- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Thalassemia intermedia
Total 1536 results
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Karyopharm Therapeutics IncActive, not recruitingAcute Myeloid Leukemia (AML) | Metastatic Colorectal Cancer (mCRC) | Metastatic Castration-Resistant Prostate Cancer (mCRPC) | Relapsed/Refractory Multiple Myeloma (RRMM) | Higher-Risk Myelodysplastic Syndrome (HR-MDS) | Newly Diagnosed Intermediate/High-Risk MDSUnited States, France, Canada, Spain, China
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University of ChicagoActive, not recruitingProstate CancerUnited States
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Clene NanomedicineAvailableAmyotrophic Lateral SclerosisUnited States
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Clene NanomedicineNational Institute of Neurological Disorders and Stroke (NINDS)AvailableAmyotrophic Lateral Sclerosis | ALS | PALS
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Fudan UniversityCompletedHepatocellular CarcinomaChina
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Clene NanomedicineMassachusetts General HospitalAvailable
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
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National Cancer Institute (NCI)Active, not recruitingCarcinoid Tumor | Functioning Pancreatic Neuroendocrine Tumor | Intermediate Grade Lung Neuroendocrine Neoplasm | Locally Advanced Pancreatic Neuroendocrine Tumor | Locally Advanced Unresectable Digestive System Neuroendocrine Neoplasm | Low Grade Lung Neuroendocrine Neoplasm | Metastatic Digestive... and other conditionsUnited States
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University of ChicagoJanssen, LPSuspendedProstate CancerUnited States
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National Cancer Institute (NCI)NRG OncologyActive, not recruitingEndometrial Endometrioid Adenocarcinoma | Stage I Uterine Corpus Cancer AJCC v8 | Stage II Uterine Corpus Cancer AJCC v8United States, Puerto Rico
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WestatEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Pediatric CancerUnited States, Brazil
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National Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationSickle Cell Anemia | Sickle Beta Thalassemia | Sickle Cell Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Pain | Hbss | Hbsc | Sickle Cell Syndrome VariantUnited States
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University of LeipzigCuris, Inc.TerminatedMyelodysplastic Syndromes | AnemiaGermany
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Memorial Sloan Kettering Cancer CenterActive, not recruitingProstate CancerUnited States
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Agios Pharmaceuticals, Inc.Active, not recruitingThalassemiaUnited States, Canada, United Kingdom
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Agios Pharmaceuticals, Inc.Active, not recruitingNon-Transfusion-dependent Alpha-Thalassemia | Non-Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United Kingdom, Malaysia, United States, Netherlands, Bulgaria, Turkey, Italy, Canada, Brazil, France, United Arab Emirates, Denmark, Greece, Lebanon, Saudi Arabia
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Istanbul Medipol University HospitalCompletedPregnancy Complications | ChronotypeTurkey
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Agios Pharmaceuticals, Inc.Active, not recruitingTransfusion-dependent Alpha-Thalassemia | Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United States, France, Canada, Malaysia, Germany, Netherlands, Bulgaria, United Kingdom, Turkey, Italy, Greece, United Arab Emirates, Brazil, Denmark, Lebanon, Saudi Arabia
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedChronic Myelomonocytic Leukemia | Myelodysplastic Syndrome | High Risk Myelodysplastic Syndrome | Acute Myeloid Leukemia With Multilineage Dysplasia | Blasts 20-30 Percent of Bone Marrow Nucleated Cells | Blasts 20-30 Percent of Peripheral Blood White Cells | IPSS Risk Category Intermediate-2United States
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ChimerixAvailableGlioma | H3 K27MUnited States
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, United Kingdom, Canada, Germany, Italy
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Geron CorporationActive, not recruitingMyelodysplastic SyndromesUnited States, Canada, Belgium, Spain, Czechia, Korea, Republic of, United Kingdom, Netherlands, Israel, Germany, Russian Federation, Switzerland, Italy, France, Turkey, Poland, Ukraine
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Bristol-Myers SquibbActive, not recruitingMyelodysplastic SyndromesArgentina, Canada, France, Germany, Italy, Korea, Republic of, Poland, United States, Australia, China, Czechia, Denmark, Greece, Hong Kong, Japan, Spain, Sweden
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University of BirminghamAstraZeneca; Cancer Trials IrelandActive, not recruitingOropharyngeal CancerUnited Kingdom, Ireland
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityActive, not recruiting
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Moscow City Oncology Hospital No. 62CompletedEndometrial Neoplasms | Endometrial Cancer | Sentinel Lymph Node | Endometrial Endometrioid Adenocarcinoma | Endometrial Adenocarcinoma | Hysterectomy | Endometrial Cancer Stage I | Laparoscopic Hysterectomy | Endometrial Cancer Stage IIRussian Federation
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityEnrolling by invitation
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AstraZenecaDaiichi Sankyo Co., Ltd.CompletedGastric or Gastroesophageal Junction (GEJ) AdenocarcinomaChina
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Astex Pharmaceuticals, Inc.TerminatedMyelodysplastic SyndromesUnited States
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Novartis PharmaceuticalsActive, not recruitingMyelodysplastic Syndromes | Leukemia, Myelomonocytic, ChronicChina, Czechia, Japan, Saudi Arabia, Taiwan, Turkey, Germany, Spain, Netherlands, Italy, Singapore, Australia, Austria, France, United Kingdom, Korea, Republic of, Thailand, Israel, Belgium, Canada, Switzerland, Lithuania, Russian Federation and more
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availablePost COVID-19 SyndromeUnited States
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Novartis PharmaceuticalsActive, not recruitingMyelodysplastic SyndromesCzechia, Hungary, Japan, Taiwan, United States, Belgium, Italy, United Kingdom, Korea, Republic of, Hong Kong, Austria, Germany, Turkey, Spain, Greece, France, Canada
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Medtronic CardiovascularActive, not recruitingSevere Aortic StenosisUnited States, Netherlands, Canada, Spain, Denmark, United Kingdom, Switzerland, Germany, Sweden
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Klein Buendel, Inc.National Institute on Minority Health and Health Disparities (NIMHD); Hilton...CompletedSickle Cell Disease | Sickle Cell Anemia in Children | Sickle Cell Thalassemia | Sickle Cell SC DiseaseUnited States
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CelgeneCompletedLeukemia, Myeloid | Isocitrate DehydrogenaseUnited States, Canada, China, Czechia, France, Germany, Italy, United Kingdom, Australia, Austria, Brazil, Denmark, Korea, Republic of, Russian Federation, Spain, Taiwan, Turkey, Belgium
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Universitätsklinikum Hamburg-EppendorfDeutsches Zentrum für Herz-Kreislauf-Forschung (DZHK); Deutsche Herzstiftung...Active, not recruiting
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University of WashingtonGenentech, Inc.SuspendedPrimary Mediastinal (Thymic) Large B-Cell Lymphoma | Aggressive Non-Hodgkin Lymphoma | Diffuse Large B-Cell Lymphoma, Not Otherwise Specified | EBV-Positive Diffuse Large B-Cell Lymphoma, Not Otherwise Specified | High Grade B-Cell Lymphoma, Not Otherwise Specified | T-Cell/Histiocyte-Rich... and other conditionsUnited States
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Seelos Therapeutics, Inc.Massachusetts General Hospital; National Institute of Neurological Disorders... and other collaboratorsNo longer available
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National Cancer Institute (NCI)Active, not recruitingRhabdomyosarcoma | Alveolar Rhabdomyosarcoma | Embryonal Rhabdomyosarcoma | Botryoid-Type Embryonal Rhabdomyosarcoma | Sclerosing Rhabdomyosarcoma | Spindle Cell RhabdomyosarcomaUnited States, Canada, Puerto Rico, Australia, New Zealand
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Sports Surgery Clinic, Santry, DublinCompletedConcussion, Mild | Concussion, Severe | Concussion, IntermediateIreland
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingDyspnea | Malignant NeoplasmUnited States
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Timothy OlsonActive, not recruitingSickle Cell Disease | Thalassemia MajorUnited States
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Emory UniversityBristol-Myers Squibb; Thrasher Research Fund; Sickle Cell Transplant Advocacy... and other collaboratorsActive, not recruitingGraft Versus Host DiseaseUnited States
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CelgeneTerminatedNeoplasms | Lymphoma, Non-HodgkinFrance, Italy, Japan, Spain, United Kingdom
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Sanguine BiosciencesCompletedDepression | Melanoma | Epilepsy | Lymphoma | Multiple Sclerosis | Kidney Cancer | Cervical Cancer | Diabetes Mellitus | Leukemia | Breast Cancer | Chronic Kidney Diseases | Chronic Obstructive Pulmonary Disease | Parkinson's Disease | Systemic Lupus Erythematosus | Multiple Myeloma | Hepatitis B | Insomnia | Colorectal Cancer | HIV/AID... and other conditionsUnited States
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Shanghai Antengene Corporation LimitedTerminated
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PfizerActive, not recruitingSickle Cell DiseaseUnited States, Oman, United Kingdom, France, Egypt, Ghana, Italy, Kenya, Nigeria, Saudi Arabia
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Association for Innovation and Biomedical Research...European Vision Institute Clinical Research NetworkActive, not recruitingAtrophy | Age Related Macular Degeneration | Prediction | Intermediate AMDPortugal, France, Germany, Ireland, Italy, Netherlands, Spain, Switzerland, United Kingdom
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Chiesi Farmaceutici S.p.A.Active, not recruitingIdiopathic Pulmonary FibrosisNorth Macedonia, Ukraine, United Kingdom
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St. Jude Children's Research HospitalNational Cancer Institute (NCI); University of Florida; The Pew Charitable TrustsActive, not recruitingBrain and Central Nervous System TumorsUnited States, Australia