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Search clinical trials for: Genetic Disease
Total 381775 results
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Boston Children's HospitalCystic Fibrosis FoundationRecruitingCystic FibrosisUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingAcute Chest SyndromeFrance
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Luye Pharma Group Ltd.RecruitingTardive Dyskinesia | Huntington DiseaseChina
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University of PennsylvaniaRecruitingLCAT DeficiencyUnited States
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Assistance Publique Hopitaux De MarseilleAix Marseille Université; ALPHENYXNot yet recruitingPsoriasis | Atopic Dermatitis
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Hospices Civils de LyonRecruiting
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Rocket Pharmaceuticals Inc.Recruiting
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Richard FryeAutism Discovery and Treatment FoundationRecruitingEpilepsy | Neurodevelopmental Disorders | Autism Spectrum Disorder | Down Syndrome | Mitochondrial Encephalomyopathies | Pediatric Acute-Onset Neuropsychiatric Syndrome | Cerebral Folate Deficiency | Pediatric Autoimmune Neuropsychiatric Disorder Associated With Streptococcal InfectionUnited States
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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Reem Ali ShakerRecruiting
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Atamyo TherapeuticsNot yet recruiting
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Hemab ApSRecruitingGlanzmann ThrombastheniaUnited States, Belgium, France, Italy, Netherlands, United Kingdom
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Foundation For Rare Disease ResearchInstitute for Asthma & Allergy; Virant Diagnostics, Inc.; MedBio Reference Laboratories...Not yet recruitingAngioedema | Urticaria | C1 Inhibitor Deficiency | Angioedemas, Hereditary | Mastocytosis | Indolent Systemic Mastocytosis | Systemic Mastocytoses | ACE Inhibitor-Induced Angioedema
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Diakonhjemmet HospitalRecruiting
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Children's Hospital of Fudan UniversityNot yet recruiting
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Perha PharmaceuticalsFondation Jérôme Lejeune; European Innovation Council; France 2030 programRecruitingHealthy Volunteers | Down Syndrome | Alzheimer's DiseaseFrance
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Thammasat UniversityNot yet recruiting
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University Hospital, Strasbourg, FranceRecruiting
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New York Stem Cell Foundation Research InstituteRecruitingPTSD | Multiple Sclerosis | Cervical Cancer | Diabetes Mellitus, Type 2 | Diabetes Mellitus | Diabetes | Macular Degeneration | Diabetes Mellitus, Type 1 | Parkinson Disease | Amyotrophic Lateral Sclerosis | Dementia | Ovarian Cancer | Alzheimer Disease | ALS | Vulvar Cancer | Post Traumatic Stress Disorder | Lewy Body Disease and other conditionsUnited States
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New York Stem Cell Foundation Research InstituteCharcot-Marie-Tooth AssociationRecruitingHealthy | Charcot-Marie-Tooth DiseaseUnited States
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Unity Health TorontoNot yet recruiting
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Lithuanian University of Health SciencesRecruitingInflammation | Cognitive Dysfunction | Genetic Predisposition to Disease | Endotoxemia | Major Depressive Disorder | Blood Brain Barrier DefectLithuania
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Inge Marie SvaneAdaptimmuneNot yet recruitingMelanoma | Melanoma Stage IV | Melanoma Stage III
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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UMC UtrechtNot yet recruitingGlanzmann Thrombasthenia
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October 6 UniversityUniversity of Florida; Beni-Suef University; National Heart Institute, EgyptRecruitingHeart Failure | Genetic PolymorphismsUnited States
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University College CorkNot yet recruitingGestational Diabetes | Neonatal Encephalopathy | Diastolic Dysfunction | Trisomy 21 | Transient Tachypnea of the Newborn | Small for Gestational Age at DeliveryIreland
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Johns Hopkins UniversityRecruitingGranular Dystrophy, CornealUnited States
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Kyowa Kirin Korea Co., Ltd.RecruitingFGF23-related Hypophosphataemic Rickets and OsteomalaciaKorea, Republic of
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Forma Therapeutics, Inc.Novo Nordisk A/SRecruitingSickle Cell DiseaseLebanon, Canada, Kenya, United Kingdom
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Children's Hospital of Fudan UniversityRecruiting
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of MedicineNot yet recruitingHepatocellular Carcinoma | Liposarcoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Malignant Rhabdoid Tumor | Yolk Sac Tumor | Embryonal Sarcoma of LiverUnited States
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Grace Science, LLCRecruitingNGLY1 DeficiencyUnited States
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Riphah International UniversityRecruiting
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Riphah International UniversityRecruitingDown SyndromePakistan
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Hospices Civils de LyonRecruiting
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Hospital Affiliated to the Institute of Neurology...Not yet recruitingHepatolenticular Degeneration; WilsonChina
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Chinese University of Hong KongNot yet recruiting
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University of SevilleRecruitingDown Syndrome | Physical Disability | FamilySpain
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University of MinnesotaRecruitingTourette Syndrome | Persistent Tic DisorderUnited States
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IRCCS San RaffaeleUniversità Vita-Salute San RaffaeleRecruitingCarcinoma, Renal Cell | Von Hippel-Lindau DiseaseItaly
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AstraZenecaNot yet recruitingHepatocellular Carcinoma | Prostate CancerUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Møreforsking ASUniversity of Manchester; Helse Møre og Romsdal HF; Epax Norway ASRecruitingAtopic DermatitisNorway
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IRCCS San RaffaeleRecruitingClear Cell Renal Cell Carcinoma | VHL SyndromeItaly
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Mirum Pharmaceuticals, Inc.RecruitingAlagille SyndromeUnited States
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University of California, Los AngelesUniversity of Iowa; Children's Hospital Colorado; University of Kansas Medical... and other collaboratorsRecruitingChronic Rhinosinusitis (Diagnosis) | Cystic Fibrosis | Olfactory Disorder | Cystic Fibrosis in Children | Olfactory ImpairmentUnited States
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SanofiPulse Infoframe Ltd.RecruitingNiemann-Pick Diseases | Acid Sphingomyelinase DeficiencyUnited States