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Clinical Trials Sponsored by Orphan Medical
Total 56046 results
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OrphalanErgomedRecruitingWilson's DiseaseSpain, United Kingdom, Belgium, Germany, Poland, France, Saudi Arabia
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Swedish Orphan BiovitrumHarvard Medical School (HMS and HSDM); Brigham and Women's HospitalCompletedHemophagocytic LymphohistiocytosesUnited States
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Columbia UniversityFDA Office of Orphan Products DevelopmentRecruiting
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Assistance Publique - Hôpitaux de ParisSwedish Orphan BiovitrumRecruiting
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Memorial Sloan Kettering Cancer CenterSwedish Orphan BiovitrumActive, not recruitingLeukemia | Multiple Myeloma | Non-Hodgkin's Lymphoma | Myelodysplastic SyndromeUnited States
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Swedish Orphan BiovitrumLight Chain Bioscience - Novimmune SATerminatedHemophagocytic LymphohistiocytosesUnited States
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FDA Office of Orphan Products DevelopmentCentocor, Inc.Completed
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Emory UniversityCompletedGlioblastoma Multiforme | Anaplastic Astrocytoma | Anaplastic Oligodendroglioma | Recurrent Brain Tumor | Mixed Gliomas
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Mayo ClinicCompletedMyocarditisUnited States
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Cellegy PharmaceuticalsCompleted
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FDA Office of Orphan Products DevelopmentSciClone PharmaceuticalsCompleted
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United TherapeuticsCompletedPulmonary HypertensionUnited States
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Philipps University Marburg Medical CenterDeutsche Krebshilfe e.V., Bonn (Germany); AOP Orphan Pharmaceuticals AGCompletedChronic Myeloid Leukemia in RemissionFrance, Germany
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University of CincinnatiChildren's Hospital Medical Center, CincinnatiTerminatedAdrenoleukodystrophy | Zellweger Syndrome | Infantile Refsum's Disease | Bifunctional Enzyme Deficiency
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Boston Children's HospitalFDA Office of Orphan Products DevelopmentActive, not recruiting
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Jupiter Orphan Therapeutics Inc.National Institute on Aging (NIA)CompletedPharmacokinetics | Food-drug Interaction | SafetyUnited States
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Aegerion Pharmaceuticals, Inc.FDA Office of Orphan Products DevelopmentCompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, South Africa
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University of ChicagoCompleted
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University of FloridaCompleted
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National Jewish HealthCompletedMycobacterium Avium-intracellulare Infection
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Johns Hopkins UniversityCompletedCerebral HemorrhageUnited States
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University of MichiganCompletedGraft Versus Host DiseaseUnited States
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University of TexasTerminated
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University of TexasCompletedAcute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia
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University of PittsburghCompletedTrigeminal NeuralgiaUnited States
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Holles Laboratories, Inc.Completed
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University of VermontCompleted
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University of TexasCompletedEsophageal Achalasia
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AOP Orphan Pharmaceuticals AGPharmaEssentia Corporation (for the U.S.)CompletedPolycythemia VeraSpain, Austria, Bulgaria, France, Germany, Hungary, Poland, Romania, Russian Federation, Slovakia, Ukraine, Czechia
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NeuroHealing Pharmaceuticals Inc.FDA Office of Orphan Products DevelopmentSuspended
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AOP Orphan Pharmaceuticals AGPharmaEssentia (Co-Sponsor for USA)CompletedPolycythemia VeraSpain, Belgium, Austria, Italy, Bulgaria, Czech Republic, France, Germany, Hungary, Poland, Romania, Russian Federation, Slovakia, Ukraine
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University of PittsburghCompletedSezary Syndrome | Cutaneous T-cell LymphomaUnited States
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FDA Office of Orphan Products DevelopmentUniversity of UtahCompleted
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University of ChicagoCompleted
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University of IowaCompletedLymphatic MalformationsUnited States
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University of TexasCompleted
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The Cleveland ClinicCompleted
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FDA Office of Orphan Products DevelopmentBoston Children's HospitalCompleted
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University of TexasCompletedAcute Renal FailureUnited States
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University of PittsburghCompletedMycosis Fungoides | Sezary Syndrome | Cutaneous T-cell LymphomaUnited States
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University of WashingtonCompleted
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Johns Hopkins UniversityCompletedEpilepsy | Cysticercosis
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Bellus Health IncFDA Office of Orphan Products DevelopmentCompletedGastrointestinal Diseases | Kidney Diseases | Rheumatoid Arthritis | Nephrotic Syndrome | Secondary (AA) Amyloidosis | Familial Mediterranean SyndromeUnited States, Israel, Finland, France, Italy, Lithuania, Netherlands, Poland, Russian Federation, Spain, Turkey, United Kingdom
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Boston Children's HospitalFDA Office of Orphan Products DevelopmentTerminated
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Swedish Orphan BiovitrumPRA Health Sciences; BioMérieux; Cytel Inc.TerminatedGraft FailureItaly, Belgium, United Kingdom, France, Germany, Netherlands
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IWK Health CentreCompletedPertussis | Whooping Cough
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Ohio State UniversityCompletedMuscular Dystrophy, Facioscapulohumeral
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University of IowaCompleted
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FDA Office of Orphan Products DevelopmentLeadiant Biosciences, Inc.Completed
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Boston Children's HospitalCompletedSickle Cell AnemiaUnited States