Search clinical trials for: Gene transfer vector
Total 270403 results
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Tenaya TherapeuticsMedical University of South Carolina; Johns Hopkins University; University of... and other collaboratorsRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States, Italy, United Kingdom, France, Sweden, Germany
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David WilliamsNational Heart, Lung, and Blood Institute (NHLBI); bluebird bio; California Institute... and other collaboratorsRecruitingA Gene Transfer Study Inducing Fetal Hemoglobin in Sickle Cell Disease (GRASP, BMT CTN 2001) (GRASP)Sickle Cell DiseaseUnited States
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Weill Medical College of Cornell UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingMyocardial Fibrosis | Cardiomyopathies | Friedreich Ataxia | Cardiac HypertrophyUnited States
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National Human Genome Research Institute (NHGRI)Sio Gene TherapiesRecruitingGangliosidosis | Lysosomal Diseases | GM1United States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI); Alaunos Therapeutics; National Center for Research...RecruitingRetroviridae Infections | CancerUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingX-linked Severe Combined Immunodeficiency (XSCID)United States
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National Cancer Institute (NCI)RecruitingBreast Cancer | Lung Cancer | Prostate Cancer | Colon Cancer | Liver CancerUnited States
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National Cancer Institute (NCI)Enrolling by invitationCervical Intraepithelial Neoplasia | Oropharyngeal Neoplasms | Squamous Intraepithelial Lesions of the Cervix | Cervical Neoplasms | Hematologic MalignaciesUnited States
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St. Jude Children's Research HospitalChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingHemophilia BUnited States, United Kingdom
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David WilliamsActive, not recruitingGene Therapy | Severe Combined Immunodeficiency, X LinkedUnited States, United Kingdom
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VegaVect, Inc.National Eye Institute (NEI)Active, not recruiting
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); Assisi Foundation; California...SuspendedSevere Combined Immunodeficiency Disease, X-linkedUnited States
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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Spark TherapeuticsCompletedHematologic Diseases | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Gene Therapy | Blood Coagulation Disorder | Gene Transfer | Adeno-Associated Virus (AAV) | Factor VIII (FVIII) | Factor VIII (FVIII)... and other conditionsUnited States
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Sarepta Therapeutics, Inc.Active, not recruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
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Fondazione TelethonCompletedImmunologic Deficiency SyndromesItaly, Israel
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Spark TherapeuticsCompletedHemophilia AUnited States, Australia, Canada, Israel, Thailand
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Bangabandhu Sheikh Mujib Medical University, Dhaka...Institute of Technology Transfer and Innovation (ITTI)Completed
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David WilliamsUniversity of California, Los Angeles; Boston Children's Hospital; Children's...CompletedSevere Combined ImmunodeficiencyUnited States
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Adverum Biotechnologies, Inc.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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David WilliamsActive, not recruiting
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic L-amino Acid Decarboxylase (AADC) DeficiencyTaiwan
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University of AlbertaCanadian Institutes of Health Research (CIHR); Imperial College London; University... and other collaboratorsCompleted
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Baxalta now part of ShireTerminatedHemophilia BTurkey, Spain
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Adverum Biotechnologies, Inc.Completed
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Neurocrine BiosciencesVoyager TherapeuticsCompletedBrain Diseases | Central Nervous System Diseases | Nervous System Diseases | Parkinson's Disease | Parkinsonian Disorders | Movement Disorders | Neurodegenerative Diseases | Idiopathic Parkinson's Disease | Basal Ganglia DiseaseUnited States
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Donald B. Kohn, M.D.National Institutes of Health (NIH); FDA Office of Orphan Products DevelopmentCompletedSevere Combined ImmunodeficiencyUnited States
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Liverpool School of Tropical MedicineLondon School of Hygiene and Tropical Medicine; University of Bergen; Kamuzu... and other collaboratorsCompletedMalaria in Pregnancy | Adherence, TreatmentKenya
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH)CompletedBatten Disease | Late-Infantile Neuronal Ceroid LipofuscinosisUnited States
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Weill Medical College of Cornell UniversityNathan's Battle FoundationCompletedBatten Disease | Late Infantile Neuronal Ceroid LipofuscinosisUnited States
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Armauer Hansen Research Institute, EthiopiaUnited States Agency for International Development (USAID); Tulane University; Addis Continental Institute of Public Health and other collaboratorsUnknown
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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GiveWellNew Incentives; All Babies are Equal InitiativeCompletedHepatitis B | Measles | Pertussis | Tetanus | Diphtheria | Tuberculosis | Pneumonia, Bacterial | Yellow Fever | Polio | Rotavirus Infections | Haemophilus Influenzae Type b InfectionNigeria
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Neurocrine BiosciencesOregon Health and Science University; University of California, San Francisco; Veristat, Inc... and other collaboratorsCompletedParkinson's DiseaseUnited States
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); University of Tennessee; Assisi...Completed
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National Human Genome Research Institute (NHGRI)CompletedSevere Combined Immunodeficiency SyndromeUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedArteriosclerosis | Intermittent ClaudicationUnited States
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National Institute of Allergy and Infectious Diseases...UnknownX-Linked Combined Immunodeficiency DiseasesUnited States
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Shenzhen Geno-Immune Medical InstituteUnknownAdenosine DeAminase Severe Combined ImmunoDeficiency (ADA-SCID)China
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Shenzhen Geno-Immune Medical InstituteUnknownSCID, X LinkedChina
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Shenzhen Geno-Immune Medical InstituteUnknown
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha-1 Antitrypsin DeficiencyUnited States, Ireland
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St. Jude Children's Research HospitalNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Assisi...CompletedGalactosialidosisUnited States
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Tocagen Inc.CompletedGlioblastoma | Anaplastic Oligoastrocytoma | Anaplastic Astrocytoma | Anaplastic OligodendrogliomaUnited States
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Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, WorcesterCompletedLeber Congenital AmaurosisUnited States
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National Human Genome Research Institute (NHGRI)National Institutes of Health Clinical Center (CC); National Cancer Institute... and other collaboratorsCompletedADA-SCID | Adenosine Deaminase DeficiencyUnited States
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H. Lee Moffitt Cancer Center and Research InstituteNational Gene Vector LaboratoryCompletedMalignant MelanomaUnited States
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); Doris Duke Charitable FoundationCompleted
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EpicentreCentre de Recherche Médicale et Sanitaire (Cermes), NiameyCompleted