Search clinical trials for: GBA, Glucocerceramide, AAV9, CNS gene therapy
Total 291982 results
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Benjamin GreenbergActive, not recruiting
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uniQure France SASRecruitingMesial Temporal Lobe EpilepsyUnited States
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REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom
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Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
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University of FloridaLacerta TherapeuticsCompletedPompe DiseaseUnited States
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Shanghai Jiao Tong University School of MedicineShanghai Vitalgen BioPharma Co., Ltd.RecruitingAromatic L-amino Acid Decarboxylase (AADC) DeficiencyChina
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingType II Gaucher DiseaseChina
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Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingAromatic L-amino Acid Decarboxylase Deficiency
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Grace Science, LLCRecruitingNGLY1 DeficiencyUnited States
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Megan WaldropAudentes TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited States
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Excision BioTherapeuticsActive, not recruiting
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Excision BioTherapeuticsEnrolling by invitationHIV-1-infectionUnited States
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Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
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PfizerRecruitingHousehold ContactsUnited States
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Novartis Gene TherapiesTerminatedSpinal Muscular AtrophyUnited States
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Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
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Taysha Gene Therapies, Inc.National Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGene Transfer | Giant Axonal NeuropathyUnited States
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Prevail TherapeuticsEli Lilly and CompanyRecruitingFrontotemporal DementiaUnited States, Australia, Belgium, Spain, United Kingdom, France
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Prevail TherapeuticsEli Lilly and CompanyRecruitingParkinson DiseaseUnited States, Israel
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Encoded TherapeuticsRecruiting
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Prevail TherapeuticsEli Lilly and CompanyRecruitingGaucher Disease | Gaucher Disease, Type 1United States, Spain, Germany
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Encoded TherapeuticsRecruiting
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Prevail TherapeuticsEli Lilly and CompanyActive, not recruitingGaucher Disease, Type 2United States, United Kingdom
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National Human Genome Research Institute (NHGRI)Sio Gene TherapiesRecruitingGangliosidosis | Lysosomal Diseases | GM1United States
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AviadoBio LtdRecruitingFrontotemporal Dementia | FTD | FTD-GRN | Dementia, FrontotemporalNetherlands, Spain, Poland, United States
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Tenaya TherapeuticsMedical University of South Carolina; Johns Hopkins University; University of... and other collaboratorsRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States, Italy, United Kingdom, France, Sweden, Germany
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Aspa TherapeuticsRecruiting
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SwanBio Therapeutics, Inc.RecruitingAMN | AMN Gene Mutation | X-ALDNetherlands, United States
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Accelerated Cure Project for Multiple SclerosisCharite University, Berlin, Germany; United States Department of Defense; US... and other collaboratorsNot yet recruitingMultiple Sclerosis | Fatigue
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University of Kansas Medical CenterNot yet recruiting
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University of Kansas Medical CenterNot yet recruiting
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Bristol-Myers SquibbNot yet recruitingRelapsing Multiple SclerosisChina
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Kyverna TherapeuticsNot yet recruitingMultiple Sclerosis | Multiple Sclerosis, Secondary Progressive | Multiple Sclerosis, Primary Progressive
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Inonu UniversityNot yet recruiting
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Biruni UniversityRecruiting
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Ankara Yildirim Beyazıt UniversityLokman Hekim ÜniversitesiRecruitingMultiple SclerosisTurkey
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Assiut UniversityNot yet recruiting
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University of Texas Southwestern Medical CenterNational Multiple Sclerosis Society; International Progressive Multiple Sclerosis...RecruitingProgressive Multiple SclerosisUnited States
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RenJi HospitalAbelZeta Pharma Inc.RecruitingA Study of C-CAR168 in the Treatment of Autoimmune Diseases Refractory to Standard Therapy (CAR-AID)Systemic Lupus Erythematosus (SLE) | Neuromyelitis Optica Spectrum Disorders | Immune-Mediated Necrotizing Myopathy | Multiple Sclerosis-Relapsing-RemittingChina
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University Hospital OstravaRecruitingMultiple Sclerosis | Lower Urinary Tract SymptomsCzechia
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Universidad de CórdobaRecruiting
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Ankara City Hospital BilkentRecruiting
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Stanford UniversityKyverna TherapeuticsRecruitingMultiple Sclerosis | Multiple Sclerosis, Secondary Progressive | Multiple Sclerosis, Primary ProgressiveUnited States
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MGH Institute of Health ProfessionsNot yet recruitingMultiple SclerosisUnited States
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St. Olavs HospitalRecruitingMultiple Sclerosis | InsomniaNorway
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Hunter College of City University of New YorkRecruiting
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Apurano Pharmaceuticals GmbHRecruitingStroke | Pain | Multiple Sclerosis | Chronic Pain | Traumatic Brain Injury | Neuropathic Pain | Pain, Chronic | Chronic Pain Syndrome | Paraplegia | Phantom Pain | Pain Syndrome | Central Neuropathic Pain | Phantom Limb Syndrome With PainGermany
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Apurano Pharmaceuticals GmbHRecruitingStroke | Pain | Multiple Sclerosis | Chronic Pain | Traumatic Brain Injury | Neuropathic Pain | Pain, Chronic | Chronic Pain Syndrome | Paraplegia | Phantom Pain | Pain Syndrome | Central Neuropathic Pain | Phantom Limb Syndrome With PainGermany
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University of California, San FranciscoNot yet recruitingDemyelinating Diseases | Clinically Isolated Syndrome, CNS Demyelinating | Multiple Sclerosis Brain Lesion | Multiple Sclerosis Acute and Progressive | Demyelination; Corpus CallosumUnited States