- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Compassionate Use
Total 20963 results
-
Regeneron PharmaceuticalsAvailableCD55-Deficient Protein-Losing Enteropathy
-
UCB Biopharma SRLAvailable
-
Amicus TherapeuticsAvailablePompe Disease Infantile-OnsetTaiwan, United States, Italy
-
Amicus TherapeuticsAvailable
-
Regeneron PharmaceuticalsAvailableDiffuse Large B-Cell Lymphoma (DLBCL) | Relapsed or Refractory (R/R) Follicular Lymphoma (FL) | B-Cell Non-Hodgkin Lymphoma (NHL) | High-Grade B-Cell Lymphoma (HGBCL)
-
Regeneron PharmaceuticalsAvailable
-
Regeneron PharmaceuticalsAvailable
-
University of MiamiTemporarily not availablePseudoaneurysm, Carotid | PseudoaneurysmUnited States
-
Rhizen Pharmaceuticals SACompletedHematological MalignanciesUnited States, Georgia, Poland
-
Kieuhoa VoCannonball Kids Cancer Foundation, IncAvailableNeuroblastomaUnited States
-
JC Medical, Inc.AvailableAortic Valve Stenosis | Aortic Valve Disease | Aortic Valve Insufficiency
-
Northwell HealthCohen Children's Medical CenterAvailableNeuroblastoma | PheochromocytomaUnited States
-
Amylyx Pharmaceuticals Inc.CompletedAmyotrophic Lateral SclerosisUnited States
-
Fundación GECPCompletedMetastatic Non Small Cell Lung CancerSpain
-
Joseph JankovicNo longer availableHyperkinetic Movement Disorders
-
Dolores Herreros MarcosCompleted
-
Intergroupe Francophone de Cancerologie ThoraciqueNovartisCompletedNon Small Cell Lung Cancer | MET Alterations | METex14 MutationsFrance
-
Advenchen Laboratories, LLCAvailableGynecologic Cancer | Sarcoma,Soft Tissue
-
Chiesi Canada CorpNo longer availablePantothenate Kinase-Associated Neurodegeneration
-
Gruppo Italiano Malattie EMatologiche dell'AdultoTerminatedChronic Myeloid Leukemia | Philadelphia PositiveItaly
-
Ferrer Internacional S.A.AvailablePulmonary Hypertension | Interstitial Lung Disease | Combined Pulmonary Fibrosis and Emphysema
-
Merck Sharp & Dohme LLCNo longer availableLymphoma, T-Cell, Cutaneous
-
SanofiApproved for marketing
-
Montefiore Medical CenterNo longer availableCongenital HyperinsulinismUnited States
-
Talaris Therapeutics Inc.Northwestern UniversityNo longer availableRenal FailureUnited States
-
Talaris Therapeutics Inc.Duke UniversityNo longer availableMetachromatic LeukodystrophyUnited States
-
AbbVieNo longer availableCrohn's Disease | Ulcerative Colitis (UC)
-
AbbVieNo longer availableHigh Grade Serous Ovarian Cancer | Solid Tumors With Documented BRCA, BARD, or PALB or Other Acceptable DNA Mutations or Anomalies That Are Scientifically Sound | Triple Negative Breast Cancer (TNBC) | Patients Requiring Veliparib Suspension Formulation
-
Cara Therapeutics, Inc.Approved for marketing
-
Genexine, Inc.No longer availableMelanoma | Glioblastoma | High Grade Glioma | Recurrent Glioblastoma | Advanced CancerKorea, Republic of
-
RedHill Biopharma LimitedAvailableCholangiocarcinoma | Cholangiocarcinoma Non-resectable | Cholangiocarcinoma, Perihilar | Cholangiocarcinoma, Extrahepatic | Cholangiocarcinoma, Intrahepatic
-
Centre Hospitalier le MansCompleted
-
CytoDyn, Inc.No longer availableMetastatic Triple-Negative Breast Carcinoma
-
Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
-
UNC Lineberger Comprehensive Cancer CenterBellicum PharmaceuticalsNo longer availableImmune System Diseases | Immunoproliferative Disorders | Acute Lymphoblastic LeukemiaUnited States
-
UNC Lineberger Comprehensive Cancer CenterNo longer available
-
Bristol-Myers SquibbNo longer availableRenal TransplantationUnited States
-
Medtronic CardiovascularNo longer availableAbdominal Aortic AneurysmsUnited States
-
TRPHARMFennec PharmaAvailableCisplatin-Induced Hearing Loss in Children Who Had Standard-risk HepatoblastomaTurkey
-
Implicit BioscienceNo longer availableCOVID | SARS-CoV2 | ARDS, Human | ArdsItaly
-
Baylor College of MedicineBoston Children's HospitalCompletedCholestasis | Cholestasis of Parenteral NutritionUnited States
-
ViiV HealthcareAvailableInfection, Human Immunodeficiency Virus
-
Matrix Biomed, Inc.AvailableProstate CancerUnited States
-
University of Colorado, DenverNo longer available
-
Galderma R&DNo longer availableBasal Cell Carcinoma | Bowen's Disease | Field Actinic Keratoses
-
Arthur J De LorimierCompletedParenteral Nutrition Associated CholestasisUnited States