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Search clinical trials for: Hereditary Angioedema Type I
Total 492001 results
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St. Jude Children's Research HospitalActive, not recruitingRetinoblastomaUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingStage III Kidney Wilms Tumor | Stage IV Kidney Wilms TumorUnited States, Canada, Australia, New Zealand, Puerto Rico, Israel, Switzerland
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Washington University School of MedicineThe Foundation for Barnes-Jewish HospitalTerminatedLynch Syndrome | Hereditary Breast and Ovarian CancerUnited States
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Amsterdam UMC, location VUmcCompleted
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Jaeb Center for Health ResearchFoundation Fighting BlindnessActive, not recruitingUsher Syndrome, Type 2A | Retinitis Pigmentosa 39United States, Canada, France, Germany, Netherlands, United Kingdom
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National Cancer Institute (NCI)CompletedNeurofibromatosis 1 | Neurofibroma, PlexiformUnited States
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Washington University School of MedicineEnrolling by invitation
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Region SkaneNovartisActive, not recruitingChild | Neurofibromatosis 1 | Neurofibroma, PlexiformSweden
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Basal Cell CarcinomaAustralia
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Memorial Sloan Kettering Cancer CenterActive, not recruitingHearing Loss | Intraocular RetinoblastomaUnited States
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Sun Yat-sen UniversityFudan UniversityActive, not recruiting
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Giselle ShollerTranslational Genomics Research Institute; Dell, Inc.CompletedGlioma | Renal Cell Carcinoma | Osteosarcoma | Ependymoma | Medulloblastoma | Neuroblastoma | Meningioma | Craniopharyngioma | Choroid Plexus Neoplasms | Rhabdomyosarcoma | Wilms Tumor | Ewings Sarcoma | Malignant Rhabdoid Tumor | Liver Tumors | Germ Cell Tumors | Dysembryoplastic Neuroepithelial Tumor | Clear Cell Sarcoma | ... and other conditionsUnited States, Lebanon
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Pharming Technologies B.V.US Hereditary Angioedema AssociationCompleted
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Great Ormond Street Hospital for Children NHS Foundation...AstraZenecaCompletedNeurofibromatosis Type 1 | Optic Nerve Glioma | Plexiform NeurofibromaUnited Kingdom
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The Cleveland ClinicActive, not recruitingAL Amyloidosis | Amyloidosis | Amyloid Neuropathies, Familial | Amyloid | Transthyretin Amyloidosis | Amyloid Cardiomyopathy | Amyloid - PrimaryUnited States
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Memorial Sloan Kettering Cancer CenterCompletedSarcoma | Small Intestine Cancer | Ovarian Cancer | Lung Cancer | Brain and Central Nervous System Tumors | Metastatic Cancer | Neuroblastoma | Intraocular Melanoma | Melanoma (Skin) | RetinoblastomaUnited States
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Cellatoz Therapeutics, IncActive, not recruitingCharcot Marie Tooth Disease, Type 1Korea, Republic of
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Pharnext S.C.A.Worldwide Clinical TrialsActive, not recruitingCharcot-Marie-Tooth DiseaseUnited States, Spain, Belgium, Italy, Israel, Canada, Denmark, France, Germany
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Ashley ShoemakerEnrolling by invitationPseudohypoparathyroidism Type 1a | Albright Hereditary Osteodystrophy | PseudohypoparathyroidismUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI)Active, not recruitingBRCA1 Syndrome | BRCA2 Syndrome | No Evidence of Disease | Hereditary Ovarian Carcinoma | Hereditary Female Breast CarcinomaUnited States
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Pharming Technologies B.V.CompletedHereditary AngioedemaIsrael, Italy, United States, Czechia, Germany, Hungary, Poland, Romania, Slovakia, North Macedonia
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingHereditary Breast and Ovarian Cancer Syndrome | Premenopausal | Deleterious BARD1 Gene Mutation | Deleterious BRCA1 Gene Mutation | Deleterious BRCA2 Gene Mutation | Deleterious BRIP1 Gene Mutation | Deleterious EPCAM Gene Mutation | Deleterious MLH1 Gene Mutation | Deleterious MSH2 Gene Mutation | Deleterious... and other conditionsUnited States
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ShireTakedaCompleted
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SpringWorks Therapeutics, Inc.Active, not recruitingPlexiform Neurofibroma | Neurofibromatosis Type 1 (NF1)United States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Maastricht University Medical CenterEnrolling by invitationTuberous Sclerosis | Basal Cell Nevus Syndrome | Cutis Laxa | Epidermolysis Bullosa | Ichthyosis | Ectodermal Dysplasia | Albinism | Xeroderma Pigmentosum | Birt-Hogg-Dube Syndrome | Palmoplantar KeratosesNetherlands
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National Cancer Institute (NCI)Completed
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.TerminatedNeurofibromatosis and Malignant Peripheral Nerve Sheath TumorsChina
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Wuhan Union Hospital, ChinaCompletedNeuroblastoma | Wilms Tumor | Hepatoblastoma | 18F-FDGChina
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City of Hope Medical CenterActive, not recruitingUnspecified Childhood Solid Tumor, Protocol Specific | Solid Tumor | Ewing Sarcoma | Unspecified Adult Solid Tumor, Protocol Specific | Recurrent Childhood Medulloblastoma | Recurrent Childhood Ependymoma | Recurrent Neuroblastoma | Recurrent Adult Soft Tissue Sarcoma | Recurrent Adult Brain Tumor | Recurrent... and other conditionsUnited States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingNeurofibromatosis 1United States
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Hospital JP GarrahanHospital San Juan de Dios, SantiagoActive, not recruitingUnilateral RetinoblastomaArgentina
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AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis 1 | Plexiform Neurofibroma (PN)United States, Canada, France, Italy, Germany, China, United Kingdom, Spain, Japan, Russian Federation, Australia, Poland, Brazil
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SpringWorks Therapeutics, Inc.AvailableNeurofibromatosis Type 1-Associated Plexiform Neurofibromas | Histiocytic Neoplasm | Other MAP-K Pathway Driven Diseases
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BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | PediatricSpain, Austria, Canada, France, Germany, Israel, Italy, Poland, Romania, United Kingdom
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Massachusetts General HospitalPfizerActive, not recruitingPain | SchwannomatosisUnited States
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Washington University School of MedicineNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National...CompletedDiabetes Mellitus | Ataxia | Wolfram Syndrome | Optic Nerve AtrophyUnited States
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Praxis Precision MedicinesCompletedEssential TremorUnited States, Canada
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Intellia TherapeuticsActive, not recruitingHereditary AngioedemaFrance, New Zealand, Germany, United Kingdom, Netherlands, Australia
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National Cancer Institute (NCI)Completed
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingFatigue | Overweight | Lynch Syndrome | Chronic Lymphocytic Leukemia | BRCA1 Gene Mutation | BRCA2 Gene Mutation | Breast Carcinoma | Cancer Survivor | Ovarian Carcinoma | Health Status Unknown | Body Mass Index 25 or GreaterUnited States
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Praxis Precision MedicinesPraxis Precision Medicines Australia Pty LtdCompletedEssential TremorUnited States, Australia, New Zealand
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St. Jude Children's Research HospitalNational Cancer Institute (NCI)Active, not recruitingRetinoblastoma | Retinal NeoplasmUnited States
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Masonic Cancer Center, University of MinnesotaCompletedSoft Tissue Sarcoma | Medulloblastoma | Retinoblastoma | Rhabdomyosarcoma | Hepatoblastoma | Primary Malignant Brain Neoplasms | CNS Tumors | Germ Cell Tumors | Ewing's Family Tumors | Renal Tumors | Supra-tentorial Primative Neuro-Ectodermal Tumor (PNET) | Atypical Teratoid/Rhabdoid Tumor (AT/RT)United States
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National Cancer Institute (NCI)Active, not recruitingNeurofibromatosis 1 (NF1) | Plexiform Neurofibromas (PN)United States
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Pharnext S.C.A.Premier Research Group plc; Eurofins Optimed; Synteract HCR (Syneos Health); Gr... and other collaboratorsActive, not recruitingCharcot-Marie-Tooth Disease, Type IAUnited States, Belgium, Canada, France, Netherlands, Spain, United Kingdom
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University Hospital, Clermont-FerrandActive, not recruitingCharcot-Marie-Tooth Type 1A NeuropathyFrance
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingBreast Carcinoma | Fallopian Tube Carcinoma | Endometrial Carcinoma | Ovarian Carcinoma | Primary Peritoneal Carcinoma | Deleterious CDH1 Gene Mutation | Deleterious DICER1 Gene Mutation | Deleterious SMARCA4 Gene Mutation | Deleterious STK11 Gene MutationUnited States
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Vanderbilt University Medical CenterEnrolling by invitationFamilial Adenomatous PolyposisUnited States
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Jonsson Comprehensive Cancer CenterNovartis PharmaceuticalsTerminatedNeuroma, Acoustic | Neurofibromatosis Type 2United States