration | Geographic Atrophy | AtrophyGermany
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Children's Hospital Medical Center, CincinnatiMassachusetts General Hospital; The University of Texas Health Science Center... and other collaboratorsCompletedTuberous Sclerosis ComplexUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedPrecancerous Condition | Adrenocortical Carcinoma | Localized Resectable NeuroblastomaUnited States, Canada, Australia
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Columbia UniversityUniversity of North Carolina, Chapel HillTerminated
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The Cleveland ClinicCompleted
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Dana-Farber Cancer InstituteNational Cancer Institute (NCI)Completed
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Alcon ResearchCompletedOcular Hypertension | Open-angle Glaucoma
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RenJi HospitalUnknownTreatment Side Effects | Intracranial Aneurysm | Unruptured Cerebral Aneurysm
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Bastyr UniversityCompleted