- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials Sponsored by Orphan Medical
Total 56046 results
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The Cleveland ClinicTerminated
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University of FloridaCompleted
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University of MichiganCompleted
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Seattle Children's HospitalCompletedPain | Infant, Newborn, Diseases
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Massachusetts General HospitalCompleted
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University of PennsylvaniaTerminatedOrnithine Transcarbamylase Deficiency Disease
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University of TennesseeFDA Office of Orphan Products DevelopmentCompleted
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University of ArizonaFDA Office of Orphan Products DevelopmentTerminated
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Medical University of South CarolinaMerck Sharp & Dohme LLC; FDA Office of Orphan Products DevelopmentCompletedFractures | Juvenile Osteoporosis | Low Bone DensityUnited States
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Children's Hospital Los AngelesCompletedThrombosis | Heparin-induced ThrombocytopeniaUnited States
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University of North CarolinaCompleted
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FDA Office of Orphan Products DevelopmentChildren's Hospital of PhiladelphiaCompleted
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Brigham and Women's HospitalCompletedErythropoietic Protoporphyria
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FDA Office of Orphan Products DevelopmentCase Western Reserve UniversityCompleted
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Children's Hospital of PhiladelphiaMedical University of South Carolina; FDA Office of Orphan Products DevelopmentCompleted
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Medical University of South CarolinaMerck Sharp & Dohme LLC; FDA Office of Orphan Products DevelopmentCompletedOsteoporosisUnited States
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Lundquist Institute for Biomedical Innovation at...Swedish Orphan Biovitrum; Cure Sanfilippo FoundationCompleted
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Dr. David SpanerSwedish Orphan BiovitrumUnknownChronic Lymphocytic Leukemia
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FDA Office of Orphan Products DevelopmentUniversity of North CarolinaCompleted
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FDA Office of Orphan Products DevelopmentCase Western Reserve UniversityCompleted
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Children's Hospital of PhiladelphiaCompleted
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Children's Hospital of PhiladelphiaCompleted
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Hanny Al-Samkari, MDSwedish Orphan BiovitrumRecruitingGastrointestinal Neoplasms | Gastrointestinal Cancer | Chemotherapy-Induced ThrombocytopeniaUnited States
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Fondazione per la Ricerca Ospedale MaggioreAOP Orphan Pharmaceuticals AGCompleted
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Swedish Orphan BiovitrumKantar Health; Cerner Enviza (former Kantar Health)CompletedHemophilia A | Hemophilia BFrance
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Bioverativ Therapeutics Inc.Swedish Orphan Biovitrum; Syntonix Pharmaceuticals, Inc.Completed
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AOP Orphan Pharmaceuticals AGPharmaEssentia Corporation (Co-Sponsor for USA)CompletedPolycythemia VeraAustria, Bulgaria, Czech Republic, France, Hungary, Poland, Slovakia, Ukraine
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Case Western Reserve UniversityTerminated
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University of North CarolinaCompletedSickle Cell AnemiaUnited States
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FDA Office of Orphan Products DevelopmentUniversity of Massachusetts, WorcesterCompletedJuvenile Rheumatoid Arthritis
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M.D. Anderson Cancer CenterCompletedLymphoproliferative Disorders | Leukemia | Hematologic Neoplasms | Leukemia, Lymphocytic, ChronicUnited States
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University of North CarolinaCompletedOsteoporosis | Cystic FibrosisUnited States
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George BrewerFDA Office of Orphan Products DevelopmentCompletedPrimary Biliary CirrhosisUnited States
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FDA Office of Orphan Products DevelopmentUniversity of Illinois at ChicagoCompleted
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University of California, San DiegoCompletedLactic AcidosisUnited States
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Memorial Hospital of Rhode IslandCompleted
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UCSF Benioff Children's Hospital OaklandCompletedPneumonia | Anemia, Sickle CellUnited States
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Retina Foundation of the SouthwestCompleted
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California Department of Health ServicesCompletedBotulism | Infant BotulismUnited States
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FDA Office of Orphan Products DevelopmentSt. Luke's-Roosevelt Hospital CenterCompletedErythropoietic Protoporphyria
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PTC TherapeuticsCystic Fibrosis Foundation; FDA Office of Orphan Products DevelopmentCompleted
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Orhan ÜreyenCompletedAppendicitis, Surgery
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Johns Hopkins UniversityGenentech, Inc.; FDA Office of Orphan Products DevelopmentCompletedIntraventricular HemorrhageUnited States, Germany, Canada, United Kingdom
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University of California, San FranciscoFDA Office of Orphan Products DevelopmentCompleted
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University of California, San FranciscoFDA Office of Orphan Products DevelopmentTerminatedPersistent Corneal Epithelial Defects
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State University of New YorkCompletedDupuytren's Contracture
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FDA Office of Orphan Products DevelopmentChildren's Hospital and Health CenterCompletedHeart Defects, Congenital | Tricuspid Atresia
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State University of New YorkCompletedDupuytren's ContractureUnited States
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Merit CudkowiczFDA Office of Orphan Products DevelopmentCompleted
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Organ, Tissue, Regeneration, Repair and ReplacementEuraxi Pharma; ARANZ MedicalRecruitingEpidermolysis Bullosa Dystrophica | Epidermolysis Bullosa, JunctionalFrance